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Clinical Trials on Spinal Muscular Atrophy in United Kingdom
Total 20430 results
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AveXis, Inc.United BioSource, LLCRecruitingSpinal Muscular Atrophy (SMA)Japan, United States, Korea, Republic of, Israel, Greece, Ireland, Portugal, Russian Federation, Taiwan
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Hoffmann-La RocheRecruiting
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University of UtahCompleted
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Ohio State UniversityCure SMAActive, not recruitingSpinal Muscular AtrophyUnited States
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Clinic for Special ChildrenGenentech, Inc.Active, not recruitingSpinal Muscular AtrophyUnited States
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University of UtahAbbott; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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Stanford UniversityCompletedA Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy PatientsMuscular Atrophy, SpinalUnited States
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WestatNational Institute of Neurological Disorders and Stroke (NINDS)TerminatedSpinal Muscular Atrophy Type IUnited States
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Biohaven Pharmaceuticals, Inc.Active, not recruitingNeuromuscular Diseases | Spinal Muscular Atrophy | SMAUnited States, Netherlands, United Kingdom, Spain, Czechia, Belgium, Germany, Italy, Poland
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Bakri ElsheikhGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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Columbia UniversityThe Spinal Muscular Atrophy FoundationCompleted
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Ohio State UniversityBiogen; Cure SMACompleted
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United BioSource, LLCAveXis, Inc.Approved for marketing
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National Institute of Neurological Disorders and...Terminated
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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BiogenCompleted
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BiogenCompleted
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Columbia UniversityGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheRecruitingMuscular Atrophy, SpinalGermany, United States, Belgium
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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University of UtahEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedSpinal Muscular AtrophyUnited States
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BiogenCompleted
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BiogenActive, not recruitingMuscular Atrophy, SpinalChina, United States, Netherlands, Spain, Korea, Republic of, Taiwan, Australia, Canada, Chile, Saudi Arabia, Poland, Israel, Brazil, Russian Federation, Hungary, Japan, United Kingdom, Italy, Germany, Estonia, Greece, Mexico, Colombia and more
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Hoffmann-La RocheRecruiting
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Grand Valley State UniversityActive, not recruitingCerebral Palsy | Spinal Cord Injuries | Spinal Muscular Atrophy | Genetic Disease | Spina Bifida | Development DelayUnited States
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Columbia UniversityCompletedSpinal Muscular Atrophy | Neuromuscular DiseaseUnited States
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BiogenCompletedSpinal Muscular AtrophyUnited States, Canada
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Bio-Medical Research, Ltd.Liverpool University Hospitals NHS Foundation TrustCompletedKnee Osteoarthritis | Disuse AtrophyUnited Kingdom
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BiogenCompletedSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheActive, not recruitingMuscular Atrophy, SpinalUnited States, Belgium, Brazil, Russian Federation, Australia, Taiwan, Poland
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BiogenActive, not recruitingMuscular Atrophy, SpinalUnited States, Spain, Germany, Italy, Israel
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University of UtahLeadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular Atrophy Type IUnited States, Canada, Germany
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States, Canada
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BiogenTerminatedSpinal Muscular AtrophyUnited States, Germany
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Massachusetts General HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknownSpinal Muscular AtrophyUnited States
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CytokineticsAstellas Pharma Global Development, Inc.CompletedSpinal Muscular AtrophyUnited States, Canada
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HealthCore-NERIThe Spinal Muscular Atrophy FoundationCompletedSpinal Muscular AtrophyUnited States, Canada
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Novartis PharmaceuticalsActive, not recruitingType 2 Spinal Muscular AtrophyUnited States, China, Saudi Arabia, Thailand, Singapore, Brazil, Malaysia, Taiwan, Colombia, Mexico, Denmark, Egypt, India, South Africa, Vietnam
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NMD Pharma A/SRecruitingSpinal Muscular AtrophyUnited States, Spain, Belgium, Denmark, Germany, Netherlands, Italy, Canada
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National Institute of Neurological Disorders and...CompletedMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy (SBMA)United States
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
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BiogenCompletedSpinal Muscular AtrophyUnited States, Germany, Spain, Canada, France, Hong Kong, Italy, Japan, Korea, Republic of, Sweden
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Genentech, Inc.Approved for marketingMuscular Atrophy, SpinalUnited States
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Nemours Children's ClinicRecruitingCharcot-Marie-Tooth Disease | Motor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Muscular Atrophy | Neuromuscular Disease | Spinal Muscular Atrophy With Respiratory Distress 1 | Peroneal Muscular AtrophyUnited States
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BiogenRecruitingSpinal Muscular AtrophyUnited States, Germany, Italy, Hungary, Japan
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, France, Brazil, Croatia, Italy, Russian Federation, Saudi Arabia, Serbia, Switzerland, Turkey, Ukraine, Poland
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GlaxoSmithKlineCompleted
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BiogenEnrolling by invitationMuscular Atrophy, SpinalUnited States, Spain, Taiwan, Chile, Saudi Arabia, Brazil, Russian Federation, Mexico, Germany, Estonia, Japan, Canada, Colombia, Lebanon, Poland, Italy, China
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AbiliTech Medical Inc.Richard M. Schulze Family FoundationRecruitingCerebral Palsy | Muscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Spinal Muscular Atrophy | Limb Girdle Muscular Dystrophy | FSHDUnited States
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Nemours Children's ClinicCompleted