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Clinical Trials on Tetrahydrobiopterin Deficiencies in Italy
Total 172 results
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Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated Amyloidosis | ATTR AmyloidosisIsrael, Italy, Netherlands, Spain, United States, France, Denmark, Germany, Portugal, Brazil, Taiwan
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Mario Negri Institute for Pharmacological ResearchALS Association; Get out ONLUSCompleted
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Advice Pharma Group srlCompletedAcute Myeloid Leukemia | Multiple Myeloma | Hodgkin Lymphoma | Amyloidosis | Chronic Lymphocytic Leukemia | Chronic Myeloid Leukemia | Treatment Adherence | Myelodysplasia | Lymphocytic Lymphoma | Treatment Adherence and Compliance | T Cell Non-Hodgkin Lymphoma | B-cell Non Hodgkin Lymphoma | Solitary Plasmacytoma and other conditionsItaly
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Prothena Biosciences Ltd.RecruitingLight Chain (AL) AmyloidosisUnited States, Korea, Republic of, Australia, Denmark, France, Italy, Spain, Israel, Taiwan, Austria, Canada, Czechia, Germany, Greece, Hungary, Japan, Netherlands, Poland, Portugal, Turkey, United Kingdom, Belgium, Ireland
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Boston UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Food and Drug...CompletedFamilial Amyloid Polyneuropathy | Familial AmyloidosisUnited States, Italy, Japan, Sweden, United Kingdom
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K-Group Alpha, Inc., a wholly owned subsidiary...Active, not recruitingAL Amyloidosis | AmyloidosisSpain, Australia, Israel, United States, Greece, Italy, Cyprus
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Ionis Pharmaceuticals, Inc.AstraZenecaRecruitingTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)United States, Austria, Belgium, Canada, France, Germany, Israel, Italy, Portugal, Spain, Sweden, United Kingdom, Australia, Greece
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Eidos Therapeutics, a BridgeBio companyActive, not recruitingAmyloid Cardiomyopathy, Transthyretin-RelatedUnited States, Spain, Australia, Canada, Italy, Netherlands, Ireland, New Zealand, Belgium, Israel, Greece, Korea, Republic of, Czechia, Brazil, Denmark, Portugal, United Kingdom
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Humanitas Mirasole SpAKU Leuven; UMC Utrecht; University of Sheffield; Istituto Superiore di Sanità; University... and other collaboratorsActive, not recruitingAmyotrophic Lateral Sclerosis (ALS)United Kingdom, Germany, France, Netherlands, Belgium, Ireland, Italy
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency | Isolated Sulfite Oxidase DeficiencySpain, Israel, United States, United Kingdom, Canada, Netherlands, Germany, Saudi Arabia, Tunisia, Japan, Italy, Malaysia, Poland, Turkey
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Ionis Pharmaceuticals, Inc.RecruitingHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Italy, Portugal, Spain, Taiwan, Sweden, Canada, Brazil, France, New Zealand, Argentina, Cyprus, Australia, Turkey
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Alexion Pharmaceuticals, Inc.RecruitingTransthyretin Amyloid CardiomyopathyUnited States, Spain, United Kingdom, Norway, Israel, China, Korea, Republic of, Belgium, France, Germany, Italy, Japan, Australia, Argentina, Austria, Taiwan, Switzerland, Canada, Sweden, Poland, Denmark, Turkey, Brazil, Netherlands, G... and more
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ZevraDenmarkTerminatedAmyotrophic Lateral SclerosisUnited States, Canada, Netherlands, Belgium, Poland, United Kingdom, France, Germany, Italy, Spain, Sweden
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PfizerTerminatedHeart Failure With Preserved Ejection Fraction | Transthyretin Amyloid CardiomyopathySpain, United States, Japan, Canada, France, Italy, Poland, United Kingdom
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Passage Bio, Inc.RecruitingFrontotemporal Dementia | FTD | Dementia Frontotemporal | FTD-GRNUnited States, Brazil, Italy, Portugal, Canada
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Ferrer Internacional S.A.Julius Clinical; Stichting TRICALS FoundationActive, not recruitingAmyotrophic Lateral SclerosisBelgium, Netherlands, United Kingdom, Spain, Germany, France, Ireland, Italy, Poland, Portugal, Sweden
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Ono Pharmaceutical Co. LtdCompletedAmyotrophic Lateral Sclerosis (ALS)Belgium, France, Germany, Italy, Netherlands, Switzerland, United Kingdom
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Alector Inc.Active, not recruitingFrontotemporal DementiaCanada, United States, Germany, United Kingdom, Italy, Netherlands
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Teva Branded Pharmaceutical Products R&D, Inc.CompletedALSUnited States, Netherlands, Canada, Italy, Spain, Belgium, France, Germany, Hungary, Israel
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Eidos Therapeutics, a BridgeBio companyCompletedHeart Diseases | Amyloidosis | Cardiomyopathies | Transthyretin Amyloidosis | Amyloid CardiomyopathyUnited States, Netherlands, Ireland, Canada, Italy, Spain, Belgium, New Zealand, Israel, Australia, Portugal, Brazil, Poland, Czechia, Denmark, Greece, Korea, Republic of, United Kingdom
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Prothena Biosciences Ltd.TerminatedAL AmyloidosisUnited States, Spain, Australia, Italy, Germany, Austria, Greece, France, Israel, United Kingdom
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BiogenActive, not recruitingAmyotrophic Lateral SclerosisUnited States, Netherlands, Italy, Canada
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Ionis Pharmaceuticals, Inc.Active, not recruitingTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)United States, Australia, Spain, Canada, Germany, Japan, Italy, Israel, Argentina, France, Portugal, Austria, Brazil, Greece, United Kingdom, Czechia, Sweden, Belgium, Denmark, Poland, Puerto Rico
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ZevraDenmarkCompletedAmyotrophic Lateral SclerosisCanada, United States, Belgium, Netherlands, Poland, United Kingdom, France, Germany, Italy, Spain, Sweden, Switzerland
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Ionis Pharmaceuticals, Inc.CompletedHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Spain, Taiwan, Italy, Germany, Argentina, Australia, Brazil, Canada, Cyprus, France, Greece, New Zealand, Portugal, Sweden, Turkey
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Ono Pharmaceutical Co. LtdCompletedAmyotrophic Lateral Sclerosis (ALS)Belgium, France, Austria, Germany, Italy, Netherlands, Switzerland, United Kingdom
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Amylyx Pharmaceuticals Inc.Enrolling by invitationAmyotrophic Lateral SclerosisBelgium, Spain, Netherlands, United Kingdom, Sweden, France, Germany, Ireland, Italy, Poland, Portugal
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Prothena Biosciences Ltd.CompletedAL AmyloidosisUnited States, Spain, Australia, Germany, United Kingdom, France, Greece, Israel, Italy, Austria
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FORUM Pharmaceuticals IncUnknownGranulin MutationBelgium, United States, France, Italy, Netherlands, United Kingdom
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SanofiRecruitingRelapsed/Refractory Multiple Myeloma | Amyloid Light-chain AmyloidosisItaly, Australia, Hungary, United Kingdom, Czechia, Belgium, Spain
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GlaxoSmithKlineCompletedAmyotrophic Lateral SclerosisUnited States, France, Australia, Canada, Belgium, Germany, Korea, Republic of, Japan, Netherlands, Italy, United Kingdom
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AB ScienceRecruitingAmyotrophic Lateral SclerosisFrance, Spain, United States, Sweden, Denmark, Portugal, Italy, Israel, Germany, Norway, Poland, Russian Federation, Slovenia, Ukraine, Greece, Belgium, Serbia
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CytokineticsTerminatedAmyotrophic Lateral SclerosisCanada, United States, Australia, Spain, Belgium, Ireland, Italy, Netherlands, Sweden
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Universitätsklinikum Hamburg-EppendorfCharite University, Berlin, Germany; Deutsches Zentrum für Herz-Kreislauf-Forschung...CompletedIron Deficiency | Systolic Heart FailureGermany, Serbia, Hungary, Italy, Poland, Portugal, Slovenia, Spain
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Apellis Pharmaceuticals, Inc.TerminatedMotor Neuron Disease | Amyotrophic Lateral SclerosisUnited States, Netherlands, Spain, Germany, Japan, Australia, France, Poland, Ukraine, Belgium, Czechia, Ireland, Italy, United Kingdom
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinUnited States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinNew Zealand, United States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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Ionis Pharmaceuticals, Inc.RecruitingAmyotrophic Lateral SclerosisUnited States, Germany, Netherlands, Spain, Korea, Republic of, Canada, Switzerland, Belgium, Italy, United Kingdom, Ireland, Sweden, Taiwan, Brazil
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BiogenIonis Pharmaceuticals, Inc.CompletedAmyotrophic Lateral SclerosisUnited States, Canada, Belgium, France, Australia, Japan, Denmark, Korea, Republic of, United Kingdom, Germany, Italy, Poland
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PTC TherapeuticsActive, not recruitingAmyotrophic Lateral SclerosisUnited States, Belgium, Spain, Australia, Germany, Italy, Czechia, France, Netherlands, Japan, Poland, Argentina, Sweden
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CENTOGENE GmbH RostockActive, not recruitingFrontotemporal DementiaItaly, Spain, Belgium, Turkey, Portugal, Germany, Greece
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Amylyx Pharmaceuticals Inc.Active, not recruitingAmyotrophic Lateral SclerosisUnited States, Belgium, Spain, Netherlands, United Kingdom, Germany, Sweden, France, Ireland, Italy, Poland, Portugal
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Amoneta Diagnostics SASAssistance Publique - Hôpitaux de Paris; University Hospital, Geneva; University... and other collaboratorsUnknownFrontotemporal Lobar Degeneration | Progressive Supranuclear Palsy (PSP) | Dementia With Lewy Bodies (DLB) | Corticobasal Degeneration (CBD) | Alzheimer Disease (AD) | Parkinson Disease Dementia (PDD)Belgium, France, Italy, Switzerland, Turkey
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Denali Therapeutics Inc.TakedaActive, not recruitingFrontotemporal DementiaSpain, Turkey, France, Belgium, Netherlands, Portugal, Italy, Colombia, Czechia, Brazil, United Kingdom, Serbia
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... and other collaboratorsRecruitingALS | Kennedy Disease | MND (Motor Neurone DIsease) | PLS | PMA - Progressive Muscular Atrophy | PBP - Progressive Bulbar PalsyUnited States, Italy
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SanofiTerminatedAmyotrophic Lateral SclerosisNetherlands, China, Poland, Italy, Belgium, United States, Canada, France, Germany, Japan, Spain, Sweden, United Kingdom
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Orion Corporation, Orion PharmaCompletedAmyotrophic Lateral SclerosisCanada, United States, Australia, Austria, United Kingdom, Germany, Finland, Spain, France, Italy, Sweden, Netherlands, Belgium, Ireland
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CytokineticsTerminatedAmyotrophic Lateral SclerosisUnited States, Germany, Spain, Australia, United Kingdom, Canada, France, Belgium, Denmark, Ireland, Italy, Netherlands, Poland, Portugal, Sweden, Switzerland
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CytokineticsCompletedAmyotrophic Lateral SclerosisCanada, United States, Netherlands, France, United Kingdom, Belgium, Germany, Spain, Ireland, Italy, Portugal
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Orion Corporation, Orion PharmaTerminatedAmyotrophic Lateral SclerosisCanada, United States, Australia, Germany, Belgium, Finland, Spain, Austria, Italy, France, Ireland, Netherlands, Sweden, United Kingdom