- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Thalassemia Major
Total 3197 results
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Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
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Vifor (International) Inc.Labcorp Corporation of America Holdings, IncCompletedBeta-Thalassemia | Non-transfusion-dependent ThalassemiaGreece, Israel, Italy, Lebanon, Thailand
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University of British ColumbiaCompletedSickle Cell Disease | Beta-Thalassemia | Sickle Cell Trait | Sickle Cell-Beta Thalassemia | Sickle Cell-SS DiseaseCanada, Nepal
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Columbia UniversityCompletedMyelodysplastic Syndromes | Sickle Cell Disease | Aplastic Anemia | Transfusional Iron Overload | Thalassemia MajorUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationSickle Cell Anemia | Sickle Beta Thalassemia | Sickle Cell Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Pain | Hbss | Hbsc | Sickle Cell Syndrome VariantUnited States
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Cyprus Institute of Neurology and GeneticsRecruitingSickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, BetaUnited States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
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Children's Hospital of PhiladelphiaNot yet recruiting
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Shenzhen HemogenRecruiting
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Shanghai BDgene Co., Ltd.Ruijin HospitalNot yet recruiting
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Bristol-Myers SquibbRecruiting
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Assiut UniversityRecruiting
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CelgeneAcceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway...RecruitingBeta-ThalassemiaUnited States, Turkey, Italy, Thailand, Germany, Greece, China, India, Lebanon
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, United Kingdom, Canada, Germany, Italy
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityEnrolling by invitation
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Rare Partners srl Impresa SocialeUniversità degli Studi di FerraraCompletedBeta-ThalassemiaItaly
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Acceleron Pharma Inc. (a wholly owned subsidiary...Completed
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University Hospital of PatrasCompleted
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IRCCS San RaffaeleOrchard Therapeutics; Fondazione TelethonUnknown
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Hoffmann-La RocheCompletedBeta-ThalassemiaItaly, Lebanon, Thailand
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Prolong PharmaceuticalsCompleted
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Shenzhen Geno-Immune Medical InstituteUnknown
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI); George Papanicolaou HospitalCompletedBeta-ThalassemiaGreece
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Institute of Hematology & Blood Diseases HospitalR&D Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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First Affiliated Hospital of Guangxi Medical UniversityGenmedicn Biopharma Ltd.RecruitingTransfusion Dependent Beta-ThalassemiaChina
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Protagonist Therapeutics, Inc.Completedβ-thalassemia | Ineffective ErythropoiesisMalaysia, Thailand, United States, Greece, United Kingdom, Turkey, Lebanon, Tunisia
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Kind Pharmaceuticals LLCNot yet recruiting
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Shenzhen HemogenRecruiting
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Università degli Studi di FerraraAzienda Ospedaliero, Universitaria Pisana; Rare Partners srl Impresa Sociale; Azienda Ospedaliero, Universitaria MeyerRecruitingBeta-ThalassemiaItaly
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National Institute of Blood and Marrow Transplant...Completed
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Children's Hospital KarachiCompleted
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Vifor (International) Inc.Labcorp Drug Development IncWithdrawnBeta-ThalassemiaUnited States, Bulgaria, Israel
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Dr.Saqib Hussain AnsariUnknownThalassemia, BetaPakistan
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Xiaofang SunNanfang Hospital of Southern Medical University; Third Affiliated Hospital,... and other collaboratorsUnknownBeta-Thalassemia
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Lantu BiopharmaNot yet recruitingBeta-Thalassemia
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingBeta-ThalassemiaUnited States
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Children's Hospital of Fudan UniversityCorrectSequence Therapeutics Co., LtdRecruiting
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Shenzhen HemogenRecruiting
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Shanghai BDgene Co., Ltd.Shanghai Children's Medical CenterNot yet recruiting
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Assiut UniversityNot yet recruiting
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityActive, not recruiting
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bluebird bioCompletedBeta-ThalassemiaUnited States, Germany, United Kingdom, France, Greece, Italy
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Bioray LaboratoriesXiangya Hospital of Central South University; First Affiliated Hospital of... and other collaboratorsEnrolling by invitation
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bluebird bioCompletedBeta-ThalassemiaFrance, United Kingdom, United States, Thailand, Italy, Germany
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Imara, Inc.Terminatedβ ThalassemiaIsrael, France, Malaysia, Turkey, Denmark, Georgia, Greece, Italy, Lebanon, Morocco, Netherlands, Tunisia, United Kingdom
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Acceleron Pharma Inc. (a wholly owned subsidiary...CompletedB-ThalassemiaItaly, Greece