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Clinical Trials on Steroid Metabolism, Inborn Errors
Total 4351 results
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Pharming Technologies B.V.CompletedHereditary AngioedemaUnited States, Bulgaria, Canada, Hungary, Israel, Italy, Macedonia, The Former Yugoslav Republic of, Poland, Romania, Serbia, South Africa
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Ferring PharmaceuticalsCompletedHyperphagia in Prader-Willi SyndromeUnited States
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CSL BehringCompletedHereditary AngioedemaUnited States, Canada
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CSL BehringCompletedHereditary AngioedemaBulgaria, United States, Poland, Spain, Hungary, United Kingdom, Russian Federation, Macedonia, The Former Yugoslav Republic of, Argentina, Australia, Canada, Czech Republic, Israel, Romania, Sweden
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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Oslo University HospitalCompletedHereditary Factor VIII Deficiency Disease With InhibitorNorway
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University of RochesterCompletedMyotonic Muscular Dystrophy
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Ionis Pharmaceuticals, Inc.RecruitingHereditary AngioedemaUnited States, Puerto Rico, Belgium, Bulgaria, Canada, France, Germany, Israel, Italy, Netherlands, Poland, Spain, Turkey, United Kingdom
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University Hospital, LilleRecruitingDiabetes | Myotonic Dystrophy 1 | Carbohydrate IntoleranceFrance
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Intellia TherapeuticsEnrolling by invitationHereditary AngioedemaFrance, New Zealand, United Kingdom, Netherlands
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BioMarin PharmaceuticalActive, not recruitingHereditary Angioedema | HAESpain, United States, Australia
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Pharming Technologies B.V.CompletedHereditary AngioedemaIsrael, Italy, United States, Czechia, Germany, Hungary, Poland, Romania, Slovakia, North Macedonia
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Astria Therapeutics, Inc.Completed
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, France, Netherlands, Spain, United Kingdom, Belgium, Bulgaria, Canada, Denmark, Germany, Israel, Italy, Poland, Turkey
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CSL BehringCompletedHereditary AngioedemaUnited States, Germany, Japan, Hungary, Canada, Netherlands, Israel
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TakedaCompletedHereditary AngioedemaBelgium, Bulgaria, Estonia, Spain, Hungary, Israel, Germany, Czechia, Portugal, Greece, Lithuania, Poland, Latvia, Croatia, Slovakia, Austria, Canada, Ireland, North Macedonia, Romania, Serbia, Slovenia
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TakedaCompletedHereditary AngioedemaJapan
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ShireTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, France, Netherlands, Spain, Hungary, Italy, Canada, Poland, Japan, Germany
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University Hospital, ToulouseCompletedPrader-Willi SyndromeFrance
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Nova Scotia Health AuthorityAtlantic Provinces Dermatology AssociationCompletedFamilial Cold UrticariaCanada
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CSL BehringCompletedHereditary AngioedemaCanada, Australia, Germany, United States, Israel
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ShireCompletedHereditary AngioedemaUnited States, Canada, Germany, Hungary, Spain
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TakedaCompletedHereditary AngioedemaJapan
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CENTOGENE GmbH RostockTerminated
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited Kingdom
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AO GENERIUMWithdrawnHereditary AngioedemaRussian Federation
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ShireCompletedHereditary AngioedemaUnited States
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ShireCompletedHereditary AngioedemaUnited States
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ShireCompletedHereditary AngioedemaUnited States, Australia, Israel, Canada, Hungary, Romania, Russian Federation, South Africa, Ukraine
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ShireCompletedHereditary AngioedemaItaly
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ShireCompletedHereditary AngioedemaUnited States
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AO GENERIUMCompletedHereditary AngioedemaRussian Federation
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Universitas PadjadjaranHasan Sadikin General HospitalCompletedVitamin D Deficiency | Tuberculosis | ThalassemiaIndonesia
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BioCryst PharmaceuticalsTerminatedHereditary Angioedema | HAEFrance, Belgium
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaGermany, United Kingdom
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BioCryst PharmaceuticalsCompletedHereditary AngioedemaUnited Kingdom
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Johns Hopkins UniversityTerminated
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Federal University of São PauloCSL BehringCompletedCommon Variable Immunodeficiency | AgammaglobulinemiaBrazil
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy | Kennedys DiseaseUnited States
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M.D. Anderson Cancer CenterRecruitingLynch Syndrome | Hereditary Nonpolyposis Colorectal CancerUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedHigh-Frequency Microsatellite Instability | Mismatch Repair Gene Mutation | Mutation-Negative Lynch Syndrome | Mutation-Positive Lynch SyndromeUnited States
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Johann Wolfgang Goethe University HospitalUnknownAtaxia TelangiectasiaGermany
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PYC TherapeuticsRecruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia
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Centre Leon BerardWithdrawnMyelodysplastic Syndromes | Severe Combined Immunodeficiency | Acute Leukemia | Haematological Malignancy | Hemoglobinopathy in Children | Bone Marrow AplasiaFrance
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University Hospital, LilleCompleted
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Joanne JeterNational Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Colon Adenoma | Colon Carcinoma | MLH1 Gene Mutation | MSH2 Gene MutationUnited States
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National Institute of Neurological Disorders and...CompletedMotor Neuron DiseaseUnited States
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Jose Luis Urcelay SeguraUnknownAmyotrophic Lateral SclerosisSpain
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Premier Specialists, AustraliaUnknownEpidermolysis Bullosa Simplex | Epidermolysis Bullosa Simplex Kobner | Weber-Cockayne SyndromeAustralia
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Johann Wolfgang Goethe University HospitalUnknownGrowth Failure | Ataxia TelangiectasiaGermany