Clinical Trials on X-linked Adrenoleukodystrophy in United Kingdom
Total 1257 results
-
Regeneron PharmaceuticalsRecruitingHemophilia BUnited States, Germany, United Kingdom, Canada
-
AnnJi Pharmaceutical Co., Ltd.Active, not recruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
-
ArmaGen, IncCompletedMucopolysaccharidosis IIUnited States, Germany, Philippines
-
Swedish Orphan BiovitrumCompletedHaemophilia A | Haemophilia BFrance, Germany, Italy, Spain, Sweden, Belgium, United Kingdom
-
Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
-
Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
-
Applied Genetic Technologies CorpCompletedX-Linked Retinitis PigmentosaUnited States
-
Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
-
Eunice Kennedy Shriver National Institute of Child...TerminatedFragile X Syndrome | Premature Ovarian Failure | Premature Menopause | FMR1 Premutation | Primary Ovairan InsufficiencyUnited States
-
Cooperative International Neuromuscular Research...UnknownBecker Muscular DystrophyUnited States, Canada, Italy, United Kingdom
-
Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
-
TakedaTakeda Development Center Americas, Inc.Active, not recruitingHunter SyndromeUnited States, Germany, Malaysia, Philippines, Thailand, Dominican Republic, Serbia, Vietnam
-
PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
-
ItalfarmacoRecruitingDuchenne Muscular DystrophyCanada, Italy, France, Belgium, Germany, Netherlands, United Kingdom
-
iECURE, Inc.RecruitingUrea Cycle Disorders, Inborn | Ornithine Transcarbamylase Deficiency | Ornithine Transcarbamylase Deficiency Disease | Ornithine Carbamoyltransferase Deficiency (Disorder)United Kingdom
-
Freeline TherapeuticsCompletedLysosomal Storage Diseases | Fabry DiseaseGermany, United Kingdom
-
Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
-
Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
-
Beacon TherapeuticsRecruitingX-Linked Retinitis PigmentosaUnited States
-
National Institute of Arthritis and Musculoskeletal...CompletedIchthyosis | Ichthyosis, X-Linked | Ichthyosis, Lamellar | Darier Disease | Hailey-Hailey Disease | Hyperkeratosis, Epidermolytic | KeratodermaUnited States
-
GlaxoSmithKlineCompletedMuscular DystrophiesGermany, Belgium, Turkey, Netherlands, Spain, Israel, Australia, France, United Kingdom
-
National Institute of Neurological Disorders and...CompletedMotor Neuron DiseaseUnited States
-
Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
-
Swedish Orphan BiovitrumCerner EnvizaActive, not recruitingHemophilia BCzechia, Greece, Ireland, Italy, Norway, Saudi Arabia, Spain, Sweden, United Kingdom
-
Duke UniversityRecruiting
-
Beacon TherapeuticsEnrolling by invitationX-Linked Retinitis PigmentosaUnited States
-
Amicus TherapeuticsCompletedFabry DiseaseFrance, United Kingdom
-
4D Molecular TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
-
Queen Margaret UniversityUnknownCardiovascular Diseases | Metabolic Syndrome XUnited Kingdom
-
National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy | Kennedys DiseaseUnited States
-
Psyadon PharmaCompletedLesch-Nyhan DiseaseUnited States
-
Homology Medicines, IncWithdrawnMucopolysaccharidosis IIUnited States, Canada
-
Arcturus Therapeutics, Inc.RecruitingOTC Deficiency | Ornithine Transcarbamylase Deficiency | OTCDSpain, Belgium, United Kingdom, Sweden
-
Medexus Pharma, Inc.CompletedHemophilia BUnited States, France, United Kingdom, India, Israel, Italy, Poland
-
Wave Life Sciences Ltd.TerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Czechia, Canada, France, Italy, Sweden
-
Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedHemophilia BUnited States, United Kingdom, South Africa, Netherlands, Ireland, Australia
-
Catabasis PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Canada, Australia, United Kingdom, Germany, Sweden
-
Kyowa Kirin Pharmaceutical Development LtdActive, not recruitingX-Linked HypophosphatemiaSpain, Italy, United Kingdom, France, Belgium, Denmark, Germany, Hungary, Portugal, Norway, Switzerland, Israel, Netherlands, Czechia, Bulgaria, Sweden, Slovenia, Ireland, Latvia, Slovakia
-
University of CambridgeSanofiRecruiting
-
Lundquist Institute for Biomedical Innovation at...TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
-
Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
-
Cyprium Therapeutics, Inc.Enrolling by invitation
-
Eunice Kennedy Shriver National Institute of Child...Completed
-
Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy
-
Mirum Pharmaceuticals, Inc.Children's Hospital Medical Center, CincinnatiCompletedCholestasis | Peroxisomal Disorders | Adrenoleukodystrophy | Zellweger Syndrome | Infantile Refsum's DiseaseUnited States
-
Edgewise Therapeutics, Inc.Medpace, Inc.; SYSNAV; ImagingNMDRecruitingBecker Muscular DystrophyUnited States, Netherlands, United Kingdom
-
REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
-
Baxalta now part of ShireCompletedHemophilia BPoland, United Kingdom, Spain, Bulgaria, Romania, Japan, Russian Federation, Brazil, Chile, Sweden, Colombia, Ukraine, Argentina, Czechia
-
Lundquist Institute for Biomedical Innovation at...CompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VIUnited States