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Clinical Trials on Talasemia, Beta
Total 569 results
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Tanta UniversityUnknownStudy of The Therapeutic Benefits of Al-hijamah in Children With Beta Thalassemia Major (Al-hijamah)AL-Hijama in Thalassmia MajorEgypt
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M.D. Anderson Cancer CenterWithdrawnSickle Cell Disease | Sickle Beta Thalassemia | Beta Thalassemia Major | Sickle Cell-SS Disease | Sickle Beta 0 Thalassemia | Sickle Beta Plus ThalassemiaUnited States
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CelgeneTerminatedBeta Thalassemia Intermedia | Beta Thalassemia MajorFrance, United Kingdom, Italy, Greece
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University of British ColumbiaCompletedSickle Cell Disease | Beta-Thalassemia | Sickle Cell Trait | Sickle Cell-Beta Thalassemia | Sickle Cell-SS DiseaseCanada, Nepal
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Editas Medicine, Inc.RecruitingHemoglobinopathies | Thalassemia Major | Thalassemia Intermedia | Transfusion Dependent Beta ThalassemiaUnited States, Canada
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Children's Hospital of PhiladelphiaNot yet recruiting
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Bristol-Myers SquibbRecruiting
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Assiut UniversityRecruiting
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CelgeneAcceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway...RecruitingBeta-ThalassemiaUnited States, Turkey, Italy, Thailand, Germany, Greece, China, India, Lebanon
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, United Kingdom, Canada, Germany, Italy
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityEnrolling by invitation
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Rare Partners srl Impresa SocialeUniversità degli Studi di FerraraCompletedBeta-ThalassemiaItaly
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Acceleron Pharma Inc. (a wholly owned subsidiary...Completed
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University Hospital of PatrasCompleted
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IRCCS San RaffaeleOrchard Therapeutics; Fondazione TelethonUnknown
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Hoffmann-La RocheCompletedBeta-ThalassemiaItaly, Lebanon, Thailand
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Prolong PharmaceuticalsCompleted
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Shenzhen Geno-Immune Medical InstituteUnknown
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI); George Papanicolaou HospitalCompletedBeta-ThalassemiaGreece
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Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
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Aga Khan UniversityCompletedBeta Thalassemia Major
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China Medical University HospitalCompleted
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Agios Pharmaceuticals, Inc.Active, not recruitingTransfusion-dependent Alpha-Thalassemia | Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United States, France, Canada, Malaysia, Germany, Netherlands, Bulgaria, United Kingdom, Turkey, Italy, Greece, United Arab Emirates, Brazil, Denmark, Lebanon, Saudi Arabia
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Lantu BiopharmaNot yet recruitingBeta-Thalassemia
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingBeta-ThalassemiaUnited States
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Children's Hospital of Fudan UniversityCorrectSequence Therapeutics Co., LtdRecruiting
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Assiut UniversityNot yet recruiting
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityActive, not recruiting
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bluebird bioCompletedBeta-ThalassemiaUnited States, Germany, United Kingdom, France, Greece, Italy
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bluebird bioCompletedBeta-ThalassemiaFrance, United Kingdom, United States, Thailand, Italy, Germany
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI); Genzyme, a Sanofi Company; George Papanicolaou HospitalCompleted
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Boston UniversityCompletedBeta-ThalassemiaUnited States, United Kingdom
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Royal Brompton & Harefield NHS Foundation TrustCORDA, The Heart Charity; Apotex Inc.; The Cooley's Anemia Foundation,; The UK...UnknownBeta-ThalassemiaItaly
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Vifor (International) Inc.Labcorp Corporation of America Holdings, IncCompletedBeta-Thalassemia | Non-transfusion-dependent ThalassemiaGreece, Israel, Italy, Lebanon, Thailand
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Institute of Hematology & Blood Diseases HospitalR&D Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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First Affiliated Hospital of Guangxi Medical UniversityGenmedicn Biopharma Ltd.RecruitingTransfusion Dependent Beta-ThalassemiaChina
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Agios Pharmaceuticals, Inc.Active, not recruitingNon-Transfusion-dependent Alpha-Thalassemia | Non-Transfusion-dependent Beta-ThalassemiaSpain, Taiwan, Thailand, United Kingdom, Malaysia, United States, Netherlands, Bulgaria, Turkey, Italy, Canada, Brazil, France, United Arab Emirates, Denmark, Greece, Lebanon, Saudi Arabia
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National Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationSickle Cell Anemia | Sickle Beta Thalassemia | Sickle Cell Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Pain | Hbss | Hbsc | Sickle Cell Syndrome VariantUnited States
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Università degli Studi di FerraraAzienda Ospedaliero, Universitaria Pisana; Rare Partners srl Impresa Sociale; Azienda Ospedaliero, Universitaria MeyerRecruitingBeta-ThalassemiaItaly
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National Institute of Blood and Marrow Transplant...Completed
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Vifor (International) Inc.Labcorp Drug Development IncWithdrawnBeta-ThalassemiaUnited States, Bulgaria, Israel
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Dr.Saqib Hussain AnsariUnknownThalassemia, BetaPakistan
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Xiaofang SunNanfang Hospital of Southern Medical University; Third Affiliated Hospital,... and other collaboratorsUnknownBeta-Thalassemia
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Boston UniversityMahidol UniversityCompletedBeta Thalassemia IntermediaThailand
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EmeraMedCompletedBeta Thalassemia MajorAlbania