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Clinical Trials on Spinal Muscular Atrophy With Respiratory Distress 1
Total 927 results
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Holland Bloorview Kids Rehabilitation HospitalRecruiting
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BiogenRecruitingSpinal Muscular AtrophyUnited States, Germany, Italy, Hungary, Japan
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Hoffmann-La RocheActive, not recruitingMuscular Atrophy, SpinalUnited States, Belgium, Brazil, Russian Federation, Australia, Taiwan, Poland
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BiogenCompletedMuscular Atrophy, SpinalChina, United States, Netherlands, Spain, Korea, Republic of, Taiwan, Australia, Canada, Chile, Saudi Arabia, Poland, Israel, Brazil, Russian Federation, Hungary, Japan, United Kingdom, Italy, Germany, Estonia, Greece, Mexico, Colombia and more
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Ohio State UniversityCure SMAActive, not recruitingSpinal Muscular AtrophyUnited States
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BiogenEnrolling by invitationMuscular Atrophy, SpinalUnited States, Spain, Taiwan, Chile, Saudi Arabia, Brazil, Russian Federation, Mexico, Germany, Estonia, Japan, Canada, Colombia, Lebanon, Poland, Italy, China
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Clinic for Special ChildrenGenentech, Inc.Active, not recruitingSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, France, Brazil, Croatia, Italy, Russian Federation, Saudi Arabia, Serbia, Switzerland, Turkey, Ukraine, Poland
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular AtrophyUnited States, United Kingdom, Australia, Belgium, Canada, Japan
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Hospital Israelita Albert EinsteinMinistry of Health, BrazilCompletedSpinal Muscular AtrophyBrazil
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BiogenCompletedSpinal Muscular AtrophyUnited States, Germany, Spain, Canada, France, Hong Kong, Italy, Japan, Korea, Republic of, Sweden
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BiogenCompleted
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Hospices Civils de LyonUnknownResponsiveness and Validation Study of MFM-20 in SMA Patients Treated With Nusinersen (RetroNusiMFM)Spinal Muscular AtrophyFrance
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Genentech, Inc.Approved for marketingMuscular Atrophy, SpinalUnited States
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University Hospital, RouenSociety GENOMIC VISIONTerminatedSpinal Muscular AtrophyFrance
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Hoffmann-La RocheCompleted
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University of UtahAbbott; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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Rigshospitalet, DenmarkCompleted
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HealthCore-NERIThe Spinal Muscular Atrophy FoundationCompletedSpinal Muscular AtrophyUnited States, Canada
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Centro Universitário Augusto MottaCompletedSpinal Muscular Atrophy
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Centre Hospitalier Régional de la CitadelleCompletedSafety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 (EMOTAS)Spinal Muscular Atrophy Type 3Belgium
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular Atrophy Type IKorea, Republic of, Taiwan, Japan
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Stanford UniversityCompletedA Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy PatientsMuscular Atrophy, SpinalUnited States
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University of UtahLeadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular Atrophy Type IUnited States, Canada, Germany
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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GeneCradle IncRecruiting
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Charitable Foundation Children with Spinal Muscular...WithdrawnSpinal Muscular Atrophy | Neuromuscular DisordersUkraine
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University of OxfordOxford Brookes University; Oxford University Hospitals NHS Trust; Scholar Rock... and other collaboratorsRecruitingSpinal Muscular AtrophyUnited Kingdom
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McGill University Health Centre/Research Institute...Not yet recruiting
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Rigshospitalet, DenmarkRecruitingSpinal Muscular AtrophyDenmark
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National Taiwan University HospitalNot yet recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...IRCCS Eugenio Medea; Azienda Ospedaliera Universitaria Policlinico "G. Martino... and other collaboratorsNot yet recruitingSpinal Muscular Atrophy
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Hoffmann-La RocheRecruiting
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GeneCradle IncRecruitingSpinal Muscular AtrophyChina
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Fondazione Policlinico Universitario Agostino Gemelli...University of Milan; Ospedale Pediatrico Bambino GesùRecruiting
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University of Castilla-La ManchaRecruiting
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University of OxfordHoffmann-La Roche; Oxford University Hospitals NHS Trust; Novartis Gene TherapiesRecruiting
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Genentech, Inc.RecruitingSpinal Muscular AtrophyUnited States, Puerto Rico
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Bakri ElsheikhGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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BiogenRecruiting
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSpinal Muscular AtrophyUnited Kingdom
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Kaohsiung Medical University Chung-Ho Memorial...The Chinese Foundation of Health; Taipei Institute of PathologyRecruiting
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BiogenActive, not recruitingSpinal Muscular AtrophyUnited States, Taiwan, Israel, Australia, Qatar, United Kingdom, Turkey, Italy, Germany, Argentina, Canada
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Hospital Israelita Albert EinsteinBiogenActive, not recruitingSpinal Muscular AtrophyBrazil, Argentina, Chile, Colombia, Mexico, Uruguay
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Hospices Civils de LyonCompletedSpinal Muscular AtrophyFrance
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Istanbul Medipol University HospitalActive, not recruitingMuscular Atrophy, SpinalTurkey
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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Columbia UniversityThe Spinal Muscular Atrophy FoundationCompleted
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University Medical Centre LjubljanaCompleted