- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on X-rays
Total 1898 results
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Tang-Du HospitalRecruitingDiabetes Mellitus Type 2 | Mild Cognitive Impairment | Metabolic Syndrome XChina
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Masonic Cancer Center, University of MinnesotaRecruitingAplastic Anemia | Dyskeratosis CongenitaUnited States
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Boston Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingLimb-girdle Muscular Dystrophy | Neuromuscular; Disorder, Hereditary | Duchenne/Becker Muscular DystrophyUnited States
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National Institute of Allergy and Infectious Diseases...Active, not recruitingChronic Granulomatous Disease TransplantUnited States
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David WilliamsActive, not recruitingWiskott-Aldrich SyndromeUnited States
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Stealth BioTherapeutics Inc.CompletedBarth SyndromeUnited States
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University of PittsburghRespirtech, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Fondazione TelethonOspedale San RaffaeleActive, not recruitingWiskott-Aldrich SyndromeItaly, United States
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American Thrombosis and Hemostasis NetworkTakeda; CSL Behring; OctapharmaCompletedHemophilia A | Hemophilia B | Hemophilia | Hemophilia A With Inhibitor | Haemophilia | Hemophilia B With Inhibitor | Haemophilia A Without Inhibitor | Haemophilia B Without InhibitorUnited States
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Ultragenyx Pharmaceutical IncTerminatedOrnithine Transcarbamylase DeficiencyUnited States
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...Enrolling by invitationGranulomatous Disease, ChronicUnited States, Canada
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National Institute of Allergy and Infectious Diseases...CompletedAtherosclerosis | Chronic Granulomatous Disease (CGD)United States
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GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
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GlaxoSmithKlineCompletedWiskott-Aldrich SyndromeUnited States
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GenethonHôpital Necker-Enfants MaladesCompleted
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Masonic Cancer Center, University of MinnesotaCompletedAplastic Anemia | Dyskeratosis CongenitaUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Netherlands, Austria, Spain, Germany, Macedonia, The Former Yugoslav Republic of, Taiwan, United Kingdom, Italy, Malaysia, Thailand, France, Greece, Turkey, Japan, South Africa, Romania
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National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous Disease | Communicable DiseaseUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Sweden, Spain, Germany, United Kingdom, Denmark, France, Japan
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia B | HaemostasisUnited States
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Assistance Publique - Hôpitaux de ParisSanofiCompletedCoronary Artery Disease | Diabetes Mellitus | Atherosclerosis | Metabolic Syndrome XFrance
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease | InfectionUnited States
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Massachusetts General HospitalUniversity of Pittsburgh; Boston Children's Hospital; Brigham and Women's Hospital and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Myotonic Dystrophy | Facioscapulohumeral Muscular DystrophyUnited States
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Cumberland PharmaceuticalsVanderbilt University Medical CenterRecruitingCardiomyopathy, Dilated | Duchenne Muscular Dystrophy CardiomyopathyUnited States
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National Institute of Allergy and Infectious Diseases...Enrolling by invitationChronic Granulomatous Disease | p47 | Autosomal RecessiveUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Canada, United Kingdom, France, Malaysia, Brazil, Croatia, Germany, Italy, Japan, Taiwan
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GenethonActive, not recruitingWiskott-Aldrich SyndromeUnited Kingdom, France
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Washington University School of MedicineCompleted
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Northwell HealthNational Cancer Institute (NCI); University of California, San DiegoCompletedHemophilia A | Hemophilia B | HemarthrosesUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Netherlands, Austria, Spain, Germany, Macedonia, The Former Yugoslav Republic of, Taiwan, United Kingdom, Italy, Malaysia, Thailand, France, Greece, Russian Federation, Turkey, Japan, South Africa, Romania
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Capital Research Institute of PediatricsUnknownWiskott-Aldrich Syndrome
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St. Jude Children's Research HospitalCompletedWiskott-Aldrich SyndromeUnited States
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Wyeth is now a wholly owned subsidiary of PfizerCompletedBecker Muscular Dystrophy | Facioscapulohumeral Muscular Dystrophy | Limb-Girdle Muscular DystrophyUnited States
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American Thrombosis and Hemostasis NetworkLFB USA, Inc.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorUnited States
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American Thrombosis and Hemostasis NetworkGenentech, Inc.Active, not recruitingHemophilia A With Inhibitor | Hemophilia B With Inhibitor | Haemophilia A Without Inhibitor | Haemophilia B Without InhibitorUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia BUnited States, Switzerland, Germany
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Baylor College of MedicineActive, not recruitingFocal Dermal Hypoplasia (FDH) | Goltz SyndromeUnited States
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Stealth BioTherapeutics Inc.AvailableMitochondrial Diseases | Barth Syndrome
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Hacettepe UniversitySuleyman Demirel UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Posture Disorders in Children | Ambulation Disorder, NeurologicTurkey
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Catalyst BiosciencesCompletedHemophilia A | Hemophilia B | Hemophilia A With Inhibitor | Hemophilia B With Inhibitor | Hemophilia A Without Inhibitor | Hemophilia B Without InhibitorBulgaria, Russian Federation
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...CompletedWiskott-Aldrich SyndromeUnited States, Canada
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Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, Spain, United Kingdom, France, Germany
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University of TorontoCanadian Institutes of Health Research (CIHR); Canadian Diabetes Association; The Physicians' Services Incorporated FoundationUnknownCardiovascular Diseases | Stroke | Hypertension | Diabetes Mellitus, Type 2 | Gout | Metabolic Syndrome XCanada
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The Korean Society of Pediatric Hematology OncologyCompletedWiskott-Aldrich SyndromeKorea, Republic of
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Sidney Kimmel Cancer Center at Thomas Jefferson...TerminatedHodgkin's Lymphoma | Non-Hodgkin's Lymphoma | Acute Leukemia | Hematologic Malignancies | Myeloma | Myelodysplastic Syndromes (MDS) Other Than RA or RARS Subtypes | Chronic Myelogenous (or Myeloid) Leukemia (CML) Resistant to STI TherapyUnited States
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Children's Hospital Los AngelesLucile Packard Children's HospitalTerminatedMetabolic Diseases | Stem Cell Transplantation | Chronic Granulomatous Disease | Bone Marrow Transplantation | Thalassemia | Wiskott-Aldrich Syndrome | Genetic Diseases | Peripheral Blood Stem Cell Transplantation | Pediatrics | Diamond-Blackfan Anemia | Allogeneic Transplantation | Combined Immune Deficiency | X-linked Lymphoproliferative Disease
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Sardocor Corp.Not yet recruitingDMD-Associated Dilated Cardiomyopathy
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National Institute for Mother and Child Health...Marie Curie Emergency Children's Hospital, Bucharest; Victor Gomoiu Children...RecruitingChronic Granulomatous DiseaseRomania
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Ultragenyx Pharmaceutical IncActive, not recruitingOrnithine Transcarbamylase (OTC) DeficiencyCanada, United States, France, Spain, United Kingdom
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Fondazione TelethonOspedale San RaffaeleCompleted