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Clinical Trials on Telomere Biology Disorders With Bone Marrow Failure in New Zealand
Total 565 results
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The University of QueenslandRecruitingPulmonary Fibrosis | Dyskeratosis Congenita | Telomere Shortening | Telomere DiseaseAustralia
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Columbia UniversityTerminatedLymphoma | Leukemia | Histiocytosis | Bone Marrow Failure Syndromes | ImmunodeficienciesUnited States
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Memorial Sloan Kettering Cancer CenterRecruitingAplastic Anemia | Cytopenia | Hypocellular MarrowUnited States
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Merck Sharp & Dohme LLCRecruitingPrimary Myelofibrosis | Polycythemia Vera | Thrombocythemia, Essential | Myelofibrosis | Post-polycythemia Vera Myelofibrosis | Post-essential Thrombocythemia MyelofibrosisAustralia, New Zealand
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Memorial Sloan Kettering Cancer CenterRecruitingHemoglobinopathies | AML | MDS | Bone Marrow Failure | ALL | Inherited Metabolic Disorders | HLH | MPD Withou Myelofibrosis | NHL or HLUnited States
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Washington University School of MedicineRecruitingHemoglobinopathies | Bone Marrow Failure Syndromes | Metabolic Disorders | Non-malignant Disorders | Severe Sickle Cell Disease | Immunologic DisordersUnited States
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedAnemia, AplasticUnited States
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Roswell Park Cancer InstituteCompleted
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Feinstein Institute for Medical ResearchDiamond Blackfan Anemia Foundation, Inc.Recruiting
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Cellphire Therapeutics, Inc.Department of Health and Human ServicesCompletedHematologic Diseases | Thrombocytopenia | Bone Marrow AplasiaUnited States, Norway
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Memorial Sloan Kettering Cancer CenterActive, not recruiting
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Michael Pulsipher, MDActive, not recruitingSevere Aplastic AnemiaUnited States
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health... and other collaboratorsRecruitingSevere Aplastic AnemiaUnited States
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Columbia UniversityUnknownSevere Combined Immunodeficiency | Fanconi Anemia | Bone Marrow Failure | OsteopetrosisUnited States
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Northwell HealthTerminatedDiamond Blackfan AnemiaUnited States
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedSevere Aplastic AnemiaUnited States
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Adrianna Vlachos, MDTerminatedPure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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Novartis PharmaceuticalsActive, not recruitingAplastic AnemiaThailand, Russian Federation, Portugal, United Kingdom, Hong Kong, United States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Miltenyi Biotec, Inc.Completed
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsRecruitingCongenital Amegakaryocytic Thrombocytopenia | Paroxysmal Nocturnal Hemoglobinuria | Shwachman-Diamond Syndrome | Bone Marrow Failure Syndrome | Congenital Pure Red Cell Aplasia | Hereditary Sideroblastic Anemia | Hematologic Neoplasm With Germline GATA2 Mutation | Hematologic Neoplasm With Germline... and other conditionsUnited States
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Memorial Sloan Kettering Cancer CenterBoston Children's Hospital; Fred Hutchinson Cancer Center; Children's Hospital... and other collaboratorsCompletedLeukemia | Myelodysplastic Syndrome | Aplastic AnemiaUnited States
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New York Medical CollegeCompletedLymphoma | Leukemia | Sickle Cell Disease | Histiocytosis | Immunodeficiencies | Inborn Errors of Metabolism | Bone Marrow Failure | Beta ThalassemiaUnited States
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Northwell HealthCompletedPure Red Cell Aplasia | Diamond Blackfan Anemia | Blackfan Diamond Syndrome | DBA | Congenital Hypoplastic AnemiaUnited States
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ReVivo Medical, Corp.The Cleveland Clinic; Albany Medical College; IGEARecruitingNeck Pain | Spondylosis | Spondylosis With Myelopathy | Spondylosis With Radiculopathy | Spondylosis With Radiculopathy Cervical Region | Intervertebral Disc Disorder CervicalUnited States
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University of Auckland, New ZealandLeukaemia & Blood Cancer New ZealandActive, not recruiting
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AlexionAchillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal HemoglobinuriaNew Zealand, Korea, Republic of, Italy
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Washington University School of MedicineSt. Louis Children's HospitalRecruitingHemoglobinopathies | Metabolic Disorders | Hematologic, Immune, or Bone Marrow Disorders | Non-malignant DisordersUnited States, Canada
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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Weill Medical College of Cornell UniversityBristol-Myers SquibbTerminated
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Boston Children's HospitalMassachusetts General Hospital; Mayo Clinic; Karolinska University Hospital; Baylor... and other collaboratorsActive, not recruitingAplastic Anemia | Dyskeratosis Congenita | Hoyeraal Hreidarsson Syndrome | Revesz SyndromeUnited States, Norway, Sweden
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Children's Hospital Medical Center, CincinnatiMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer CenterRecruitingFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Severe Marrow FailureUnited States
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaHong Kong, Thailand, New Zealand, Malaysia
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Weill Medical College of Cornell UniversityCompleted
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New York Blood CenterTerminatedLymphoma | Leukemia | Myelodysplasia | Genetic Disease | Severe Aplastic AnemiaUnited States
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
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Novartis PharmaceuticalsCompletedMyelofibrosis | Sickle Cell Disease | Thalassemia | Diamond Blackfan AnemiaUnited States, Netherlands, Taiwan, Thailand, Italy, Germany, Spain, Canada, Belgium, Greece, Turkey, United Kingdom
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Novartis PharmaceuticalsTerminatedMyelofibrosis With High Molecular Risk MutationsBelgium, Spain, United Kingdom, Hungary, Italy, Japan, Taiwan, Germany, Canada, Singapore, Austria, Australia, France, Israel, Sweden, Switzerland, Hong Kong, Greece, Turkey, Brazil, Russian Federation, Denmark, Portugal, Norway, Poland
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Beth Israel Medical CenterCompletedImmune Thrombocytopenia | Myelodysplasia | Chemotherapy Induced Thrombocytopenia | Aplastic AnaemiaUnited States
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor ConsortiumTerminatedFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States
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University of RochesterRecruitingLymphoma | Myelodysplastic Syndromes | Multiple Myeloma | Solid Tumor | Acute Leukemia | Aplastic Anemia | Chronic Leukemia | Immune Deficiency Disorder | Congenital Hematological Disorder | Metabolism DisorderUnited States
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Impulse DynamicsRecruitingHeart Failure | Heart Failure With Preserved Ejection Fraction | Diastolic Heart Failure | Heart Failure With Mid Range Ejection Fraction | Heart Failure With Moderately Reduced Ejection FractionUnited States
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Lahey ClinicPatient-Centered Outcomes Research InstituteActive, not recruitingCervical Spondylosis With MyelopathyUnited States, Canada
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Novartis PharmaceuticalsCompletedPolycythemia Vera (PV)United States
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CelgeneCompletedMyelofibrosis | Myeloid Metaplasia | Myelofibrosis With Myeloid MetaplasiaUnited States, Italy, United Kingdom, Austria, Spain
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ExelixisTerminated
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CephalonCompletedPolycythemia Vera | Essential ThrombocytosisUnited States
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PharmaEssentiaRecruitingPolycythemia VeraUnited States, Canada
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Icahn School of Medicine at Mount SinaiThe Leukemia and Lymphoma SocietyCompletedPolycythemia Vera | Essential ThrombocythemiaUnited States
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States