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Clinical Trials on Transthyretin Gene Mutations
Total 1319 results
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Sun Yat-sen UniversityRecruitingNon-small Cell Lung Cancer (NSCLC) | EGFR-TKI Resistant Mutation | EGFR-TKI Sensitizing Mutation | Somatic Mutation | Germline MutationsChina
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Montefiore Medical CenterActive, not recruitingTransthyretin Cardiac Amyloidosis | Transthyretin Amyloid CardiomyopathyUnited States
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI)RecruitingBRCA1 Gene Mutation | BRCA2 Gene Mutation | Recurrent Ovarian Carcinoma | Recurrent Malignant Solid Neoplasm | Metastatic Malignant Solid Neoplasm | Stage IV Breast Cancer AJCC v6 and v7 | Stage III Breast Cancer AJCC v7 | Stage IIIA Breast Cancer AJCC v7 | Stage IIIB Breast Cancer AJCC v7 | Stage IIIC... and other conditionsUnited States
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Joanne JeterNational Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Colon Adenoma | Colon Carcinoma | MLH1 Gene Mutation | MSH2 Gene MutationUnited States
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Universidad de Costa RicaUniversitat Autonoma de BarcelonaUnknownColon Cancer | Chemotherapy Effect | Chemotherapeutic Toxicity | MTHFR Gene MutationCosta Rica
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China Medical University HospitalNot yet recruitingNon-small Cell Lung Cancer | EGFR Gene Mutation | EGFR-TKI Resistant Mutation
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Algalarrondo VincentBichat Hospital; BioquantisRecruitingTransthyretin Cardiac Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Amyloid CardiomyopathyFrance
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National Cancer Institute (NCI)CompletedBRCA1 Gene Mutation | BRCA2 Gene Mutation | Recurrent Breast Carcinoma | Estrogen Receptor Negative | Estrogen Receptor Positive | HER2/Neu Negative | Progesterone Receptor Negative | Progesterone Receptor Positive | Triple-Negative Breast Carcinoma | Stage IV Breast Cancer AJCC v6 and v7 | Stage IIIB Breast... and other conditionsUnited States
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Regeneron PharmaceuticalsRecruitingCongenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF)Spain, United Kingdom, United States
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Second Xiangya Hospital of Central South UniversityThe First Affiliated Hospital of Nanchang University; Xiangya Hospital of Central... and other collaboratorsRecruitingLung Cancer, Non-small Cell | Circulating Tumor DNA | EGFR Gene Mutation | EGFR-TKI Resistant Mutation | Primary ResistanceChina
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Zhejiang Cancer HospitalRecruitingHER2 Gene Mutation | Bile Duct Adenocarcinoma Non-ResectableChina
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Memorial Sloan Kettering Cancer CenterCompletedLung Cancer | Lung Cancer Metastatic | EGFR Gene MutationUnited States
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University of South FloridaBoston Children's HospitalCompletedPTEN Gene MutationUnited States
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Children's Hospital Medical Center, CincinnatiRecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello Syndrome | SYNGAP1-Related Intellectual Disability | DLG4 | RAS Mutation | Noonan Syndrome With Multiple Lentigines | Noonan Neurofibromatosis Syndrome | Smith-Kingsmore Syndrome | MTOR Gene Mutation | GATOR-1 Gene... and other conditionsUnited States
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Children's Healthcare of AtlantaEmory University; Brigham and Women's Hospital; University of California, San... and other collaboratorsWithdrawnPentalogy of Cantrell | Mutations in Non-muscle GenesUnited States
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The Affiliated Nanjing Drum Tower Hospital of Nanjing...RecruitingNSCLC | EGFR Gene MutationChina
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University Hospital, GrenobleCompletedHealthy Volunteers | Intellectual Deficiency | Asymptomatic Carrier of the Mutation of the Gene MYT1LFrance
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Dana-Farber Cancer InstituteGenentech, Inc.RecruitingSalivary Gland Cancer | HER2 Gene MutationUnited States
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Galderma R&DCompletedGene ExpressionUnited States
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University of California, Los AngelesCompleted
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SensorionNot yet recruitingOtorhinolaryngologic Diseases | Ear Diseases | Hearing Disorders | Deafness | Hearing Loss, Sensorineural | Congenital Deafness | DFNB9 | OTOF Gene MutationFrance
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Agyany Pharma LTDRecruiting
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Haukeland University HospitalTerminatedColorectal Cancer Metastatic | Colorectal Cancer Stage IV | TP53 Gene MutationNorway
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Assiut UniversityNot yet recruitingGene Amplification
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Laval UniversityCompleted
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Hamad Medical CorporationQatar UniversityCompleted
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SpringWorks Therapeutics, Inc.AvailableDesmoid Tumor | NOTCH Gene Mutation Positive Tumors
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PfizerTerminatedDilated Cardiomyopathy | Lamin A/C Gene MutationUnited States, Spain, Canada, Belgium, Italy, Argentina, Mexico, Netherlands, Norway, United Kingdom
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Cardiff OncologyCompletedMetastatic Colorectal Cancer | KRAS Gene MutationUnited States
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Cardiff OncologyNo longer availableMetastatic Colorectal Cancer | KRAS Gene Mutation
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Mayo ClinicRecruitingAortic Stenosis | Transthyretin Amyloidosis | Transthyretin Cardiac Amyloidosis | Transthyretin Amyloid CardiomyopathyUnited States
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Peking University Third HospitalRecruiting
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PfizerCompletedTransthyretin Amyloid Polyneuropathy (ATTR-PN)China
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Icahn School of Medicine at Mount SinaiMassachusetts General Hospital; National Institute of Neurological Disorders...RecruitingParkinson Disease | GBA Gene Mutation | LRRK2United States
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Shanghai University of Traditional Chinese MedicineUnknownGene Mutation-Related Cancer | Traditional Chinese Medicine
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Hideho Okada, MD, PhDNational Cancer Institute (NCI); California Institute for Regenerative Medicine...RecruitingGlioblastoma | Recurrent Glioblastoma | EGFR Gene Mutation | MGMT-Unmethylated GlioblastomaUnited States
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Betta Pharmaceuticals Co., Ltd.Active, not recruitingNon-Small Cell Lung Cancer | EGFR Gene MutationChina
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University of Colorado, DenverCancer League of ColoradoWithdrawnMetastatic Breast Cancer | Triple Negative Breast Cancer | Locally Advanced Breast Cancer | Unresectable Breast Carcinoma | PD-L1 Gene MutationUnited States
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Pr. Nicolas GIRERDRecruitingTransthyretin Cardiac AmyloidosisFrance
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Poitiers University HospitalPfizerCompletedTransthyretin Cardiac AmyloidosisFrance
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Cervesi Hospital, Cattolica, ItalyRecruiting
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Natera, Inc.CompletedSingle Gene DisordersUnited States
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Poitiers University HospitalActive, not recruitingNon Small Cell Lung Cancer | Gene Mutation-Related Cancer | PD-L1 | PET/CTFrance
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Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, France, Greece, Italy, Spain, Canada, Germany, Portugal
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PfizerCompletedPolyneuropathy | Hereditary Transthyretin Amyloidosis (ATTRv)Spain
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Ullevaal University HospitalUniversity of OsloUnknownMemory | Gene ExpressionNorway
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Hunan Province Tumor HospitalRecruitingLung Adenocarcinoma | ALK Gene Mutation | ImmunotherapyChina
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Akcea TherapeuticsRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, Canada
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Shanghai Pulmonary Hospital, Shanghai, ChinaUnknownNonsmall Cell Lung Cancer | EGFR Gene Mutation
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University Medical Center GroningenRadboud University Medical Center; Maastricht University Medical Center; Erasmus... and other collaboratorsRecruitingCarcinoma, Non-Small-Cell Lung | Lung Cancer | Drug Monitoring | Anaplastic Lymphoma Kinase Gene Mutation | Anaplastic Lymphoma Kinase Gene TranslocationNetherlands, France