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Clinical Trials on Unilineage Bone Marrow Failure Disorders in United Kingdom
Total 4699 results
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Adrianna Vlachos, MDTerminatedPure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingRecurrent Severe Aplastic Anemia | Refractory Severe Aplastic AnemiaUnited States
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Dr Yan BeauverdCompletedPolycythemia Vera | Thrombocythemia, EssentialSwitzerland, United Kingdom
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St. Jude Children's Research HospitalCompletedAnemia, Aplastic | Diamond-Blackfan Anemia | Amegakaryocytic Thrombocytopenia | Kostmann SyndromeUnited States
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David Rizzieri, MDCompletedSickle Cell Anemia | Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic AnemiaUnited States
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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University of NottinghamNottingham University Hospitals NHS Trust; Sheffield Teaching Hospitals NHS...CompletedPsychological Distress | Bone Marrow Transplantation | Haematopoietic Stem Cell TransplantationUnited Kingdom
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Masonic Cancer Center, University of MinnesotaRecruitingAplastic Anemia | Dyskeratosis CongenitaUnited States
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Masonic Cancer Center, University of MinnesotaCompletedAplastic Anemia | Dyskeratosis CongenitaUnited States
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St. Jude Children's Research HospitalBaylor College of Medicine; Children's Hospital of Philadelphia; Dana-Farber... and other collaboratorsRecruitingMyelodysplastic Syndromes | Sickle Cell Disease | Fanconi Anemia | Severe Congenital Neutropenia | Bone Marrow Failure Syndromes | Blood Coagulation Disorder | Erythrocyte Disorder | Leukocyte Disorder | Hemostasis | Dyskeratosis Congenita | Diamond-Blackfan Anemia | Congenital Thrombocytopenia | Myeloproliferative...United States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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University College, LondonMedical Research CouncilRecruitingLymphoma | Myelodysplastic Syndromes | Leukemia | Myeloma | Graft Vs Host Disease | Severe Aplastic Anemia | Primary Immune DeficiencyUnited Kingdom
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Masonic Cancer Center, University of MinnesotaCompletedDiamond-Blackfan Anemia | Shwachman-Diamond Syndrome | Kostmann's NeutropeniaUnited States
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Northwestern Memorial HospitalUnknownAplastic Anemia | Graft Versus Host DiseaseUnited States
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Paul SzabolcsRecruitingIdiopathic Pulmonary Fibrosis | Emphysema or COPDUnited States
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University of UtahNovartisCompletedSevere Aplastic Anemia | Moderate Aplastic Anemia | Very Severe Aplastic AnemiaUnited States
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Bellicum PharmaceuticalsTerminatedLymphoma, Non-Hodgkin | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Myelodysplastic Syndrome | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Osteopetrosis | Leukemia, Acute Myeloid (AML), ChildUnited Kingdom, Italy
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National Institute of Dental and Craniofacial Research...Completed
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M.D. Anderson Cancer CenterGenzyme, a Sanofi CompanyCompletedMyelodysplastic Syndrome | Aplastic AnemiaUnited States
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Washington University School of MedicineShwachman Diamond Syndrome Foundation; Barnes-Jewish HospitalRecruiting
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Queen's University, BelfastMayo Clinic; University Hospital Southampton NHS Foundation Trust; University... and other collaboratorsCompletedPrimary Myelofibrosis | Polycythemia Vera | Essential ThrombocythemiaUnited Kingdom
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic Syndromes | Purpura, Thrombocytopenic | Anemia, Aplastic | Red-Cell Aplasia, Pure | Bone Marrow Failure Syndromes | Hemoglobinuria, Paroxysmal | Leukemia, LymphocyticUnited States
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Memorial Sloan Kettering Cancer CenterBoston Children's Hospital; Fred Hutchinson Cancer Center; Children's Hospital... and other collaboratorsCompletedLeukemia | Myelodysplastic Syndrome | Aplastic AnemiaUnited States
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Masonic Cancer Center, University of MinnesotaCompleted
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Masonic Cancer Center, University of MinnesotaTerminated
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)TerminatedFanconi AnemiaUnited States
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI); Miltenyi Biotec, Inc.Completed
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Fairview University Medical CenterCompleted
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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Boston Children's HospitalCompleted
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Masonic Cancer Center, University of MinnesotaCompletedFanconi AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, CincinnatiCompletedFanconi AnemiaUnited States
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University of...TerminatedFANCONI ANEMIAUnited States
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University of MinnesotaCompleted
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingMyelodysplastic Syndrome (MDS) | Severe Aplastic Anemia | Hypo-Plastic MDSUnited States
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National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI); National Institute of Allergy and Infectious... and other collaboratorsRecruitingLymphoma | Leukemia | Aplastic Anemia | Myelodysplastic Syndrome (MDS)United States
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BioLineRx, Ltd.CompletedAplastic Anemia | Hypoplastic Myelodysplastic SyndromeUnited States
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Masonic Cancer Center, University of MinnesotaCompleted
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)CompletedFanconi AnemiaUnited States
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Medical College of WisconsinMemorial Sloan Kettering Cancer CenterCompleted
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National Heart, Lung, and Blood Institute (NHLBI)CompletedPancytopenia | Fanconi's AnemiaUnited States
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Boston Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); Children's Hospital Medical...Completed
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Neena Kapoor, M.D.Withdrawn
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedFanconi AnemiaUnited States, Brazil
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Boston Children's HospitalChildren's Hospital Medical Center, CincinnatiRecruitingShwachman-Diamond Syndrome | Shwachman-Diamond Syndrome-LikeUnited States
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Stanford UniversityUniversity of Alabama at Birmingham; University of MinnesotaCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedFanconi Anemia | Severe Aplastic AnemiaUnited States