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Clinical Trials on Ullrich Congenital Muscular Dystrophy
Total 2164 results
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University of Southern CaliforniaEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Novartis PharmaceuticalsCompletedAutosomal Dominant Polycystic Kidney DiseaseGermany, Austria, France
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); St. Jude Children... and other collaboratorsEnrolling by invitationAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia | Multisystem ProteinopathyUnited States, South Africa, Germany
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Indiana UniversityRecruitingAortic Valve Disease | Marfan Syndrome | Bicuspid Aortic Valve | Thoracic Aortic Aneurysm | Thoracic Aortic Dissection | Turner Syndrome | Vascular Ehlers-Danlos Syndrome | Familial Thoracic Aortic Aneurysm and Aortic Dissection | PHACE Syndrome | Aortopathies | Thoracic Aortic Disease | Thoracic Aortic Rupture and other conditionsUnited States
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University of Colorado, DenverRecruitingHearing Loss | Smith-Lemli-Opitz Syndrome | Cone-Rod DystrophyUnited States
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Centre Hospitalier Intercommunal CreteilEtablissement Français du Sang; Centre National de la Recherche Scientifique...RecruitingSickle Cell Disease | Stenosis | Cerebral IschemiaFrance
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Servei Central d' AnestesiologiaCompletedEhlers-Danlos Syndrome | Craniocervical SyndromeSpain
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Hospices Civils de LyonUnknownWilliams-Beuren Syndrome | Micro-duplication 7q11.23 Syndrome | VasculopathyFrance
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsTaiwan, United Kingdom, Thailand, Serbia, Croatia, Italy, Poland, Romania, Hungary, Malaysia, United States, Austria, Brazil, Greece, Japan, Puerto Rico, Russian Federation, South Africa, Turkey
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National Taiwan University HospitalCompletedFacial Angiofibroma
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsFrance, United States, Spain, Brazil, Philippines, South Africa, Poland, Turkey, Romania, Bulgaria, Russian Federation, Argentina
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The Cleveland ClinicRecruitingCardiovascular Diseases | Lymphedema | Thrombosis | Vasculitis | Peripheral Artery Disease | Metabolic Disease | Lipedema | Thoracic Outlet Syndrome | Vasospasm | Venous Disease | Fibromuscular Dysplasia | May-Thurner Syndrome | Carotid Disease | Aneurysmal Disease | Non-Atherosclerotic Chronic Arterial Occlusive Disease and other conditionsUnited States
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Central Hospital, Nancy, FranceRecruiting
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Kyorin UniversityCompletedDisease Progression | Autosomal Dominant Polycystic Kidney DiseaseJapan
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Aucta Pharmaceuticals, IncTerminatedTuberous Sclerosis | Angiofibroma of FaceUnited States, China
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Hospices Civils de LyonWithdrawnFacial AngiofibromasFrance
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University GhentTerminatedHypermobile Ehlers-Danlos Syndrome | Hypermobility Syndrome | Multidirectional Subluxation of ShoulderBelgium
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National Institute of Arthritis and Musculoskeletal...TerminatedNervous System Malformations | Urticaria | Papilledema | Arthropathy, NeurogenicUnited States
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Novo Nordisk A/SWithdrawnHealthy | Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B
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University of L'AquilaUnknownVon Willebrand Disease | Congenital Coagulation Factors Deficiency | Haemophilia CarriersItaly
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Institut National de la Santé Et de la Recherche...RecruitingVascular Malformations | PIK3CA-related Overgrowth Spectrum | Megalencephaly | Lymphatic Malformation | CLOVES Syndrome | Venous Malformation | Klippel Trenaunay Syndrome | MCAP | MacrodactylyFrance
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West China HospitalRecruitingInfantile Hemangiomas | Neck Mass | Thyroglossal Duct Cysts | Branchial Cleft Anomalies | Dermoid and Epidermoid Cysts | TeratomasChina
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University Hospital, MontpellierRecruiting
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First Affiliated Hospital, Sun Yat-Sen UniversityRecruitingStroke | G6PD DeficiencyChina
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Novo Nordisk A/SCompletedEpidemiological Study on Haemophilia Care and Orthopaedic Status in Developing Countries (HAEMOcare)Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BIndia, Morocco, South Africa, Oman
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With InhibitorsUnited States
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MallinckrodtTerminatedSickle Cell Disease | Pulmonary Hypertension | Lung Disease | Lung Transplant | Cardiac TransplantUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BSpain
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University College, LondonWashington University School of Medicine; University of Washington; Alzheimer... and other collaboratorsNot yet recruitingAlzheimer Disease | Autosomal Dominant Alzheimer Disease Due to Mutation of Presenilin 1 (Disorder) | Autosomal Dominant Alzheimer Disease Due to Mutation of Presenilin 2 (Disorder) | Autosomal Dominant Alzheimer Disease Due to Mutation of Amyloid Precursor Protein (Disorder)
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Radboud University Medical CenterRecruitingAutosomal Dominant Polycystic Kidney | Polycystic Liver Disease | Liver Cyst | Autosomal Dominant Polycystic Liver DiseaseNetherlands
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Chang Gung Memorial HospitalEnrolling by invitationMyocardial Infarction | Left Bundle-Branch Block | Atrial Flutter | Left Ventricular Hypertrophy | Long QT Syndrome | Sinus Bradycardia | Right Bundle-Branch Block | Sinus Tachycardia | Premature Atrial Complexes | Premature Ventricular ComplexesTaiwan
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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US Department of Veterans AffairsCompletedFibromyalgia | Chronic Fatigue Syndrome | Post-Traumatic Stress Disorder | Neurologic Abnormalities | General Health Status
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OHSU Knight Cancer InstituteNational Heart, Lung, and Blood Institute (NHLBI)CompletedChronic Myeloproliferative Disorders | Fanconi Anemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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Mayo ClinicCompletedAutosomal Dominant Polycystic Kidney Disease | Polycystic Liver Disease | Autosomal Dominant Polycystic Liver Disease | Somatostatin AnalogsUnited States
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Dermatology Specialties Limited PartnershipCompletedTuberous Sclerosis | Facial AngiofibromaUnited States, Taiwan, Serbia, Spain, Australia, Czechia, Hungary, New Zealand, Slovakia
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University of South FloridaUnknownEhlers-Danlos Syndrome | Joint Hypermobility | Hyperextension Knees
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Universidad de GuanajuatoCompletedDown Syndrome | Metabolic Syndrome XMexico
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B | Relatives to/Carers of PatientsSpain, Canada, United Kingdom
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NobelpharmaCompletedPlaque | Tuberous Sclerosis | Angiofibroma | Hypomelanotic MaculeJapan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BUnited States
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Le Bonheur Children's HospitalPfizer; University of Tennessee Health Science CenterCompleted
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Tulane UniversityNot yet recruitingLow Back Pain | Ehlers-Danlos Syndrome | Sacroiliac InstabilityUnited States
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First Affiliated Hospital Xi'an Jiaotong UniversitySimcere CompanyRecruitingCerebral Infarction | G6PD DeficiencyChina
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University of Alabama at BirminghamNational Heart, Lung, and Blood Institute (NHLBI)TerminatedHypertension | Proteinuria | Sickle Cell Disease | Anemia, Sickle Cell | Kidney DiseaseUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Anemia | Pulmonary Hypertension | Cerebrovascular Disease | Chuvash PolycythemiaUnited States, Russian Federation
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B | Relatives to/Carers of PatientsBrazil
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Assistance Publique - Hôpitaux de ParisAventis PharmaceuticalsCompletedEHLERS-DANLOS SYNDROME, TYPE IV, AUTOSOMAL DOMINANT | CHROMOSOME 2q31.2 DELETION SYNDROME
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Indiana UniversityCompletedAutosomal Dominant Hypophosphatemic RicketsUnited States
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Istituto Ortopedico RizzoliRecruitingCollagen Diseases | Joint Hypermobility | Hypermobility Syndrome | Laxity of Ligament | Danlos Disease, EhlersItaly