Clinical Trials on X-ALD in Belgium

Total 12115 results

Marinus Pharmaceuticals
University of California, Davis; U.S. Army Medical Research and Development...

Completed

Ganaxolone Treatment in Children With Fragile X Syndrome

Fragile x Syndrome

Belgium, United States
Patrice D. Cani
Cliniques universitaires Saint-Luc- Université Catholique de Louvain

Completed

Evaluation of the Effects Associated With the Administration of Akkermansia Muciniphila on Parameters of Metabolic Syndrome (Microbes4U)

Glucose Metabolism Disorders | Obesity | Dyslipidemias | Metabolic Syndrome x

Belgium
Universitaire Ziekenhuizen KU Leuven
KU Leuven

Completed

Angelman & Rett Syndrome: Interaction and Communication

Communication | Parent-Child Relations | Behavior, Child

Belgium
Universitair Ziekenhuis Brussel
Marguerite - Marie Delacroix Foundation

Not yet recruiting

Combining Exome and Transcriptome Data to Unravel the Genetic Basis of the Lissencephalies

Classical Lissencephalies and Subcortical Band Heterotopias

Belgium
Santhera Pharmaceuticals

Completed

Long-term Safety, Tolerability and Efficacy of Idebenone in Duchenne Muscular Dystrophy (DELPHI Extension)

Duchenne Muscular Dystrophy

Belgium
Cliniques universitaires Saint-Luc- Université...

Completed

Gait Evaluation in Haemophiliac Patients (GAIT_GENERAL)

Hemophilia A | Hemophilia B

Belgium
Santhera Pharmaceuticals

Completed

Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular Dystrophy (DELPHI)

Duchenne Muscular Dystrophy (DMD)

Belgium
Cliniques universitaires Saint-Luc- Université...

Completed

Impact of Conservative Treatment by Custom-made Orthoses in Patients With Haemophilic Ankle Arthropathy

Haemophilia A | Haemophilia B

Belgium
Laurent Servais
SYSNAV

Recruiting

Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study

Duchenne Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy

Belgium
Universiteit Antwerpen
University Hospital, Antwerp; Cliniques universitaires Saint-Luc- Université...

Recruiting

Gaining Insight Into the Complexity of Pain in Patients With Haemophilia

Hemophilia A | Hemophilia B

Belgium
BioMarin Pharmaceutical

Completed

Phase I/II Study of PRO044 in Duchenne Muscular Dystrophy (DMD)

Duchenne Muscular Dystrophy

Belgium, Netherlands, Italy, Sweden
Erasme University Hospital
Fonds National de la Recherche Scientifique; Fonds Erasme; Fonds pour la chirurgie...

Completed

Uric Acid Metabolism, Endothelial Function and Oxidative Stress in Vegans and Omnivores.

Healthy | Diet Modification

Belgium
Erasme University Hospital
Fonds National de la Recherche Scientifique; Fonds Erasme

Completed

Uric Acid Effects on Endothelium and Oxydative Stress

Hypertension | Oxidative Stress | Cardiovascular System | Endothelial Function

Belgium
Cliniques universitaires Saint-Luc- Université...

Recruiting

Endothelial Dysfunction in Covid-19 (ENDOCOVID)

Covid19 | Hypoxemic Respiratory Failure

Belgium
Novartis Pharmaceuticals

Terminated

Long-term, Safety and Tolerability Study of AFQ056 in Adolescent Patients With Fragile X Syndrome (Open-label)

Fragile X Syndrome

United States, Belgium, Australia, Israel, Switzerland, Germany, Denmark, Italy, Netherlands, Spain, Sweden, United Kingdom, France
BioMarin Pharmaceutical

Terminated

Extension Study of BMN 044 in Duchenne Muscular Dystrophy (DMD)

Duchenne Muscular Dystrophy

Netherlands, Belgium, Italy, Sweden
Sarepta Therapeutics, Inc.

Completed

Study of Eteplirsen in Young Participants With Duchenne Muscular Dystrophy (DMD) Amenable to Exon 51 Skipping

Duchenne Muscular Dystrophy

Belgium, France, Italy, United Kingdom
BioMarin Pharmaceutical

Terminated

Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD)

Duchenne Muscular Dystrophy

Belgium, Netherlands, Italy, Sweden
Universitaire Ziekenhuizen KU Leuven

Recruiting

Neuro-immune Interactions and PPI

Functional Dyspepsia

Belgium
Universiteit Antwerpen

Completed

The Effect of a Red Rice and Olive Extract Nutrition Supplement on Cholesterol Levels in Patients With Metabolic Syndrome

Hypercholesterolaemia

Belgium
Thomas More University of Applied Sciences
University of Liege; Universiteit Antwerpen; Artevelde University of Applied...

Recruiting

TreatPaCS = Treatment for Preschool Age Children Who Stutter (TreatPaCS)

Stuttering, Developmental

Belgium
Denali Therapeutics Inc.

Enrolling by invitation

An Extension Study of the Long-Term Safety, Tolerability, and Efficacy of Tividenofusp Alfa (DNL310) in Participants With Mucopolysaccharidosis Type II (MPS II) From Study DNLI-E-0002 or Study DNLI-E-0007

Mucopolysaccharidosis II

United States, Canada, Belgium, Czechia, Netherlands
University Hospital, Ghent

Completed

Natural Language Processing for Headache Medicine

Migraine | Headache Disorders

Belgium
University Ghent

Completed

The Effectiveness of Patient-tailored Treatment in Patients With (Sub)Acute Neck Pain

Neck Pain | Rehabilitation | Acute Pain | Physical Therapy Modalities

Belgium
Imelda Hospital, Bonheiden
Université Catholique de Louvain

Recruiting

Metabolic Profiling of Hematopoietic Stem Cells in Clonal Hematopoiesis (CHIP)

Aging | Hip Fractures | Osteoporosis | Osteoarthritis, Hip | Clonal Hematopoiesis of Indeterminate Potential

Belgium
Universitaire Ziekenhuizen KU Leuven

Recruiting

Comparing Pregabalin and Placebo in Patients With Persistent Globus Sensation (Lyrica)

Globus Sensation

Belgium
University Hospital, Ghent

Completed

Aortic Valve Dynamics During Exercise After Valve Sparing Root Replacement Surgery

Aneurysm Aortic Root | Aortic Valve, Bicuspid

Belgium
University Hospital, Ghent
University Ghent

Terminated

Olfactive Discriminative Ability of Dogs When Confronted With Seizure and Non-seizure Samples // Identification of Potential Biomarkers for Epilepsy in Human Sweat.

Epilepsy

Belgium
University Hospital, Antwerp

Completed

Analysis of Selective Cerebrovascular Distribution With FDCT in the Angiosuite

Ischemic Stroke | Intracranial Arterial Diseases | Intracranial Aneurysm | Cerebral Hypoxia | Intracranial Vascular Disorder

Belgium
Sarepta Therapeutics, Inc.

Terminated

A Study to Evaluate Safety, Tolerability, and Efficacy of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) Who Have Completed Study 4658-102 (NCT03218995)

Duchenne Muscular Dystrophy

Belgium, France, Italy, United Kingdom
Hasselt University

Recruiting

Intensity of Physical Activity Level During Daily Living: Unravelling Its Relationship With Chronic Musculoskeletal Disorders and Evaluating Underlying Facilitators and Barriers, An Exploratory Survey Study (MSK-SUR)

Physical Activity | Chronic Musculoskeletal Disease | Exercise Intensity | Online Survey

Belgium
Novartis Pharmaceuticals

Completed

Safety and Efficacy of AFQ056 in Adolescent Patients With Fragile X Syndrome

Fragile X Syndrome

United States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
BioMarin Pharmaceutical

Terminated

A Phase I/II Study of BMN053 in Subjects With Duchenne Muscular Dystrophy (DMD)

Duchenne Muscular Dystrophy

United Kingdom, Italy, Belgium, Netherlands, France
BioMarin Pharmaceutical

Terminated

Phase IIb Study of PRO045 in Subjects With Duchenne Muscular Dystrophy

Duchenne Muscular Dystrophy

Belgium, Netherlands, France, United Kingdom, Italy
Wave Life Sciences Ltd.

Completed

Safety and Tolerability of WVE-210201 in Patients With Duchenne Muscular Dystrophy

Duchenne Muscular Dystrophy

Belgium, United Kingdom, France, United States, Italy, Canada, Netherlands
Swedish Orphan Biovitrum

Completed

A Non-interventional Retrospective Study of the Current Treatment Practice in European Haemophilia Care

Haemophilia A | Haemophilia B

France, Germany, Italy, Spain, Sweden, Belgium, United Kingdom
Arcturus Therapeutics, Inc.

Recruiting

Study for Adolescent and Adult Participants With Ornithine Transcarbamylase Deficiency to Evaluate Safety and Tolerability of ARCT-810

OTC Deficiency | Ornithine Transcarbamylase Deficiency | OTCD

Spain, Belgium, United Kingdom, Sweden
Janssen Research & Development, LLC
Janssen Research & Development, LLC

Active, not recruiting

Follow-up Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene

X-Linked Retinitis Pigmentosa

United States, Canada, Israel, United Kingdom, Spain, Denmark, France, Belgium, Italy, Netherlands, Switzerland
Janssen Research & Development, LLC
Janssen Research & Development, LLC

Active, not recruiting

Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene

X-Linked Retinitis Pigmentosa

Belgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
Italfarmaco

Recruiting

Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy (ULYSSES)

Duchenne Muscular Dystrophy

Canada, Italy, France, Belgium, Germany, Netherlands, United Kingdom
GlaxoSmithKline

Completed

Phase II Doubleblind Exploratory Study of GSK2402968 in Ambulant Subjects With Duchenne Muscular Dystrophy

Muscular Dystrophies

Germany, Belgium, Turkey, Netherlands, Spain, Israel, Australia, France, United Kingdom
BioMarin Pharmaceutical

Terminated

A Prospective Natural History Study of Progression of Subjects With Duchenne Muscular Dystrophy.

Duchenne Muscular Dystrophy

United States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
Denali Therapeutics Inc.

Recruiting

A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II) (COMPASS)

Mucopolysaccharidosis II

United States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Colombia, Brazil
University Hospital, Ghent

Completed

Belgian Screening Project for the Detection of Anderson-Fabry Disease in Hypertrophic Cardiomyopathy

Left Ventricular Hypertrophy

Belgium
Cochlear

Completed

Innovations in Clinical Care of CE Approved Nucleus Cochlear Implant Recipients

Hearing Loss

Belgium, Australia
Novo Nordisk A/S

Enrolling by invitation

A Study Following Males With Haemophilia B on Prophylaxis With Refixia/REBINYN

Haemophilia B

Canada, United Kingdom, Czechia, Germany, Greece, Austria, Belgium, Croatia, Denmark, Finland, Norway, Portugal
Shire

Completed

Sophisticated Assessment of Disease Burden in Patients With Fabry Disease (SOPHIA)

Fabry Disease

Finland, Sweden, Germany, Belgium, Czechia, Denmark
Wave Life Sciences Ltd.

Terminated

Efficacy and Safety Study of WVE-210201 (Suvodirsen) With Open-label Extension in Ambulatory Patients With Duchenne Muscular Dystrophy (DYSTANCE 51)

Duchenne Muscular Dystrophy

United States, Belgium, United Kingdom, Czechia, Canada, France, Italy, Sweden
Sarepta Therapeutics, Inc.

Active, not recruiting

Two-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Efficacy (Part B) in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping Treatment (MOMENTUM)

Duchenne Muscular Dystrophy

United States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy
PTC Therapeutics

Completed

Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and Canada

Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Dystrophinopathy

United Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel

Clinical Trials on X-ALD in Belgium

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