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Clinical Trials on Syndrome d'immunodéficience hyper-IgM, type 1
Total 478 results
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University Hospital, Basel, SwitzerlandRecruiting
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Massachusetts General HospitalJohns Hopkins UniversityRecruitingNeurofibromatosis 1United States
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University of ArkansasRecruitingNeurofibromatosis 1United States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingNeurofibromatosis 1United States
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The University of Texas Health Science Center,...Texas Neurofibromatosis FoundationCompletedNeurofibromatosis 1United States
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Juha PeltonenUnknownNeurofibromatosis 1
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Mayo ClinicCompletedNeurofibromatosis
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Lund UniversityUnknownDiabetes Mellitus, Type 1 | Celiac Disease in Children | RemissionSweden
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Stanford UniversityJohns Hopkins University; University of California, San FranciscoRecruitingNeurofibromatosis 1United States
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National Cancer Institute (NCI)RecruitingNeurofibromatosis 1United States
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Children's Hospital Medical Center, CincinnatiUnited States Department of DefenseRecruitingNeurofibromatosis 1United States
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NobelpharmaTerminated
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Harry T Whelan, MDCompletedNeurofibromatosesUnited States
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University of ManchesterCompletedNeurofibromatosis 1United Kingdom
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Massachusetts General HospitalThe Children's Tumor FoundationCompletedNeurofibromatosesUnited States
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Assistance Publique - Hôpitaux de ParisFrench National Referral Center for NeurofibromatosesUnknown
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M.D. Anderson Cancer CenterCompleted
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Centre Hospitalier Universitaire DijonRecruiting
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Massachusetts General HospitalJohns Hopkins UniversityRecruitingNeurofibromatosis 1United States
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Masonic Cancer Center, University of MinnesotaRecruiting
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Spectrum Health HospitalsCompleted
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University of ManchesterCompletedNeurofibromatosis 1United Kingdom
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University of California, Los AngelesCompletedNeurofibromatosis 1United States
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Pharvaris Netherlands B.V.Active, not recruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Poland, Germany, Austria, Bulgaria, Canada, Ireland, Italy, United Kingdom
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Pharvaris Netherlands B.V.CompletedHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsBulgaria, United States, Spain, Israel, Germany, Canada, Czechia, France, Hungary, Italy, Netherlands, Poland, United Kingdom
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Washington University School of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedDiabetes Mellitus | Type 1 Diabetes | Diabetes Insipidus | Wolfram SyndromeUnited States
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Fundacion para la Investigacion Biomedica del Hospital...University of Alcala; Hospital Universitario Ramon y Cajal; Instituto de Salud... and other collaboratorsRecruitingPolycystic Ovary Syndrome | Hyperandrogenism | Type 1 Diabetes | Hirsutism | Oligomenorrhea | Ovulation DisorderSpain
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National Cancer Institute (NCI)CompletedParents of Children With Cancer | Parents of Children With NF1 | Parents of Children With Neurofibromatosis Type IUnited States, Canada
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Assistance Publique - Hôpitaux de ParisNational Research Agency, FranceCompletedRheumatoid Arthritis | Uveitis | Vasculitis | Type 1 Diabetes | Crohn's Disease | Myositis | Healthy Volunteer | Ankylosing Spondylitis | FMF | Systemic Lupus Erythematosus/Antiphospholipid Syndrome | Cryopyrin-Associated Periodic Syndromes /TNF-receptor Associated Periodic Syndrome | Ulcerative Rectocolitis | Unclassified...France
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National Cancer Institute (NCI)Not yet recruitingNeurofibromatosis 1 | Nerve Sheath NeoplasmsUnited States
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Shanghai Kechow Pharma, Inc.RecruitingNeurofibromatosis 1 | Plexiform NeurofibromasChina
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National Cancer Institute (NCI)RecruitingNeurofibromatosis 1 | Plexiform NeurofibromasUnited States
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National Cancer Institute (NCI)CompletedNeurofibromatosis 1 | Neurofibroma, PlexiformUnited States
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Indiana UniversityWithdrawnNeurofibroma, PlexiformUnited States
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Shenzhen Geno-Immune Medical InstituteShenzhen Children's Hospital; Shenzhen Hospital of Southern Medical UniversityUnknown
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AstraZenecaNot yet recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform
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Massachusetts General HospitalJohns Hopkins UniversityNot yet recruitingNeurofibromatosis 1 | Neurofibromas, CutaneousUnited States
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University of Wisconsin, MilwaukeeNF Midwest; NF NortheastRecruitingSocial Skills | Neurofibromatosis 1United States
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NFlection Therapeutics, Inc.CompletedNeurofibromatosis 1 | Cutaneous NeurofibromaUnited States
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Yale UniversityThe Hospital for Sick Children; United States Department of Defense; Connecticut...CompletedChronic Pain | Neurofibromatosis 1United States
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NFlection Therapeutics, Inc.CompletedNeurofibromatosis 1 | Cutaneous NeurofibromaUnited States
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National Cancer Institute (NCI)CompletedNeurofibromatosis 1United States
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Fundação Educacional Serra dos ÓrgãosCompletedNeurofibromatosis 1 | Cutaneous NeurofibromaBrazil
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Kent RobertsonCompletedNeurofibromatosis | NeurofibromasUnited States
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Indiana UniversityCompleted
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National Institute of Diabetes and Digestive and...RecruitingPrimary Hyperparathyroidism | Pseudohypoparathyroidism | Parathyroid Cancer | Inheritable Bone Diseases | Multiple Endocrine Neoplasia, Type 1United States
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Johns Hopkins UniversityNeurofibromatosis Therapeutic Acceleration ProgramRecruitingCutaneous Neurofibroma | NF1 | MonotherapyUnited States
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Massachusetts General HospitalUnited States Department of DefenseRecruiting