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Clinical Trials on Unilineage Bone Marrow Failure Disorders
Total 9631 results
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Children's Hospital Medical Center, CincinnatiFood and Drug Administration (FDA)Completed
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Assistance Publique - Hôpitaux de ParisCompleted
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OHSU Knight Cancer InstituteNational Cancer Institute (NCI)CompletedUnspecified Childhood Solid Tumor, Protocol Specific | Unspecified Adult Solid Tumor, Protocol Specific | Fanconi AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedNeoplasms | Myelodysplastic Syndromes | Hematologic Diseases | Leukemia | Severe Combined Immunodeficiency | Fanconi Anemia | Anemia, Aplastic | Hematopoietic Stem Cell Transplantation
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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National Heart, Lung, and Blood Institute (NHLBI)CompletedPurpura, Thrombocytopenic | Agranulocytosis | Anemia, Aplastic | Blood Disease
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Masonic Cancer Center, University of MinnesotaNot yet recruitingAcquired Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria | Severe Aplastic Anemia | Acquired Amegakaryocytic Thrombocytopenia
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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Postgraduate Institute of Medical Education and...Completed
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Wake Forest University Health SciencesTerminatedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Immune Deficiency | Lymphomas | Bone Marrow Failure | Osteopetrosis | HemoglobinopathyUnited States
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Zimmer BiometCompletedBone Marrow Edema | Bone Marrow LesionsGermany, Netherlands, Italy, Spain, United Kingdom
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Washington University School of MedicineSt. Louis Children's HospitalRecruitingHemoglobinopathies | Metabolic Disorders | Hematologic, Immune, or Bone Marrow Disorders | Non-malignant DisordersUnited States, Canada
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de... and other collaboratorsCompletedFanconi AnemiaSpain
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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University Health Network, TorontoRecruitingMyelofibrosis | Bone Marrow Cancer | High-Risk CancerCanada
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University of Alabama at BirminghamCompletedLymphoma | Leukemia | Myelofibrosis | Myelodysplastic Syndrome | Severe Aplastic Anemia | Allogeneic TransplantUnited States
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Seoul National University HospitalMerck Sharp & Dohme LLCCompletedMyelodysplastic Syndromes | Fungal Infection | Aplastic AnemiaKorea, Republic of
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The University of QueenslandRecruitingPulmonary Fibrosis | Dyskeratosis Congenita | Telomere Shortening | Telomere DiseaseAustralia
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States, United Kingdom, Germany
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CENTOGENE GmbH RostockWithdrawnHypophosphatemia | Photophobia | Renal Fanconi SyndromeGermany, India, Sri Lanka
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Daniel Godoy MartinezUnknownLymphoma | Leukemia | Aplastic Anemia | MyelomaBrazil
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University Hospital, LilleCompleted
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Children's Hospital Medical Center, CincinnatiMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer CenterRecruitingFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Severe Marrow FailureUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...TerminatedGenetic Disorder | Severe Aplastic Anemia | Immunodeficiency SyndromeUnited States
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedAplastic Anemia | Paroxysmal Hemoglobinuria, NocturnalUnited States
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Children's Hospital Medical Center, CincinnatiRecruiting
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group ASpain, United Kingdom
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Rocket Pharmaceuticals Inc.Active, not recruitingFanconi Anemia Complementation Group AUnited States
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Boston Children's HospitalTerminatedFanconi Anemia | Dyskeratosis CongenitaUnited States
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Hospital Universitari Vall d'Hebron Research InstituteERN-EuroBloodNet (European Reference Network on Rare Hematological DiseasesRecruitingLeukemia | Anemia | Iron Metabolism Disorders | Anemia, Sickle Cell | Thalassemia | Bleeding Disorder | Myeloma | Lymphoid Neoplasm | Blood Cancer | Bone Marrow Failure | Red Cell Membrane and Enzyme Abnormalities | Myeloma, MalignantSpain
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University Hospital, LilleCompletedFractures, Bone | Adiposity | Bone Marrow Disease | Fat DisorderFrance
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National Taiwan University HospitalRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Aplastic Anemia | Myeloproliferative NeoplasmTaiwan
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHepatitis-Associated Aplastic AnemiaUnited States
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsRecruitingCongenital Amegakaryocytic Thrombocytopenia | Paroxysmal Nocturnal Hemoglobinuria | Shwachman-Diamond Syndrome | Bone Marrow Failure Syndrome | Congenital Pure Red Cell Aplasia | Hereditary Sideroblastic Anemia | Hematologic Neoplasm With Germline GATA2 Mutation | Hematologic Neoplasm With Germline... and other conditionsUnited States
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Wuhan Union Hospital, ChinaJiangsu Hengrui Pharmaceutical Co., Ltd.Not yet recruitingAplastic Anemia | Primary Immune ThrombocytopeniaChina
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Sidney Kimmel Comprehensive Cancer Center at Johns...Duke UniversityCompletedBone Marrow Transplant
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GlaxoSmithKlineCompletedBone Marrow TransplantationUnited States
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University Hospital, Basel, SwitzerlandCompletedBone Marrow BiopsySwitzerland
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Eunice Kennedy Shriver National Institute of Child...CompletedStem Cell Transplant | Aplastic Anemia | HemoglobinUnited States
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Assistance Publique - Hôpitaux de ParisCompletedHereditary Diseases | Relapse | Acquired Aplastic Anemia | Absence of an HLA Identical DonorFrance
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedBone Marrow DonorsItaly
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Arizona State UniversityMayo ClinicCompleted
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Massachusetts General HospitalCompleted
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Wake Forest University Health SciencesOhio State University; University of Mississippi Medical CenterCompletedBone Marrow TransplantationUnited States
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University of UtahEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedBone Marrow TransplantUnited States
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Aysenur UcerizIstanbul Sabahattin Zaim UniversityCompletedMental Health | ART | Bone Marrow CancerTurkey