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Clinical Trials on Spinal Muscular Atrophy With Respiratory Distress 1
Total 927 results
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Assistance Publique - Hôpitaux de ParisNot yet recruitingMyotonic Dystrophy 1 | Steinert's Disease | MetforminFrance
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University of... and other collaboratorsCompletedMyotonic Dystrophy Type 1Netherlands, France, Germany, United Kingdom
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National Human Genome Research Institute (NHGRI)Completed
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Nantes University HospitalIstituto Giannina Gaslini; Pediatric Intensive Care Unit, Trousseau University... and other collaboratorsCompletedCardiac Arrest | Cardiogenic Shock | Acute Respiratory Distress Syndrome (ARDS)France, Italy
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University of WashingtonEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedMultiple Sclerosis | Low Back Pain | Chronic Pain | Muscular Dystrophies | Spinal Cord Injury | Other and Unspecified Amputation Stump ComplicationsUnited States
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Hospital for Special Surgery, New YorkRoche Pharma AG; Genentech, Inc.TerminatedGranulomatosis With Polyangiitis (Wegener's Granulomatosis)United States
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University of Campania "Luigi Vanvitelli"RecruitingSudden Cardiac Death | Myotonic Dystrophy 1Italy
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Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
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Yuri MatusovMallinckrodtNot yet recruitingPulmonary Hypertension | Acute Respiratory Distress SyndromeUnited States
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University of OklahomaActelionCompletedPulmonary Hypertension | Acute Respiratory Distress Syndrome | Acute Lung InjuryUnited States
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University of Alabama at BirminghamNational Institutes of Health (NIH); Mereo BioPharmaCompletedEmphysema or COPD | Alpha-1 Antitrypsin Deficiency (AATD) | Pi*ZZ, Pi*SZ, Pi*Null, Another Rare Phenotype/Genotype Known to be Associated With Either Low or Functionally Impaired AAT Including F or I MutationsUnited States
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Instituto Nacional de Cancerologia de MexicoCompletedPhase II Clinical Trial | Ninety-six Histologically Confirmed NSCLC Patients With BM | Randomized 1:1 to Received TN Plus WBR or Only WBR | ICPFS Evaluated by Two Blinded and Independent Radio-oncologist With MRIMexico
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Inonu UniversityCompletedCoping With Prenatal Stress | Fetal Health AnxietyTurkey
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University College, LondonNational Institute for Health Research, United Kingdom; Myotonic Dystrophy... and other collaboratorsRecruitingMyotonic Dystrophy 1 | Dysphagia, OropharyngealUnited Kingdom
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Shirley Ryan AbilityLabRecruitingMultiple Sclerosis | Paralysis | Muscular Dystrophy | Spinal Cord Injuries | Cerebrovascular Accident | Post-polio SyndromeUnited States
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Leigh R. Hochberg, MD, PhD.National Institute of Neurological Disorders and Stroke (NINDS); US Department... and other collaboratorsRecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Cord Injuries | Tetraplegia | Brain Stem Infarctions | Locked in SyndromeUnited States
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Hannover Medical SchoolWithdrawnHeart Failure | Pulmonary Hypertension | Heart Failure With Reduced Ejection Fraction | Heart Failure With Normal Ejection FractionGermany
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Fudan UniversityNot yet recruitingMalnutrition | Sarcopenia | Non Small Cell Lung CancerChina
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University of CalgaryInternational Collaboration on Repair DiscoveriesUnknownSpinal Cord Injuries | Autonomic Dysreflexia | Orthostatic Hypotension, DysautonomicCanada
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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University of WashingtonCompletedMultiple Sclerosis | Muscular Dystrophy | Spinal Cord Injury | Post-polio SyndromeUnited States
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Powell Mansfield Inc.CompletedHealthy | Amyotrophic Lateral Sclerosis | Obstructive Sleep Apnea | Muscular DystrophiesUnited States
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Aga Khan UniversityMedical Research Council, PakistanCompletedPulmonary Hypertension | Adult Respiratory Distress Syndrome
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Montefiore Medical CenterCompletedTransient Tachypnea of the Newborn | Respiratory Distress | Delayed Transition of the Newborn | Persistent Pulmonary HypertensionUnited States
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Assistance Publique Hopitaux De MarseilleRecruitingAcute Respiratory Distress SyndromeFrance
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NICHD Neonatal Research NetworkNational Center for Research Resources (NCRR)TerminatedPneumonia | Sepsis | Hypertension, Pulmonary | Infant, Small for Gestational Age | Infant, Premature | Infant, Low Birth Weight | Infant, Newborn | Respiratory Distress Syndrome (RDS)United States
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Lokman Hekim ÜniversitesiHacettepe UniversityCompletedQuality of Life | Lower Urinary Tract Symptoms | Muscle Weakness | Duchenne Muscular Dystrophy | Pelvic Floor Muscle Weakness | Posture Disorders in Children | Lumbar LordosisTurkey
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University of PittsburghRespirtech, Inc.CompletedDuchenne Muscular DystrophyUnited States
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National Institute of Neurological Disorders and...Terminated
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Beijing Anzhen HospitalRecruitingHeart Failure | Cardiac Arrest | Acute Respiratory Distress Syndrome | Cardiogenic Shock | Acute Respiratory FailureChina
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University Medical Center GroningenGlaxoSmithKlineRecruitingEGPA - Eosinophilic Granulomatosis With PolyangiitisNetherlands
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Imperial College LondonAstraZenecaEnrolling by invitationEGPA - Eosinophilic Granulomatosis With PolyangiitisUnited Kingdom
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Centre d'Investigation Clinique et Technologique...UnknownHeart, Respiratory, Disease, FunctionalFrance
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Ultragenyx Pharmaceutical IncNewcastle UniversityCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Nonaka Disease | Quadriceps Sparing Myopathy (QSM) | Distal Myopathy With Rimmed Vacuoles (DMRV)United States, Bulgaria, Canada, France, United Kingdom
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Nanjing Medical UniversityRecruitingHeart Failure | Cardiac Arrest | Acute Respiratory Distress Syndrome | Cardiogenic Shock | Acute Respiratory FailureChina
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University of South FloridaBristol-Myers Squibb; University of Pennsylvania; National Institute of Arthritis... and other collaboratorsActive, not recruitingWegener's Granulomatosis | Granulomatosis With Polyangiitis | ANCA-Associated Vasculitis | Granulomatosis With Polyangiitis (Wegener's)United States, United Kingdom, Ireland, Canada, Germany
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Royal College of Surgeons, IrelandBeaumont Hospital; Post Polio Support Group IrelandCompleted
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NMC Specialty HospitalCompletedThrombosis | COVID-19 Pneumonia | Severe Acute Respiratory Syndrome (SARS) Pneumonia | COVID-19 Acute Respiratory Distress SyndromeIndia
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Institut Català d'OncologiaDepartment of Health, Generalitat de CatalunyaRecruitingSarcopenia | Head and Neck Small Cell CarcinomaSpain
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Cure CMDCompletedCongenital Muscular DystrophyUnited States
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Shanghai Zhongshan HospitalRecruitingGranulomatosis With PolyangiitisChina
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Centre hospitalier de l'Université de Montréal...CompletedPneumonia | Acute Respiratory Distress Syndrome | Pulmonary Embolism | Dyspnea | Hypoxemia | AtelectasisCanada
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Bayside HealthCompletedRespiratory Insufficiency | Shock, Cardiogenic | Respiratory Distress Syndrome, AdultAustralia
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prof. dr. Koen Van LaereUniversitaire Ziekenhuizen KU Leuven; KU Leuven; University Hospital, Ghent; Fund...Not yet recruitingParkinson Disease | Alzheimer Disease | Dementia With Lewy Bodies | MSA - Multiple System AtrophyBelgium
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University of Health Sciences LahoreNot yet recruitingPatient With IV Cannula Induce Phlebitis
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
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IRCCS Eugenio MedeaCompleted
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Leigh R. Hochberg, MD, PhD.National Institute on Deafness and Other Communication Disorders (NIDCD)RecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Dysarthria | Brain Stem Infarctions | Locked-in Syndrome | AnarthriaUnited States
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyCanada, United States, Bulgaria