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Clinical Trials on X-Linked Hypophosphatemia in United States
Total 1363 results
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Medexus Pharma, Inc.TerminatedHemophilia BUnited States, United Kingdom, India
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Skulpt, Inc.National Institute of Neurological Disorders and Stroke (NINDS)CompletedDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Completed
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University of FloridaChildren's Hospital of Philadelphia; National Institute of Arthritis and Musculoskeletal... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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National Institute of Allergy and Infectious Diseases...CompletedMycosesUnited States
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University of UtahNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsTerminatedErythropoietic Protoporphyria (EPP) | X Linked Erythropoietic ProtoporphyriaUnited States
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SanofiCompletedHemophilia A | Hemophilia BBulgaria, Switzerland, United Kingdom, United States, Russian Federation
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Bioverativ Therapeutics Inc.Swedish Orphan Biovitrum; Syntonix Pharmaceuticals, Inc.Completed
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CSL BehringEnrolling by invitation
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States
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Processa PharmaceuticalsTerminated
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Massachusetts General HospitalCompletedDuchenne Muscular Dystrophy | Dystrophinopathy | Becker's Muscular DystrophyUnited States
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal DysplasiaUnited States
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada, United Arab Emirates, United Kingdom
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National Institute of Allergy and Infectious Diseases...TerminatedChronic Granulomatous DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...Terminated
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National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous DiseaseUnited States
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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The University of Texas Health Science Center,...Samsung ElectronicsCompletedChest X-ray for Clinical EvaluationUnited States
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University of California, San FranciscoUniversity of Washington; California Institute of TechnologyRecruiting
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Ohio State UniversityUniversity of Colorado, Denver; University of California, Los Angeles; Vanderbilt... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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Summit TherapeuticsCompletedModified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced DietMuscular Dystrophy, DuchenneUnited Kingdom
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Indiana UniversityCompletedChronic Kidney DiseaseUnited States
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal DysplasiaUnited States
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... and other collaboratorsRecruitingALS | Kennedy Disease | MND (Motor Neurone DIsease) | PLS | PMA - Progressive Muscular Atrophy | PBP - Progressive Bulbar PalsyUnited States, Italy
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Sarepta Therapeutics, Inc.TerminatedMuscular Dystrophy, DuchenneUnited States, Canada
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Daiichi Sankyo, Inc.CompletedHyperphosphatemiaUnited States
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Ultragenyx Pharmaceutical IncTerminatedHemophilia BUnited States, United Kingdom, Bulgaria
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CSL BehringRecruiting
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Dart Therapeutics. LLCCompletedDuchenne Muscular DystrophyUnited States
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Shriners Hospitals for ChildrenCompletedDuchenne Muscular DystrophyUnited States
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University of Colorado, DenverCompletedChronic Granulomatous DiseaseUnited States
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Children's Healthcare of AtlantaWithdrawnScoliosis | Duchenne's Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...UnknownDuchenne Muscular DystrophyUnited States, Canada
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Baylor College of MedicineAicardi Syndrome FoundationRecruitingBrain Disorders | Aicardi SyndromeUnited States
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New York Presbyterian HospitalCompletedHemophilia A | Hemophilia BUnited States
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States, Canada
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PTC TherapeuticsMuscular Dystrophy AssociationCompletedDuchenne Muscular DystrophyUnited States