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Clinical Trials on Type 2 Spinal Muscular Atrophy
Total 16758 results
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Ohio State UniversityCure SMAActive, not recruitingSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheActive, not recruitingMuscular Atrophy, SpinalUnited States, Belgium, Brazil, Russian Federation, Australia, Taiwan, Poland
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BiogenEnrolling by invitationMuscular Atrophy, SpinalUnited States, Spain, Taiwan, Chile, Saudi Arabia, Brazil, Russian Federation, Mexico, Germany, Estonia, Japan, Canada, Colombia, Lebanon, Poland, Italy, China
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Clinic for Special ChildrenGenentech, Inc.Active, not recruitingSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, France, Brazil, Croatia, Italy, Russian Federation, Saudi Arabia, Serbia, Switzerland, Turkey, Ukraine, Poland
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular AtrophyUnited States, United Kingdom, Australia, Belgium, Canada, Japan
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Hospital Israelita Albert EinsteinMinistry of Health, BrazilCompletedSpinal Muscular AtrophyBrazil
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BiogenCompletedSpinal Muscular AtrophyUnited States, Germany, Spain, Canada, France, Hong Kong, Italy, Japan, Korea, Republic of, Sweden
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BiogenCompleted
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Hospices Civils de LyonUnknownResponsiveness and Validation Study of MFM-20 in SMA Patients Treated With Nusinersen (RetroNusiMFM)Spinal Muscular AtrophyFrance
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Genentech, Inc.Approved for marketingMuscular Atrophy, SpinalUnited States
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University Hospital, RouenSociety GENOMIC VISIONTerminatedSpinal Muscular AtrophyFrance
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Hoffmann-La RocheCompleted
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University of UtahAbbott; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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Rigshospitalet, DenmarkCompleted
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HealthCore-NERIThe Spinal Muscular Atrophy FoundationCompletedSpinal Muscular AtrophyUnited States, Canada
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Centro Universitário Augusto MottaCompletedSpinal Muscular Atrophy
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University of Erlangen-Nürnberg Medical SchoolCompletedMuscular Diseases | Spinal Muscular AtrophyGermany
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University of Erlangen-Nürnberg Medical SchoolUnknownMuscular Diseases | Spinal Muscular AtrophyGermany
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Children's Hospital Medical Center, CincinnatiCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Congenital Muscular Dystrophy
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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GeneCradle IncRecruiting
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Charitable Foundation Children with Spinal Muscular...WithdrawnSpinal Muscular Atrophy | Neuromuscular DisordersUkraine
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McGill University Health Centre/Research Institute...Not yet recruiting
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Rigshospitalet, DenmarkRecruitingSpinal Muscular AtrophyDenmark
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National Taiwan University HospitalNot yet recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...IRCCS Eugenio Medea; Azienda Ospedaliera Universitaria Policlinico "G. Martino... and other collaboratorsNot yet recruitingSpinal Muscular Atrophy
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Hoffmann-La RocheRecruiting
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GeneCradle IncRecruitingSpinal Muscular AtrophyChina
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Fondazione Policlinico Universitario Agostino Gemelli...University of Milan; Ospedale Pediatrico Bambino GesùRecruiting
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University of Castilla-La ManchaRecruiting
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University of OxfordHoffmann-La Roche; Oxford University Hospitals NHS Trust; Novartis Gene TherapiesRecruiting
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Genentech, Inc.RecruitingSpinal Muscular AtrophyUnited States, Puerto Rico
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Bakri ElsheikhGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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BiogenRecruiting
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSpinal Muscular AtrophyUnited Kingdom
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Kaohsiung Medical University Chung-Ho Memorial...The Chinese Foundation of Health; Taipei Institute of PathologyRecruiting
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Hospital Israelita Albert EinsteinBiogenActive, not recruitingSpinal Muscular AtrophyBrazil, Argentina, Chile, Colombia, Mexico, Uruguay
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Hospices Civils de LyonCompletedSpinal Muscular AtrophyFrance
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Istanbul Medipol University HospitalActive, not recruitingMuscular Atrophy, SpinalTurkey
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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BiogenActive, not recruitingSpinal Muscular AtrophyUnited States, Taiwan, Israel, Australia, Qatar, United Kingdom, Turkey, Italy, Germany, Argentina, Canada
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Columbia UniversityThe Spinal Muscular Atrophy FoundationCompleted
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University Medical Centre LjubljanaCompleted
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Ohio State UniversityBiogen; Cure SMACompleted
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Institut de Myologie, FranceCompletedSpinal Muscular AtrophyFrance
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Centre Hospitalier Régional de la CitadelleRoche Pharma AG; Biogen; AveXis, Inc.; Association Belge contre les Maladies neuro...CompletedSpinal Muscular AtrophyBelgium
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BiogenCompletedSpinal Muscular AtrophyUnited States
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BiogenCompletedSpinal Muscular AtrophyUnited States, Canada