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Clinical Trials on Transthyretin Gene Mutations
Total 1319 results
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingProgressive Disease | Recurrent Fallopian Tube Carcinoma | Recurrent Ovarian Carcinoma | Recurrent Primary Peritoneal Carcinoma | Recurrent Endometrial Carcinoma | Endometrial Adenocarcinoma | Primary Peritoneal High Grade Serous Adenocarcinoma | Platinum-Resistant Ovarian Carcinoma | High Grade Ovarian... and other conditionsUnited States
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AstraZenecaCompletedEGFR Mutation Status in aNSCLC PatientsKorea, Republic of, Russian Federation, Malaysia, China, Australia, Taiwan, Thailand, Indonesia, Singapore
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Second Affiliated Hospital, School of Medicine,...RecruitingRisk Factors | Gene Polymorphism | Severe PeriodontitisChina
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Uludag UniversityUnknownOvarian Reserve, Endometrioma, PTEN-AKT-FOXO3 Gene ExpressionTurkey
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AnHeart Therapeutics Inc.RecruitingIDH1 Inhibitor AB-218 in Patients With Advanced IDH1 Mutant Cholangiocarcinoma and Other Solid TumorCholangiocarcinoma With IDH1 Mutation | Solid Tumors With IDH1 MutationChina
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Gynecologic Oncology GroupNational Cancer Institute (NCI)WithdrawnBreast Carcinoma | BRCA1 Mutation Carrier | BRCA2 Mutation CarrierUnited States
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Eloxx Pharmaceuticals, Inc.TerminatedGenetic Diseases | Nonsense Mutations
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Columbia UniversityNational Institute on Aging (NIA)RecruitingLumbar Spinal Stenosis | Cardiomyopathy, Hypertrophic | Cardiac Amyloidosis | ATTR Amyloidosis Wild Type | ATTR Gene Mutation | ATTRV122I AmyloidosisUnited States
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Rutgers, The State University of New JerseyNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...RecruitingParkinson Disease | Cognitive Decline | Parkinson | Genetic Predisposition | GBA Gene MutationUnited States
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Sarah GoldbergMirati Therapeutics Inc.TerminatedLung Diseases | Carcinoma, Non-Small-Cell Lung | Lung Neoplasms | Metastatic Lung Non-Small Cell Carcinoma | PD-L1 Gene Mutation | Pembrolizumab | Stage IV Lung Non-Small Cell Cancer AJCC v7 | Advanced Treatment-Naïve PD-L1 | SitravatinibUnited States
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Royal Marsden NHS Foundation TrustPfizer; Breast Cancer NowActive, not recruitingGastric Cancer | Triple Negative Breast Cancer | Lobular Breast Carcinoma | CDH1 Gene MutationUnited Kingdom
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Stanford UniversityCompletedRecurrent Non-Small Cell Lung Carcinoma | KRAS Gene Mutation | Metastatic Malignant Neoplasm in the Brain | Stage IV Non-Small Cell Lung Cancer AJCC v7United States
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PfizerCompletedTransthyretin Familial Amyloidosis Polyneuropathy (TTR-FAP) | Transthyretin Cardiomyopathy (TTR-CM) | Familial Amyloid Cardiomyopathy | Senile Systemic Amyloidosis (SSA)
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The University of Hong KongCompletedAML | FLT3-ITD MutationHong Kong
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Centre Hospitalier Universitaire de NiceUnknownMitochondrial Diseases | Diagnosis | DNA MutationsFrance
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MapKure, LLCRecruitingSolid Tumor | B-Raf Mutation-Related TumorsUnited States, Australia
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PfizerCompletedSolid Tumors Harboring a BRAF V600 MutationUnited States, France, Italy, Singapore, Australia, Spain, Switzerland, Canada, Belgium
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Fujian Cosunter Pharmaceutical Co. LtdUnknownSolid Tumor | C-Met Mutation-Related TumorsChina
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University Health Network, TorontoActive, not recruitingMutation | Hereditary Cancer Syndrome | High-Risk | Germline MutationCanada
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Chang Gung Memorial HospitalIntuitive SurgicalActive, not recruitingBreast Cancer | BRCA1 Mutation | BRCA2 Mutation | Nipple-sparing Mastectomy | Prophylactic MastectomyTaiwan
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Centre Jean PerrinInternational Cancer Research Group; Institut Max Planck d'optique quantiqueRecruitingBRCA1 Mutation | BRCA2 Mutation | Breast Cancer FemaleFrance
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Georgetown UniversityGeorge Washington UniversityEnrolling by invitation
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Umeå UniversityCompletedTransthyretin Amyloidosis | CardiomyopathySweden
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University of AarhusUnknown
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Taiho Oncology, Inc.Approved for marketingAdvanced CholangiocarcinomaUnited States
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National Cancer Center, JapanEisai Co., Ltd.Active, not recruitingAdvanced or Recurrent Solid Tumors | FGFR Gene AlterationsJapan
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Oslo Metropolitan UniversitySophies Minde Foundation; UniCare Bakke ASCompleted
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National Institute of Allergy and Infectious Diseases...TerminatedIFN-Gamma Therapy | CGD Gene Mutation | CGD Response to IFNg | CGD - Chronic Granulomatous Disease | Immunodeficiency DiseaseUnited States
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ArriVent BioPharma, Inc.RecruitingAdvanced Non-Small Cell Lung Cancer | Metastatic Non-Small Cell Lung Cancer | Non-Small Cell Lung Cancer (NSCLC) | HER2 Exon 20 Mutations | EGFR Exon 20 Mutations | EGFR Uncommon Mutations, Including G719X and S768IUnited States, Australia, Spain, United Kingdom, France, Italy, China, Korea, Republic of, Canada, Japan, Netherlands
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Columbia UniversityAmerican Cancer Society, Inc.CompletedBreast Cancer | Ovarian Cancer | BRCA1 Mutation | BRCA2 MutationUnited States
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PfizerTerminatedHeart Failure With Preserved Ejection Fraction | Transthyretin Amyloid CardiomyopathySpain, United States, Japan, Canada, France, Italy, Poland, United Kingdom
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Novartis PharmaceuticalsCompletedNALP3 MutationUnited Kingdom, France, Germany, India, Spain
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National Institutes of Health Clinical Center (CC)WithdrawnAcute Pain | Nitric Oxide | Gene Expression
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University of HelsinkiCompletedAndroid Obesity, Metabolic Parameters and Adipose Tissue (AT) Gene ExpressionFinland
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Alnylam PharmaceuticalsRecruitingPolyneuropathy | Hereditary Transthyretin-mediated (hATTR) AmyloidosisNetherlands, Spain, United States, Germany, France, Italy, Portugal
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Brigham and Women's HospitalNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedCircadian Rhythm | Melatonin | Glucose | GenesUnited States
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BeBetter Med IncXiangya Hospital of Central South UniversityRecruitingAdvanced or Metastatic Solid Tumor | KRAS G12C MutationChina
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Boehringer IngelheimCompleted
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingFatigue | Overweight | Lynch Syndrome | Chronic Lymphocytic Leukemia | BRCA1 Gene Mutation | BRCA2 Gene Mutation | Breast Carcinoma | Cancer Survivor | Ovarian Carcinoma | Health Status Unknown | Body Mass Index 25 or GreaterUnited States
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UNICANCERARCAGY/ GINECO GROUP; SOLTI Breast Cancer Research GroupActive, not recruitingER-positive and HER2-negative Metastatic or Locally Advanced Breast Cancer | a Germline or Somatic BRCA Mutation, or a Deleterious Alteration of Other Genes Involved in Homologous Recombination Repair (HRR) or in MSI StatusFrance
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Genzyme, a Sanofi CompanyCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Gene Therapy | Age-Related Maculopathies | Age-Related Maculopathy | Retinal Neovascularization | Maculopathies, Age-Related | Maculopathy, Age-Related | Therapy, GeneUnited States
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Spark TherapeuticsCompletedHematologic Diseases | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Gene Therapy | Blood Coagulation Disorder | Gene Transfer | Adeno-Associated Virus (AAV) | Factor VIII (FVIII) | Factor VIII (FVIII)... and other conditionsUnited States
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Mayo ClinicNational Institute of Neurological Disorders and Stroke (NINDS); National Institute... and other collaboratorsRecruitingAmyotrophic Lateral Sclerosis | Progressive Supranuclear Palsy (PSP) | Corticobasal Degeneration (CBD) | GRN Related Frontotemporal Dementia | Behavioral Variant Frontotemporal Dementia (bvFTD) | Semantic Variant Primary Progressive Aphasia (svPPA) | Nonfluent Variant Primary Progressive Aphasia... and other conditionsUnited States, Canada
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Roswell Park Cancer InstituteCompletedStage IIIA Non-Small Cell Lung Cancer | Stage IIIB Non-Small Cell Lung Cancer | Recurrent Non-Small Cell Lung Carcinoma | Stage IV Non-Small Cell Lung Cancer | EGFR Gene MutationUnited States
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Shanghai Chest HospitalUnknownNon-Small Cell Lung Cancer | Brain Metastases | EGFR Gene MutationChina
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Novosibirsk Scientific Research Institute for Circulatory...Recruitingto Evaluate the Association of GUCY1A3 rs7692387 Gene Polymorphism Carrier on the Development of Cardiovascular Events After Coronary Artery Bypass GraftingRussian Federation
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Cancer Institute and Hospital, Chinese Academy...RecruitingCarcinoma, Transitional Cell | HER-2 Gene AmplificationChina
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The University of Texas Health Science Center at...WithdrawnOvarian Cancer | Breast Cancer Stage IV | BRCA1 Mutation | BRCA2 Mutation
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Ionis Pharmaceuticals, Inc.RecruitingHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Italy, Portugal, Spain, Taiwan, Sweden, Canada, Brazil, France, New Zealand, Argentina, Cyprus, Australia, Turkey
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Ionis Pharmaceuticals, Inc.CompletedHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Spain, Taiwan, Italy, Germany, Argentina, Australia, Brazil, Canada, Cyprus, France, Greece, New Zealand, Portugal, Sweden, Turkey