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Clinical Trials on Unilineage Bone Marrow Failure Disorders
Total 9639 results
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European Society for Blood and Marrow TransplantationNovartis; PfizerCompletedSevere Aplastic AnemiaSwitzerland, Netherlands, France, Italy, Spain, United Kingdom
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Wu XiaoxiongUnknown
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Sidney Kimmel Comprehensive Cancer Center at Johns...TerminatedSevere Aplastic AnemiaUnited States
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Cancer Institute and Hospital, Chinese Academy...UnknownSevere Aplastic AnemiaChina
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Asan Medical CenterUnknownAcquired Aplastic AnemiaKorea, Republic of
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National Heart, Lung, and Blood Institute (NHLBI)CompletedThrombocytopenia | Anemia, Aplastic | Anemia, HypoplasticUnited States
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medac GmbHSyneos Health; Celerion; Venn Life SciencesCompletedBone Marrow Failure Syndromes | Inborn Errors of Metabolism | Primary Immunodeficiencies | HaemoglobinopathiesPoland, Czechia, Germany, Italy
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Peking Union Medical College HospitalNot yet recruiting
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Novartis PharmaceuticalsActive, not recruitingSevere Aplastic Anemia (SAA)Japan, Korea, Republic of, China, Taiwan
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Novartis PharmaceuticalsActive, not recruitingAplastic AnemiaThailand, Russian Federation, Portugal, United Kingdom, Hong Kong, United States
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Roswell Park Cancer InstituteCompleted
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National Center for Research Resources (NCRR)University of California, Los AngelesCompletedAplastic AnemiaUnited States
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Jiangsu HengRui Medicine Co., Ltd.Recruiting
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Institute of Hematology & Blood Diseases HospitalRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA)United States
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National Institutes of Health Clinical Center (CC)National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA)United States
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Anjali SharathkumarAmgenActive, not recruitingThrombocytopenia | Bone Marrow Failure Disorders | Aplastic Anemia | Refractory Cytopenia of Childhood | Myelodysplastic Syndrome(MDS)United States
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Peking Union Medical College HospitalNot yet recruitingNon Severe Aplastic AnemiaChina
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AmgenWithdrawn
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Institute of Hematology & Blood Diseases Hospital...Jiangsu Hengrui Pharmaceuticals Co.,LtdRecruitingNon Severe Aplastic Anemia | UntreatedChina
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Jiangsu HengRui Medicine Co., Ltd.RecruitingTreatment-naive Severe Aplastic AnemiaChina
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Memorial Sloan Kettering Cancer CenterRecruitingHemoglobinopathies | AML | MDS | Bone Marrow Failure | ALL | Inherited Metabolic Disorders | HLH | MPD Withou Myelofibrosis | NHL or HLUnited States
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Children's Hospital of PhiladelphiaRecruitingLeukemia | Bone Marrow Failure Syndromes | Immunodeficiencies | Inborn Errors of Metabolism | Immunodysregulation Polyendocrinopathy Enteropathy X-linked SyndromeUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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Shandong UniversityWithdrawn
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Burnasyan Federal Medical Biophysical CenterUnknownNeutropenic Enterocolitis | Myeloablative Chemotherapy Induced Bone Marrow AplasiaRussian Federation
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Talaris Therapeutics Inc.Duke UniversityWithdrawnAnemia, Sickle Cell | Thalassemia | Beta-Thalassemia | Bone Marrow Failure Syndromes | Diamond-Blackfan Anemia | Alpha-Thalassemia | Complex and Transfusion-dependent HemoglobinopathiesUnited States
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National Heart, Lung, and Blood Institute (NHLBI)NovartisRecruitingSevere Aplastic AnemiaUnited States
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Institute of Hematology & Blood Diseases Hospital...RecruitingPlatelet Transfusion Refractoriness | Severe Aplastic AnemiaChina
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Federal Research Institute of Pediatric Hematology...Not yet recruitingAplastic Anemia | Aplastic Anemia Idiopathic
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic AnemiaUnited States
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University Children's Hospital TuebingenUnknownAplastic Anemia | Acute Leukemias | Childhood Solid TumorGermany, Austria
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National Heart, Lung, and Blood Institute (NHLBI)CompletedNeutropenia | Pancytopenia | Aplastic Anemia | Severe Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedSevere Aplastic Anemia (SAA)United States
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Cooperative Study Group A for HematologyUnknownAplastic AnemiaKorea, Republic of
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Peking Union Medical College HospitalRecruitingAplastic Anemia | Drug Therapy | CSAChina
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The Korean Society of Pediatric Hematology OncologyUnknownAnemia, AplasticKorea, Republic of
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The Korean Society of Pediatric Hematology OncologyUnknown
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingAnemia, Diamond-BlackfanUnited States
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Northwell HealthTerminatedDiamond Blackfan AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedDiamond Blackfan AnemiaUnited States
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Sidney Kimmel Comprehensive Cancer Center at Johns...RecruitingPrimary Immune Deficiency Disorder | Bone Marrow Failure | Immune Deficiency DiseaseUnited States
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National Cancer Institute (NCI)CompletedDyskeratosis Congenita | Telomere Biology DisordersUnited States
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Columbia UniversityUnknownSevere Combined Immunodeficiency | Fanconi Anemia | Bone Marrow Failure | OsteopetrosisUnited States
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Federal Scientific Clinical Centre of Pediatric...Unknown
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Novartis PharmaceuticalsTerminatedAplastic AnemiaRussian Federation
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Novartis PharmaceuticalsCompleted
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Cellphire Therapeutics, Inc.Department of Health and Human ServicesTerminatedMyelodysplastic Syndromes | Myeloproliferative Disorders | Thrombocytopenia | Hematologic Malignancy | Bone Marrow Aplasia | Platelet RefractorinessUnited States, Israel, Norway
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Feinstein Institute for Medical ResearchDiamond Blackfan Anemia Foundation, Inc.Recruiting
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Federal Research Institute of Pediatric Hematology...CompletedLeukemia, Myeloid, Acute | Opportunistic Infections | Graft vs Host Disease | Precursor T-Cell Lymphoblastic Leukemia-Lymphoma | Bone Marrow Failure Syndromes | Immune Deficiency DiseaseRussian Federation