Clinical Trials on X-ALD in United Kingdom
Total 169808 results
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Great Ormond Street Hospital for Children NHS Foundation...UnknownX-linked Severe Combined ImmunodeficiencyUnited Kingdom
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingX-linked Myotubular Myopathy | Centronuclear Myopathy | Myotubular Myopathy | Myotubular Myopathy 1 | Myotubular (Centronuclear) Myopathy | Centronuclear Myopathy, X-LinkedUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSevere Combined Immunodeficiency, X-LinkedUnited Kingdom
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaboratorsRecruitingX Linked Myotubular MyopathyUnited Kingdom, Canada, United States
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Queen Margaret UniversityUnknownCardiovascular Diseases | Metabolic Syndrome XUnited Kingdom
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...WithdrawnGranulomatous Disease, Chronic, X-linked, VariantUnited Kingdom
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David WilliamsActive, not recruitingGene Therapy | Severe Combined Immunodeficiency, X LinkedUnited States, United Kingdom
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Rare Thyroid Therapeutics International ABVitaccess LtdCompletedAllan-Herndon-Dudley Syndrome | Monocarboxylate Transporter 8 (MCT8) DeficiencyUnited Kingdom
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Astellas Gene TherapiesCompletedX-linked Myotubular MyopathyUnited States, France, United Kingdom, Canada, Germany
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University of DundeeCompleted
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Astellas Gene TherapiesCompletedMales With X-linked Myotubular Myopathy (XLMTM)United States, United Kingdom
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University of OxfordUniversity College, London; Moorfields Eye Hospital NHS Foundation TrustCompleted
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital for... and other collaboratorsRecruiting
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Viking Therapeutics, Inc.RecruitingAdrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)United States, France, Germany, Italy, United Kingdom
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Edimer PharmaceuticalsActive, not recruitingX-linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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EspeRare FoundationIqvia Pty Ltd; Pierre Fabre MedicamentRecruitingX-Linked Hypohidrotic Ectodermal Dysplasia (XLHED)United States, Spain, France, Germany, Italy, United Kingdom
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ClasadoUniversity of ReadingCompletedMetabolic Syndrome XUnited Kingdom
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Manchester University NHS Foundation TrustCompletedMucopolysaccharidosis Type IIUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRecruitingPyruvate Dehydrogenase Complex Deficiency | Pyruvate Dehydrogenase E1 Alpha Deficiency | Pyruvate Dehydrogenase E1-Beta Deficiency | Pyruvate Dehydrogenase E2 Deficiency | Pyruvate Dehydrogenase Phosphatase DeficiencyUnited Kingdom
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VegaVect, Inc.National Eye Institute (NEI)Active, not recruiting
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University of California, DavisNational Institute of Mental Health (NIMH)CompletedFragile X PremutationUnited States
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRecruitingMonocarboxylate Transporter 8 Deficiency | Allan-Herndon-Dudley SyndromeUnited States, United Kingdom, Netherlands
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
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Imperial College LondonSarepta Therapeutics, Inc.; Department of Health, United KingdomCompletedDuchenne Muscular DystrophyUnited Kingdom
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ShireCompleted
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National Eye Institute (NEI)CompletedRetinoschisis | X-LinkedUnited States
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GE HealthcareCompleted
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REGENXBIO Inc.CompletedMucopolysaccharidosis IIBrazil, United States, United Kingdom
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Bio Products LaboratoryCompletedFactor X DeficiencyUnited Kingdom
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University of East AngliaHarvard School of Public Health (HSPH)CompletedInsulin Resistance | Metabolic Syndrome XUnited Kingdom, United States
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Anavex Life Sciences Corp.Completed
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ShireCompleted
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Medialis Ltd.Metabolic Support UKCompletedX-linked Hypophosphatemia (XLH)United Kingdom
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University of GlasgowGlaxoSmithKline; British Heart FoundationTerminatedAngina Pectoris | Metabolic Syndrome XUnited Kingdom
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Summit TherapeuticsCompletedModified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced DietMuscular Dystrophy, DuchenneUnited Kingdom
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University College, LondonRecruiting
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Novo Nordisk A/SEnrolling by invitationHaemophilia BNetherlands, United Kingdom
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Sheffield Children's NHS Foundation TrustSheffield Hallam University; National Institute for Health Research, United... and other collaboratorsActive, not recruiting
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GenethonInstitute of MyologyUnknownDuchenne Muscular DystrophyUnited Kingdom, France
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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University College, LondonRecruitingOrnithine Transcarbamylase DeficiencyUnited Kingdom
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University of MiamiJackson Health SystemNo longer available
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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University of California, DavisUniversity of Alberta; St. Justine's HospitalCompletedNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXS | Mental Retardation, X LinkedUnited States, Canada
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The University of Texas Health Science Center,...Samsung ElectronicsCompletedChest X-ray for Clinical EvaluationUnited States
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Cangene CorporationWithdrawnHemophilia BUnited Kingdom, United States