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Clinical Trials on Unilineage Bone Marrow Failure Disorders
Total 9633 results
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National Heart, Lung, and Blood Institute (NHLBI)CompletedNeutropenia | Pancytopenia | Aplastic Anemia | Severe Aplastic AnemiaUnited States
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Children's Hospital Medical Center, CincinnatiHoxworth Blood CenterTerminatedBone Marrow Failure | Waning Donor Chimerism | Waning Immune Function | Primary Immunodeficiency Disease(s)United States
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Children's Hospital Medical Center, CincinnatiFDA Office of Orphan Products DevelopmentCompleted
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Assistance Publique - Hôpitaux de ParisNot yet recruitingRefractory Idiopathic Aplastic Anemia | Haploidentical Allogeneic Hematopoietic Stem Cell Transplantation
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Memorial Sloan Kettering Cancer CenterActive, not recruiting
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSteroid-refractory Diamond-Blackfan Anemia (DBA)United States
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National Heart, Lung, and Blood Institute (NHLBI)TerminatedAplastic Anemia | Pure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedThrombocytopenia | Neutropenia | Pancytopenia | ImmunosuppresionUnited States
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King's College Hospital NHS TrustCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, Acute | Bone Marrow Transplantation | Aplastic AnemiaUnited Kingdom
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Adrianna Vlachos, MDTerminatedPure Red Cell Aplasia | Diamond Blackfan AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Aplastic | Red-Cell Aplasia, Pure | Anemia, Diamond-BlackfanUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingSevere Aplastic Anemia | Idiopathic Aplastic Anemia | Moderate Aplastic Anemia Requiring Transfusions
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National University Hospital, SingaporeUnknownHaematological Malignancies | Acquired Aplastic AnaemiaSingapore
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Fondazione Italiana Sindromi Mielodisplastiche-ETSCompletedMyelofibrosis | Aplastic Anemia | MyelodysplasiaItaly
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David Rizzieri, MDCompletedSickle Cell Anemia | Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic AnemiaUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingRecurrent Severe Aplastic Anemia | Refractory Severe Aplastic AnemiaUnited States
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St. Jude Children's Research HospitalCompletedAnemia, Aplastic | Diamond-Blackfan Anemia | Amegakaryocytic Thrombocytopenia | Kostmann SyndromeUnited States
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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Seoul National University HospitalMinistry of Food and Drug Safety, KoreaUnknownAcute Leukemia | Severe Aplastic Anemia | Chronic LeukemiaKorea, Republic of
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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Masonic Cancer Center, University of MinnesotaRecruitingAplastic Anemia | Dyskeratosis CongenitaUnited States
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Masonic Cancer Center, University of MinnesotaCompletedAplastic Anemia | Dyskeratosis CongenitaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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European Institute of OncologyRecruitingLymphoma | Leukemia | Aplastic Anemia | Leukemia, Acute | Leukemia, ChronicItaly
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St. Jude Children's Research HospitalBaylor College of Medicine; Children's Hospital of Philadelphia; Dana-Farber... and other collaboratorsRecruitingMyelodysplastic Syndromes | Sickle Cell Disease | Fanconi Anemia | Severe Congenital Neutropenia | Bone Marrow Failure Syndromes | Blood Coagulation Disorder | Erythrocyte Disorder | Leukocyte Disorder | Hemostasis | Dyskeratosis Congenita | Diamond-Blackfan Anemia | Congenital Thrombocytopenia | Myeloproliferative...United States
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University College, LondonBloodwiseCompletedHodgkin's Lymphoma | Non-Hodgkin's Lymphoma | Myelodysplastic Syndrome | Acute Myeloid Leukaemia | Chronic Lymphocytic Leukaemia | Acute Lymphoblastic Leukaemia | Chronic Myeloid Leukaemia | Acquired Bone Marrow Failure Syndromes | Other Haematological Malignancies; Unrelated HSCT IndicatedUnited Kingdom
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Masonic Cancer Center, University of MinnesotaCompletedDiamond-Blackfan Anemia | Shwachman-Diamond Syndrome | Kostmann's NeutropeniaUnited States
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Alberta Children's HospitalStollery Children's HospitalTerminatedChildhood Cancer | Aplastic Anemia | Metabolic DisordersCanada
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University of UtahNovartisCompletedSevere Aplastic Anemia | Moderate Aplastic Anemia | Very Severe Aplastic AnemiaUnited States
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Memorial Sloan Kettering Cancer CenterBoston Children's Hospital; Fred Hutchinson Cancer Center; Children's Hospital... and other collaboratorsCompletedLeukemia | Myelodysplastic Syndrome | Aplastic AnemiaUnited States
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Institute of Hematology & Blood Diseases HospitalUnknownUrination Disorders | Thrombosis | Proteinuria | Anemia, Hemolytic | Hemoglobinuria, Paroxysmal | Hemoglobinuria | Paroxysmal Nocturnal Hemoglobinuria | Bone Marrow Failure | Aplastic Anemia,China
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic Syndromes | Purpura, Thrombocytopenic | Anemia, Aplastic | Red-Cell Aplasia, Pure | Bone Marrow Failure Syndromes | Hemoglobinuria, Paroxysmal | Leukemia, LymphocyticUnited States
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Paul SzabolcsRecruitingIdiopathic Pulmonary Fibrosis | Emphysema or COPDUnited States
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Northwestern Memorial HospitalUnknownAplastic Anemia | Graft Versus Host DiseaseUnited States
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Xiaofan ZhuAvailableFanconi Anemia | Autosomal or Sex Linked Recessive Genetic Disease | Bone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases. | Hematopoiesis Maintainance.China
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National Institute of Dental and Craniofacial Research...Completed
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Washington University School of MedicineShwachman Diamond Syndrome Foundation; Barnes-Jewish HospitalRecruiting
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Institute of Hematology & Blood Diseases HospitalUnknownUrination Disorders | Thrombosis | Proteinuria | Anemia, Hemolytic | Hemoglobinuria, Paroxysmal | Hemoglobinuria | Paroxysmal Nocturnal Hemoglobinuria | Bone Marrow Failure | Aplastic Anemia,China
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M.D. Anderson Cancer CenterGenzyme, a Sanofi CompanyCompletedMyelodysplastic Syndrome | Aplastic AnemiaUnited States
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Peking University People's HospitalNot yet recruitingMyelodysplastic Syndromes | Acute Leukemia | Severe Aplastic Anemia
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Boston Children's HospitalCompleted
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Masonic Cancer Center, University of MinnesotaCompletedFanconi AnemiaUnited States
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERERCompleted
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National Heart, Lung, and Blood Institute (NHLBI)Children's Hospital Medical Center, CincinnatiCompletedFanconi AnemiaUnited States
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Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of Medicine; University of...TerminatedFANCONI ANEMIAUnited States
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University of MinnesotaCompleted
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Masonic Cancer Center, University of MinnesotaCompleted
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Masonic Cancer Center, University of MinnesotaTerminated