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Clinical Trials on Spinal Muscular Atrophy 1
Total 3064 results
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McGill University Health Centre/Research Institute...RecruitingDiabetes Mellitus, Type 1 | Wolfram Syndrome | Neonatal Diabetes | Monogenic Diabetes | Maturity-onset Diabetes in the Young (MODY) | Wolcott-Rallison Syndrome | Mitochondrial DiabetesCanada
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AmgenRecruitingJuvenile Psoriatic Arthritis | Behçet's DiseaseSpain, Turkey, Israel, Greece
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Emory UniversityNational Cancer Institute (NCI); AstraZenecaRecruitingMantle Cell Lymphoma | Marginal Zone Lymphoma | Lymphoplasmacytic Lymphoma | Lymphoproliferative Disorder | Indolent Non-Hodgkin Lymphoma | Grade 1 Follicular Lymphoma | Grade 2 Follicular Lymphoma | Grade 3a Follicular LymphomaUnited States
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AIDS Malignancy ConsortiumNational Cancer Institute (NCI); University of California, Los Angeles; Montefiore... and other collaboratorsActive, not recruitingHuman Immunodeficiency Virus 1 Positive | Skin Kaposi SarcomaUganda, Kenya, Malawi
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Sheba Medical CenterUnknownType I Diabetes Mellitus With Ulcer | Type II Diabetes Mellitus With UlcerIsrael
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The University of Texas Health Science Center,...Society for Pediatric DermatologyCompletedTuberous Sclerosis | Neurofibromatoses | Neurofibroma | AngiofibromaUnited States
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Pharvaris Netherlands B.V.RecruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Puerto Rico
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Pharvaris Netherlands B.V.RecruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Bulgaria, Czechia, Hungary, Spain, France, Germany, Poland, Canada, Israel
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University of Colorado, DenverNational Institute on Aging (NIA)CompletedStroke | Multiple Sclerosis | Glaucoma | Brain Injuries | Macular Degeneration | Arthritis | Chronic Obstructive Pulmonary Disease | Parkinson Disease | Restless Legs Syndrome | Diabetic Retinopathy | Insomnia | Retinitis Pigmentosa | Obstructive Sleep Apnea | Dementia | End Stage Renal Disease | Sleep Apnea | Syncope | Seizures and other conditionsUnited States
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National Institute of Neurological Disorders and...CompletedAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Hereditary Spastic ParaplegiaUnited States
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NYU Langone HealthMichael J. Fox Foundation for Parkinson's ResearchCompletedParkinson Disease | Multiple System Atrophy | REM Sleep Behavior Disorder | Pure Autonomic Failure | Dementia With Lewy BodiesUnited States
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Inozyme PharmaGACI GlobalNot yet recruitingATP-Binding Cassette Subfamily C Member 6 Deficiency | Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
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Chinese University of Hong KongRecruitingCardiovascular Diseases | Stroke | Diabetes Mellitus | Diabetes | Diabetic Angiopathies | Diabetic Retinopathy | Type 1 Diabetes | Diabetic Kidney Disease | Diabetic Nephropathies | Type 2 Diabetes | Coronary Heart DiseaseHong Kong
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AIDS Malignancy ConsortiumNational Cancer Institute (NCI); University of California, Los Angeles; University... and other collaboratorsCompletedHuman Immunodeficiency Virus 1 Positive | AIDS-Related Kaposi SarcomaTanzania
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Assistance Publique - Hôpitaux de ParisCRAT; SNFMI; SFRRecruitingRheumatoid Arthritis | Systemic Lupus Erythematosus | Vasculitis | Myositis | Psoriatic Arthritis | Antiphospholipid Syndrome | Sjogren Syndrome | Spondyloarthritis | Mastocytosis | Scleroderma | Various Autoimmune and/or Systemic and/or Rare DiseasesFrance
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Boston Children's HospitalBoston Children's Hospital - Children's Rare Disease Cohorts InitiativeRecruitingMovement Disorders | Neurodegenerative Diseases | Motor Neuron Disease | Spasticity, Muscle | Pediatric Disorder | Hereditary Spastic ParaplegiaUnited States
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University of PennsylvaniaUnited States Department of Defense; National Institutes of Health (NIH); National... and other collaboratorsRecruitingFrontotemporal Degeneration(FTD) | Primary Progressive Aphasia(PPA) | Familial Frontotemporal Lobar Degeneration (fFTLD) | Amyotrophic Lateral Sclerosis(ALS) | Lewy Body Disease(LBD) | Progressive Supranuclear Palsy(PSP) | Corticobasal Syndrome(CBS) | Posterior Cortical Atrophy(PCA) | Alzheimer's Disease(AD)United States
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National Cancer Institute (NCI)CompletedRecurrent Childhood Medulloblastoma | Recurrent Childhood Ependymoma | Childhood Atypical Teratoid/Rhabdoid Tumor | Childhood Choroid Plexus Tumor | Childhood Craniopharyngioma | Childhood Ependymoblastoma | Childhood Grade I Meningioma | Childhood Grade II Meningioma | Childhood Grade III Meningioma | Childhood High-grade Cerebellar Astrocytoma and other conditionsUnited States
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National Cancer Institute (NCI)CompletedExtranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Small Cleaved Cell Lymphoma | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular Lymphoma and other conditionsUnited States
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Cairo UniversityCompleted
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Rush University Medical CenterCompletedMultiple System Atrophy | Progressive Supranuclear Palsy | Corticobasal Syndrome | Dementia With Lewy Bodies | Atypical Parkinson DiseaseUnited States
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Queen's University, BelfastUniversity of SussexUnknownRetinitis Pigmentosa | Low Vision | Albinism | Stargardt Disease 1 | Stargardt Disease 3 | Stargardt Disease 4United Kingdom
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WepromNot yet recruitingLeukemia, Myeloid, Acute | Metastatic Cancer | Cancer, Rectum | Myelodysplasia | Cancer, Breast | Myeloma | Leukemia, Lymphocytic, Acute | Cancer, Lung | Cancer Colon | Leukemia, Lymphocytic, Chronic | Cancer, Kidney | Cancer Pancreas | Cancer Prostate | Leukemia,Myeloid, Chronic | Cancer OvariesFrance
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Mayo ClinicCompletedMultiple Sclerosis | Rheumatoid Arthritis | Systemic Lupus Erythematosus | Uveitis | Vasculitis | Psoriasis | Graves Disease | Systemic Sclerosis | Celiac Disease | Crohn Disease | Type 1 Diabetes Mellitus | Myasthenia Gravis | Ulcerative Colitis | Dermatomyositis | Polymyositis | Vitiligo | Hepatitis, Autoimmune | Polymyalgia... and other conditionsUnited States
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Istituto Auxologico ItalianoRecruitingCerebrovascular Disorders | Amyotrophic Lateral Sclerosis | Frontotemporal Degeneration | Alzheimer's Disease | Lewy Body DementiaItaly
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)TerminatedMeningioma | Neuroendocrine Neoplasm | Multiple Endocrine Neoplasia Type 1 | Von Hippel-Lindau Syndrome | Metastatic Well Differentiated Neuroendocrine Neoplasm | Somatostatin Positive Neoplastic Cells PresentUnited States
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University Hospital, Strasbourg, FranceRecruitingAlzheimer Disease | Multiple System Atrophy | Frontotemporal Dementia | Dementia With Lewy Bodies | Parkinson's Disease DementiaFrance
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RTI InternationalUniversity of North Carolina, Chapel HillEnrolling by invitationTuberous Sclerosis | Down Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Rett Syndrome | Turner Syndrome | Williams Syndrome | Angelman Syndrome | Chromosome 22q11.2 Deletion Syndrome | Klinefelter Syndrome | Phelan-McDermid Syndrome | Dup15Q Syndrome | Smith Magenis SyndromeUnited States
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National Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Recurrent Childhood Medulloblastoma | Recurrent Childhood Ependymoma | Recurrent Childhood Grade III Lymphomatoid Granulomatosis | Recurrent Childhood Large Cell Lymphoma | Recurrent Childhood Lymphoblastic Lymphoma | Recurrent Childhood Small... and other conditionsUnited States
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Universitätsklinikum Hamburg-EppendorfRecruitingCoronary Disease | Diabetes Mellitus, Type 2 | Breast Neoplasms | Diabetes Mellitus, Type 1 | Pulmonary Disease, Chronic Obstructive | Asthma | Comorbidities and Coexisting ConditionsGermany
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University of IowaCompletedThe Focus of the Study is to Monitor MRI Signal Changes and Inflammatory Biomarkers With Use of Aspirin in Patients With Unruptured Cerebral AneurysmUnited States
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University of Central FloridaRecruitingAutoimmune Diseases | Rheumatoid Arthritis | Fibromyalgia | Psoriatic Arthritis | Sjogren's Syndrome | Diet Habit | Ankylosing Spondylitis | Scleroderma | Rheumatologic Disease | Systemic Lupus Erythematous | Dermatomyositis/PolymyositisUnited States
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Beth Israel Deaconess Medical CenterCompletedStroke | Parkinson's Disease | Myasthenia Gravis | Amyotrophic Lateral Sclerosis (ALS) | MyopathiesUnited States
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NYU Langone HealthRecruitingParkinson Disease | Multiple System Atrophy | Neurogenic Orthostatic Hypotension | REM Sleep Behavior Disorder | Pure Autonomic Failure | Dementia With Lewy Bodies | Patients With Synucleinopathies | Shy-Drager DiseaseKorea, Republic of, United States, Argentina, Spain
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Sheba Medical CenterEnrolling by invitationParkinson Disease | Cerebellar Ataxia | Dystonia | Multiple System Atrophy | Corticobasal Degeneration | Progressive Supranuclear Palsy | Essential Tremor | Dementia With Lewy Bodies | Normal Pressure HydrocephalusIsrael
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University of PennsylvaniaCompletedFrontotemporal Degeneration | Multiple System Atrophy | Progressive Supranuclear PalsyUnited States
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Northwestern UniversityCompletedNeurofibromatosis Type 1 | Neurofibromatosis Type 2 | Adult Ependymoma | Recurrent Adult Brain Tumor | Acoustic Schwannoma | Adult Anaplastic Meningioma | Adult Grade I Meningioma | Adult Grade II Meningioma | Adult Meningeal Hemangiopericytoma | Adult Papillary MeningiomaUnited States
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Augusta UniversityCompletedVascular Diseases | Body Weight Changes | Cardiovascular Abnormalities | HIV-1-infection | Body Fat Disorder | HIV-Associated Lipodystrophy Syndrome | Antiviral Drug Adverse Reaction | Abnormality of Adipose TissueUnited States
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University of FloridaNational Institutes of Health (NIH); National Institute on Deafness and Other...WithdrawnStroke | Dysphagia | Spinocerebellar Ataxia | Dysarthria | Cerebral Stroke
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Momentum DataPfizer; University of SurreyCompletedRheumatoid Arthritis | Inflammatory Bowel Diseases | Crohn Disease | Deep Vein Thrombosis | Ulcerative Colitis | Venous Thromboembolism | Psoriatic Arthritis | Pulmonary Embolism | Venous ThrombosesUnited Kingdom
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Brown UniversityActuate Therapeutics Inc.WithdrawnSarcoma | Soft Tissue Sarcoma | Leiomyosarcoma | High Grade Sarcoma | Liposarcoma | Rhabdomyosarcoma | Angiosarcoma | Bone Sarcoma | Synovial Sarcoma | Undifferentiated Pleomorphic Sarcoma | Metastatic Sarcoma | Myxofibrosarcoma | Spindle Cell SarcomaUnited States
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Children's Hospital Medical Center, CincinnatiPatient-Centered Outcomes Research Institute; Children's Hospital Colorado; Nationwide... and other collaboratorsCompletedWounds and Injuries | Brain Injuries | Craniocerebral Trauma | Trauma, Nervous System | Brain Concussion | Head Injuries, Closed | Head Injury | Brain Edema | Disorders of Environmental Origin | Brain Hemorrhage, Traumatic | Subdural Hematoma | Epidural Hematoma | Intracranial Edema | Tbi | Cortical ContusionUnited States
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National Cancer Institute (NCI)TerminatedNodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Lymphoblastic Lymphoma | Recurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Mantle Cell Lymphoma | Recurrent Marginal Zone... and other conditionsUnited States
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Memorial Sloan Kettering Cancer CenterPfizer; Dana-Farber Cancer Institute; University of Pittsburgh; University of VirginiaCompletedNeurofibromatosis | Meningioma | CNS Cancer | Hemangioblastoma | Intracranial HemangiopericytomaUnited States
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Beth Israel Deaconess Medical CenterRecruitingParkinson's Disease | Parkinsonian Disorders | Multiple System Atrophy | Corticobasal Degeneration | Progressive Supranuclear Palsy | Huntington Disease | Atypical Parkinson Disease | Gait, FrontalUnited States
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New York Stem Cell Foundation Research InstituteLaser and Skin Surgery Center of New YorkActive, not recruitingMacular Degeneration | Cancer | Diabetes Mellitus, Type 1 | Parkinson Disease | Alzheimer Disease | ALS | Huntington DiseaseUnited States
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National Cancer Institute (NCI)CompletedRecurrent Childhood Medulloblastoma | Recurrent Childhood Ependymoma | Childhood Atypical Teratoid/Rhabdoid Tumor | Extra-adrenal Paraganglioma | Childhood Choroid Plexus Tumor | Childhood Craniopharyngioma | Childhood Ependymoblastoma | Childhood Grade I Meningioma | Childhood Grade II Meningioma | Childhood... and other conditionsUnited States, Canada
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National Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Recurrent Childhood Medulloblastoma | Recurrent Childhood Ependymoma | Childhood Chronic Myelogenous Leukemia | Recurrent Childhood Acute Lymphoblastic Leukemia | Recurrent Childhood Acute Myeloid Leukemia | Relapsing Chronic Myelogenous Leukemia and other conditionsUnited States
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University of PittsburghNational Institute on Disability, Independent Living, and Rehabilitation...CompletedCerebral Palsy | Amyotrophic Lateral Sclerosis | Traumatic Brain Injury | Speech Disorders | Brain Stem StrokeUnited States
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Duke UniversityCompletedHead Injuries, Closed | Head Trauma | Head Injuries | Craniocerebral Injuries | Crushing Skull Injury | Head Injuries, Multiple | Head Trauma,Closed | Head Trauma Injury | Head Trauma, Penetrating | Head Injury, Minor | Head Injury Major | Head Injury, Open | Injuries, Craniocerebral | Injuries, Head | Multiple Head... and other conditionsUnited States