Clinical Trials on Urea Cycle Disorders, Inborn in New Zealand
Total 1095 results
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Teachers College, Columbia UniversityCompleted
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New York Medical CollegeCompleted
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University of RochesterCompletedMyotonic DystrophyUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed IncorporatedCompleted
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Baxalta now part of ShireCompleted
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Genentech, Inc.Terminated
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedSevere Hemophilia AUnited States, United Kingdom, Spain, Hong Kong, Israel, New Zealand, Sweden, Australia, Brazil, Japan, Austria, Belgium, Italy, India, Switzerland, Canada, France, Germany, South Africa
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Travere Therapeutics, Inc.UnknownCerebrotendinous Xanthomatosis (CTX)United States
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Instituto Grifols, S.A.WithdrawnHypofibrinogenemia | Congenital AfibrinogenemiaIndia, Turkey, Lebanon, United States, Bulgaria
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Tasly Pharmaceuticals, Inc.Not yet recruitingTourette SyndromeUnited States
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Yale UniversityTourette Association of AmericaTerminated
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Yale UniversityEdison Pharmaceuticals Inc; Rembrandt FoundationCompleted
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BayerCompletedHemophilia ABelgium, New Zealand, Netherlands, Greece, United Kingdom, Austria, United States, Italy, Romania, Bulgaria, Canada, Israel, Poland, Lithuania, Norway, Argentina, Spain
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited States
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University of California, DavisTerminatedHemophilia A | Hemophilia A With InhibitorUnited States
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PfizerActive, not recruitingHemophilia BUnited States, Canada, Australia, Turkey
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ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
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Genzyme, a Sanofi CompanyActive, not recruitingGaucher Disease Type 1 | Gaucher Disease Type 3Germany, United States, Japan, United Kingdom
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Sangamo TherapeuticsEnrolling by invitationFabry Disease | Fabry Disease, Cardiac VariantUnited States, Australia, United Kingdom
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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Newark Beth Israel Medical CenterGenentech, Inc.Not yet recruiting
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Canada, Japan, France, Denmark
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Amryt PharmaRecruitingHomozygous Familial HypercholesterolemiaItaly, United States, Argentina, Canada, France, Greece, Netherlands, United Kingdom
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa, Australia, Austria, Canada, Czechia, France, Greece, Italy, Japan, Ukraine
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Alexander KolevzonCompletedPhelan-McDermid SyndromeUnited States
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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BayerAmerican Thrombosis and Hemostasis NetworkTerminated
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Vanderbilt UniversityNational Heart, Lung, and Blood Institute (NHLBI); University of South Florida and other collaboratorsCompletedHermansky Pudlak SyndromeUnited States
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Bio Products LaboratoryCompletedFactor 10 DeficiencyUnited States
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI)TerminatedHematologic Diseases | Anemia, Sickle Cell | Cerebrovascular Accident | HemochromatosisUnited States
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Freeline TherapeuticsTerminatedLysosomal Storage Diseases | Fabry DiseaseUnited States, Norway, Germany, Austria, United Kingdom, Italy, Canada
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BayerCompleted
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Boston Children's HospitalPhelan-McDermid Syndrome FoundationCompletedIntellectual Disability | Autism Spectrum Disorder | Phelan-McDermid SyndromeUnited States
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaNetherlands, United States, United Kingdom, France
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Huntington Study GroupRoche Products LimitedRecruitingHuntington DiseaseUnited States
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University of RochesterCompletedHuntington Disease | ChoreaUnited States
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BioSensicsUniversity of RochesterUnknownHuntington DiseaseUnited States
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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Yale UniversityAmerican Academy of Child Adolescent Psychiatry.Completed
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaNetherlands, United States, Canada, Russian Federation, South Africa
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, United Kingdom, Canada, France, Germany
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AstraZenecaCompletedTourette SyndromeUnited States
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PfizerTerminatedHyperlipoproteinemia Type IIICanada, United States
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Yale UniversityNational Institute of Mental Health (NIMH)RecruitingTourette Syndrome in AdolescenceUnited States
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PfizerWithdrawnTourette's SyndromeUnited States
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University of RochesterKaneka CorporationCompleted