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Clinical Trials on Spinal Muscular Atrophy in United States
Total 20360 results
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Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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Marco CapogrossoRoche-GenentechRecruitingSpinal Muscular Atrophy Type 3 | Spinal Muscular Atrophy Type 4United States
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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Northwell HealthCompletedAdult Spinal Muscular AtrophyUnited States
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Alcyone Therapeutics, IncBiogenRecruitingScoliosis | Spinal Muscular Atrophy | Spine DeformityUnited States
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Natera, Inc.WithdrawnGenetic Testing | Spinal Muscular Atrophy (SMA) | Carrier ScreeningUnited States
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Nationwide Children's HospitalNovartisActive, not recruitingSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IUnited States
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSpinal Muscular Atrophy Type 3 | Mitochondrial MyopathyUnited States
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WestatNational Institute of Neurological Disorders and Stroke (NINDS)TerminatedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IIIUnited States
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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Stanford UniversityCompletedMuscular Atrophy, SpinalUnited States
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Ohio State UniversityCure SMAActive, not recruitingSpinal Muscular AtrophyUnited States
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Clinic for Special ChildrenGenentech, Inc.Active, not recruitingSpinal Muscular AtrophyUnited States
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University of UtahAbbott; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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Novartis PharmaceuticalsCompleted
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NYU Langone HealthWinthrop University HospitalWithdrawnSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheCompletedSpinal Muscular AtrophyUnited States
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National Institute of Neurological Disorders and...Completed
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Columbia UniversityCompletedSpinal Muscular AtrophyUnited States
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Stanford UniversityCompletedA Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy PatientsMuscular Atrophy, SpinalUnited States
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Hoffmann-La RocheRecruiting
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Bakri ElsheikhGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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Columbia UniversityThe Spinal Muscular Atrophy FoundationCompleted
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Ohio State UniversityBiogen; Cure SMACompleted
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United BioSource, LLCAveXis, Inc.Approved for marketing
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National Institute of Neurological Disorders and...Terminated
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Columbia UniversityGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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University of UtahCompleted
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Hoffmann-La RocheRecruiting
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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University of UtahEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedSpinal Muscular AtrophyUnited States
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Washington University School of MedicineActive, not recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | Spinal Muscular Atrophy Type IIUnited States, Canada
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Columbia UniversityCompletedSpinal Muscular Atrophy | Neuromuscular DiseaseUnited States
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Hoffmann-La RocheRecruitingSpinal Muscular Atrophy (SMA)Belgium, United States, Croatia, Japan, Netherlands, Spain, Canada, Poland, United Kingdom, Italy, Portugal, Australia
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Scholar Rock, Inc.CompletedNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2United States, Spain, Italy, Netherlands
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Novartis Gene TherapiesCompletedGene Therapy | SMA - Spinal Muscular AtrophyUnited States
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Grand Valley State UniversityActive, not recruitingCerebral Palsy | Spinal Cord Injuries | Spinal Muscular Atrophy | Genetic Disease | Spina Bifida | Development DelayUnited States
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Ohio State UniversityMassachusetts General Hospital; National Institute of Neurological Disorders... and other collaboratorsCompletedSpinal Muscular Atrophy (SMA)United States
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WestatNational Institute of Neurological Disorders and Stroke (NINDS)TerminatedSpinal Muscular Atrophy Type IUnited States
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BiogenCompleted
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Massachusetts General HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknownSpinal Muscular AtrophyUnited States
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BiogenCompleted
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BiogenCompleted
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BiogenCompletedSpinal Muscular AtrophyUnited States, Canada
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BiogenCompletedSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheAssociation Française contre les Myopathies (AFM), ParisCompletedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type III Non AmbulantGermany, Italy, France, Belgium, Poland, Netherlands, United Kingdom