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Clinical Trials on Urea Cycle Disorders, Inborn in India
Total 120 results
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, United Kingdom, Bulgaria, Canada, Colombia, India, Israel, Lebanon, Mexico, Russian Federation, Serbia, Tunisia
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OctapharmaCompletedCongenital Fibrinogen Deficiency | AfibrinogenemiaIran, Islamic Republic of, United States, Bulgaria, India, Switzerland, United Kingdom
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FVII DeficiencySlovakia, Israel, Spain, India, Iran, Islamic Republic of, Pakistan, Turkey, Germany, Serbia, Italy, Greece, Thailand, France, United States, Hong Kong, Venezuela
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Enzyvant Therapeutics GmBHCompletedFarber Disease | Farber's Disease | Farber Lipogranulomatosis | Acid Ceramidase Deficiency | Ceramidase Deficiency | N-Laurylsphingosine Deacylase Deficiency | ASAH1 MutationUnited States, Egypt, Canada, Italy, Turkey, Argentina, Germany, India, Sweden
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ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
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Catalyst BiosciencesTerminatedFactor VII Deficiency | Hemophilia A With Inhibitor | Glanzmann ThrombastheniaUnited States, India, Italy, Russian Federation, Ukraine
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Genzyme, a Sanofi CompanyActive, not recruitingHemophiliaCanada, Italy, Turkey, Spain, United States, India
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CENTOGENE GmbH RostockWithdrawnSkin and Connective Tissue Diseases | Hyaline Membrane Disease | Hyalinosis | Juvenile Hyaline Fibromatosis | Fibromatosis Hyalinica Multiplex JuvenilisGermany, Sri Lanka, India
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OctapharmaCompletedSevere Hemophilia AUnited States, France, Canada, United Kingdom, India, Georgia, Moldova, Republic of, Poland, Ukraine
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Christian Medical College, Vellore, IndiaUnknownHemophiliaIndia, Argentina, Brazil, Egypt, Iran, Islamic Republic of, Singapore, South Africa, Thailand, Venezuela
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Baxalta now part of ShireCompletedAcquired Hemophilia AUnited States, Canada, India, United Kingdom
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
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OctapharmaCompletedCongenital Fibrinogen DeficiencyUnited States, Bulgaria, India, Iran, Islamic Republic of, Lebanon, Russian Federation, Saudi Arabia, Turkey, United Kingdom
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ErydelCompletedAtaxia TelangiectasiaItaly, United States, India, Israel
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OctapharmaCompletedPrevent Bleeding in Major SurgeryUnited States, Turkey, Romania, India, Bulgaria, Italy, Oman, Poland, South Africa
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CENTOGENE GmbH RostockTerminatedPancreatitis | Failure to Thrive | Meconium Ileus | Breathlessness | Lung Infection | Chronic Nasal Congestion | Clubbing ToesIndia, Sri Lanka, Albania, Georgia, Pakistan
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Grifols Therapeutics LLCGrifols Biologicals, LLCTerminatedHemophilia A, CongenitalUnited States, Spain, Italy, India, Canada, Russian Federation
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Crinetics Pharmaceuticals Inc.RecruitingCongenital Adrenal Hyperplasia | Classic Congenital Adrenal HyperplasiaBrazil, India, United States, Argentina, Italy, United Kingdom
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Kastle Therapeutics, LLCCompletedHypercholesterolemia | Heterozygous FamilialUnited States, Italy, Poland, Ukraine, United Kingdom, Germany, Hong Kong, Taiwan, Spain, Argentina, Belgium, Israel, Malaysia, South Africa, Turkey, Netherlands, Korea, Republic of, Canada, New Zealand, Russian Federation, Brazil, Austral... and more
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Medexus Pharma, Inc.CompletedHemophilia BUnited States, France, United Kingdom, India, Israel, Italy, Poland
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University Hospital, GenevaCompletedAfibrinogenemia, CongenitalFrance, Turkey, Switzerland, Netherlands, Spain, India, Poland, Canada, United States, Algeria, Egypt, Germany, Italy, Japan, Kuwait, Lebanon, Morocco, Pakistan, Serbia, Slovakia, Tunisia
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Baxalta now part of ShireCompletedHemophilia BTaiwan, Colombia, Argentina, Brazil, Bulgaria, Chile, Czechia, India, Ireland, Italy, Japan, Poland, Romania, Russian Federation, Sweden, Ukraine, United Kingdom
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Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
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CENTOGENE GmbH RostockCompletedScoliosis | Muscular Atrophy | Duchenne Muscular Dystrophy | Lordosis | Muscular Weakness | Increased Lordosis/Scoliosis | Hyporeflexia | Red-Green Color BlindnessEgypt, India, Albania, Pakistan, Georgia, Lebanon, Romania, Sri Lanka
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OctapharmaCompletedSevere Hemophilia ACanada, United States, France, Spain, Ukraine, United Kingdom, Belarus, Georgia, Germany, India, Italy, Moldova, Republic of, Morocco, Poland, Portugal, Russian Federation, Slovenia
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Fondazione Angelo Bianchi BonomiSintesi Research SrlCompletedHemophilia AUnited States, India, Spain, Argentina, Austria, Brazil, Chile, Egypt, Iran, Islamic Republic of, Italy, Mexico, Saudi Arabia, South Africa, Turkey
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Natera, Inc.Houston Perinatal Associates; Lyndhurst Clinical Research; Dr. Carpenter Maternal... and other collaboratorsCompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Sex Chromosome AbnormalitiesUnited States, India, Malaysia
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BayerCompletedHemophilia AChina, United States, Ukraine, Taiwan, Mexico, Thailand, Romania, Colombia, Turkey, Serbia, Russian Federation, South Africa, Japan, Indonesia, Argentina, Czech Republic, India, Slovakia
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Novartis PharmaceuticalsCompletedCystic FibrosisRussian Federation, Egypt, Romania, Estonia, Latvia, Lithuania, Bulgaria, South Africa, India
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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Novo Nordisk A/SRecruitingHaemophilia A With or Without InhibitorsKorea, Republic of, India, China, Canada, Spain, Netherlands, South Africa, United States, Israel, Japan, Poland, United Kingdom, Italy, Lithuania, Portugal, Switzerland, Taiwan
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PfizerRecruitingHemophilia A | Hemophilia BHong Kong, Spain, Serbia, Turkey, United States, China, Mexico, South Africa, India, Japan, Croatia, Korea, Republic of, Oman, Taiwan, Italy, Canada, France
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NovartisCompletedMuckle Wells SyndromeUnited States, Spain, United Kingdom, France, Germany, India
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Genzyme, a Sanofi CompanyRecruitingFabry DiseaseCroatia, United States, Argentina, Australia, Belgium, Bulgaria, Canada, Germany, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Malaysia, Philippines, Poland, Romania, Singapore, Slovakia, Taiwan, Thailand, United Kingdom, Vietn... and more
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BSpain, Taiwan, United Kingdom, Italy, Germany, United States, South Africa, Australia, Poland, Armenia, France, India, Canada, Brazil, Turkey, Egypt
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Baxalta now part of ShireCompletedVon Willebrand DiseaseNetherlands, Spain, United States, Belgium, Australia, United Kingdom, Austria, Italy, Bulgaria, Japan, Poland, Germany, India, Canada, Russian Federation, Sweden
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Genzyme, a Sanofi CompanyActive, not recruitingHemophiliaChina, Hungary, Turkey, Canada, Korea, Republic of, United States, Australia, Denmark, France, Germany, India, Ireland, Israel, Italy, Japan, Malaysia, South Africa, Taiwan, Ukraine, United Kingdom
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BUnited States, Italy, Spain, Taiwan, Australia, Belgium, United Kingdom, France, Germany, India, South Africa, Canada, Poland, Armenia, Turkey
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy
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CENTOGENE GmbH RostockTerminatedLymphangioleiomyomatosis | Subependymal Giant Cell Astrocytoma | Facial Angiofibroma | Cortical Dysplasia | Renal Angiomyolipoma | Hypomelanotic Macules | Shagreen Patches | Ungual Fibromas | Cardiac RhabdomyomaSri Lanka, Albania, Romania, Egypt, Pakistan, Georgia, India, Lithuania
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Hoffmann-La RocheCompletedHemophilia ACanada, Australia, Belgium, India, Germany, Israel, Italy, Spain, Colombia, United Kingdom, Netherlands, Saudi Arabia, Hungary, Guatemala, Russian Federation, Poland, Switzerland, Finland, Panama, Brazil, Mexico, Portugal, Romania, Sw...
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BayerCompletedHemophilia A | Blood Coagulation DisordersSpain, Taiwan, Austria, United States, Germany, Thailand, United Kingdom, Italy, Turkey, Croatia, Serbia, Poland, Israel, Sweden, Indonesia, Argentina, Norway, South Africa, India, Hong Kong, Denmark, Pakistan
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SanofiRecruitingHemophiliaGreece, Korea, Republic of, France, Taiwan, Italy, Spain, United States, Canada, China, Germany, India, Japan, Mexico, South Africa, Turkey, Poland, Saudi Arabia
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Catalyst BiosciencesTerminatedHemophilia A With Inhibitor | Hemophilia B With InhibitorUnited States, United Kingdom, Taiwan, Italy, Spain, India, Turkey, Malaysia, Russian Federation, Armenia, Georgia, Hungary, Mexico, Poland, South Africa, Ukraine
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of RochesterRecruitingFriedreich Ataxia | Neuro-Degenerative DiseaseUnited States, Canada, New Zealand, Australia, India
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PfizerActive, not recruitingHemophilia A | Hemophilia BUnited States, Spain, Canada, China, Korea, Republic of, Hong Kong, Serbia, Taiwan, Turkey, France, Oman, Saudi Arabia, Japan, India, South Africa, Mexico, Croatia, Italy, Bulgaria, Russian Federation
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedSevere Hemophilia BSweden, United States, France, Italy, Russian Federation, United Kingdom, Germany, China, Poland, Japan, Australia, Brazil, Canada, India, South Africa, Hong Kong, Belgium
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Bioverativ Therapeutics Inc.CompletedHemophilia AUnited States, Canada, Italy, Australia, Austria, Belgium, Brazil, France, Germany, Hong Kong, India, Ireland, Israel, Japan, Netherlands, New Zealand, Poland, South Africa, Spain, Sweden, Switzerland, United Kingdom