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Clinical Trials on Syndrome de Bardet-Biedl 1
Total 811 results
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University Hospital, MontpellierCHU de la Timone, Marseille, France; CHU Carémeau, Nîmes, France; CHU de Bordeaux... and other collaboratorsRecruiting
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)SuspendedLiver Diseases | Alpha 1-Antitrypsin Deficiency | Alagille SyndromeUnited States, Canada
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Vanderbilt UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingNeurofibromatosis Type 1 | Reading Disability | NF1 | Learning DisabilityUnited States
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Recurrent Childhood Pilocytic Astrocytoma | Recurrent Childhood Visual Pathway GliomaUnited States, Canada, Australia, New Zealand
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedChronic Myelomonocytic Leukemia | Fanconi Anemia | Childhood Acute Erythroleukemia (M6) | Childhood Acute Megakaryocytic Leukemia (M7) | Childhood Acute Monoblastic Leukemia (M5a) | Childhood Acute Monocytic Leukemia (M5b) | Childhood Acute Myeloblastic Leukemia With Maturation (M2) | Childhood Acute... and other conditionsUnited States
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University of UlmDiaMed GmbHRecruiting
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Centre Hospitalier Régional d'OrléansImmunologie et Neurogénétique Expérimentales et Moléculaires (INEM)WithdrawnInflammation | Guillain-Barre Syndrome | Sclerosis, MultipleFrance
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White Plains HospitalActive, not recruitingPancreatic Cancer | Pancreatic Adenocarcinoma | Lynch Syndrome | Pancreas Cancer | HNPCC | Familial Pancreatic Cancer | Hereditary Pancreatitis | BRCA 1/2 | FAMMM | Familial Atypical Multiple Mole Melanoma | Peutz Jeghers SyndromeUnited States
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National Cancer Institute (NCI)CompletedChronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Inv(16)(p13;q22) | Adult Acute Myeloid Leukemia With t(16;16)(p13;q22) | Adult Acute Myeloid Leukemia With t(8;21)(q22;q22) and other conditionsUnited States
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University of North Carolina, Chapel HillNational Institute on Drug Abuse (NIDA); National Institute of Mental Health...CompletedHIV Infections | HIV-1United States, Puerto Rico
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Tibotec Pharmaceuticals, IrelandCompletedHIV Infections | HIV-1United States, France, Spain, Canada, South Africa, Argentina, Brazil, Romania
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Ruth M. Rothstein CORE CenterVircoUnknownHIV Infections | HIV-1United States
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University of Sao Paulo General HospitalUnknownHeart Failure | Chest Pain | Syncope | Pulmonary Embolism | Pulmonary Edema | Acute Coronary Syndromes | Aortic Aneurysm, Familial Thoracic 1Brazil
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National Cancer Institute (NCI)Children's Oncology GroupActive, not recruitingJuvenile Myelomonocytic Leukemia | Neurofibromatosis Type 1United States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedBrain and Central Nervous System Tumors | Neurofibromatosis Type 1Canada, United States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Tibotec Pharmaceuticals, IrelandCompletedHIV Infections | HIV-1United States, France, United Kingdom, China, Belgium, Germany, Spain, Chile, Mexico, Portugal, Costa Rica, Panama, South Africa, Canada, Brazil, Puerto Rico, Russian Federation, Thailand, Australia, India
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Merck Sharp & Dohme LLCNational Institute of Allergy and Infectious Diseases (NIAID); HIV Vaccine...Completed
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Merck Sharp & Dohme LLCCompleted
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Medical Research CouncilEuropean and Developing Countries Clinical Trials Partnership (EDCTP)Completed
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Medical Research CouncilEuropean and Developing Countries Clinical Trials Partnership (EDCTP)Unknown
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National Taiwan University HospitalUnknown
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Prof. Dr. Fridoon Jawad AhmadUniversity of Lahore; Bahria International HospitalUnknownNeurokinin 1 Receptor, Substance P, Respiratory Illness, Inflammation, Covid-19, CoronavirusPakistan
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University of HawaiiTobira Therapeutics, Inc.CompletedAIDS Dementia Complex | Human Immunodeficiency Virus | HIV-1-Associated Cognitive Motor ComplexUnited States
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Fundacion para la Investigacion Biomedica del Hospital...Merck Sharp & Dohme LLCCompleted
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International Partnership for Microbicides, Inc.CompletedHIV Infections | HIV-1Belgium
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Spartanburg Regional Healthcare SystemEdward Via Virginia College of Osteopathic MedicineCompletedEncephalitis | Meningitis | Subarachnoid Hemorrhage | Intracranial Neoplasm | Guillain-Barré | Intracranial CNS DisorderUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)RecruitingAcute Lymphoblastic Leukemia | Acute Leukemia | Blastic Plasmacytoid Dendritic Cell Neoplasm | Acute Leukemia of Ambiguous Lineage | Acute Undifferentiated Leukemia | Acute Biphenotypic Leukemia | Myelodysplastic Syndrome With Excess Blasts-1 | Mixed Phenotype Acute Leukemia | Blasts Under 5 Percent... and other conditionsUnited States
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Boston Children's HospitalCompletedAML | ALL | Biphenotypic Leukemia | Refractory Anemia | Refractory Cytopenia With Multilineage Dysplasia | Refractory Anemia With Ringed Sideroblasts | Undifferentiated Leukemia | Ref. Cytopenia w Multilineage Dysplasia & Ringed Sideroblasts | Refractory Anemia With Excess Blasts-1 (5-10% Blasts) | Refractory... and other conditionsUnited States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Samsung Medical CenterNot yet recruitingCharcot-Marie-Tooth Disease, Type 1
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National Human Genome Research Institute (NHGRI)RecruitingMetabolic Disease | Purine-Pyrimidine Metabolism | AICDA, OMIM *605257, Immunodeficiency With Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A<TAB>, OMIM *606224, Anemia, Hemolytic, Due to UMPH1 Deficiency | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064,... and other conditionsUnited States
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The Hospital for Sick ChildrenCompletedDiabetes Mellitus, Type 1 | Celiac Disease | CeliacCanada
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The Hospital for Sick ChildrenCompletedDiabetes Mellitus, Type 1 | Celiac DiseaseCanada
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Swiss Federal Institute of TechnologyUniversity of ZurichTerminated
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Cairo UniversityRecruitingGuillain-Barre SyndromeEgypt
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Massachusetts General HospitalJohns Hopkins UniversityRecruitingNeurofibromatosis 1United States
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University of ArkansasRecruitingNeurofibromatosis 1United States
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Children's Hospital Medical Center, CincinnatiActive, not recruitingNeurofibromatosis 1United States
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The University of Texas Health Science Center,...Texas Neurofibromatosis FoundationCompletedNeurofibromatosis 1United States
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Juha PeltonenUnknownNeurofibromatosis 1
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Mayo ClinicCompletedNeurofibromatosis
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Nohla Therapeutics, Inc.National Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedAdult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities | Adult Acute Myeloid Leukemia With Del(5q) | Adult Acute Myeloid Leukemia With Inv(16)(p13;q22) | Adult Acute Myeloid Leukemia With t(16;16)(p13;q22) | Adult Acute Myeloid Leukemia With t(8;21)(q22;q22) | Adult Acute Myeloid Leukemia... and other conditionsUnited States
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | HIV-1 | AIDS VaccinesUnited States
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Stanford UniversityJohns Hopkins University; University of California, San FranciscoRecruitingNeurofibromatosis 1United States
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National Cancer Institute (NCI)RecruitingNeurofibromatosis 1United States
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Children's Hospital Medical Center, CincinnatiUnited States Department of DefenseRecruitingNeurofibromatosis 1United States
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NobelpharmaTerminated
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Harry T Whelan, MDCompletedNeurofibromatosesUnited States