- ICH GCP
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Clinical Trials on X-koblet kreatinmangel
Total 1801 results
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TakedaCompletedMucopolysaccharidosis (MPS)Brazil
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Green Cross CorporationCompleted
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Beacon TherapeuticsRecruitingX-Linked Retinitis PigmentosaUnited States
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Taiyuan Central Hospital of Shanxi Medical UniversityCompleted
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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Rush University Medical CenterCompletedFragile X Tremor/Ataxia SyndromeUnited States
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University of ConnecticutCompleted
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Chinese Academy of SciencesCalifornia Walnut CommissionCompleted
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Wageningen UniversityAlpro FoundationCompleted
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Hannover Medical SchoolCompleted
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Health Enhancement Products, Inc.University of YaoundeCompleted
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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University Hospital, MontpellierAssociation Xtraordinaire sub-group DDX3X; GenidaUnknownIntellectual Developmental Disorder | X-LINKEDFrance
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Uskudar UniversityRecruitingLesch-Nyhan SyndromeTurkey
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ShireCompletedHunter SyndromeUnited States, Spain, Canada, United Kingdom, Mexico, Australia, France
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Green Cross CorporationCompleted
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Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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ShireCompleted
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Green Cross CorporationUnknownThe Long-term Safety Study of Idursulfase-beta in Hunter Syndrome(Mucopolysaccharidosis II) PatientsHunter SyndromeKorea, Republic of
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Institute for Neurodegenerative DisordersCompletedParkinson Disease | Alzheimer Disease | Mild Cognitive Impairment | Fragile X Syndrome | Huntington Disease | Autistic Spectrum DisordersUnited States
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Boehringer IngelheimCompletedHypertension | Metabolic Syndrome XFrance
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Randi J. Hagerman, MDCompletedFragile X-associated Tremor/Ataxia SyndromeUnited States
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National Institute of Diabetes and Digestive and...Massachusetts General HospitalCompletedMetabolic Syndrome XUnited States
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Utah State UniversityCompletedInflammation | Metabolic Syndrome XUnited States
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Foundation Research, FloridaGlaxoSmithKline; Abbott; Kos PharmaceuticalsCompletedInsulin Resistance | Metabolic Syndrome XUnited States
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Far Eastern Memorial HospitalNational Taiwan University HospitalUnknownInsulin Resistance | Hemodialysis | Metabolic Syndrome XTaiwan
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Tehran University of Medical SciencesUnknownMetabolic Syndrome XIran, Islamic Republic of
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Universidad Juárez Autónoma de TabascoUnknownMetabolic Syndrome X
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Shanghai University of Traditional Chinese MedicineCompletedMetabolic Syndrome X
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Duke UniversityRecruiting
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National Institute of Arthritis and Musculoskeletal...CompletedIchthyosis | Ichthyosis, X-Linked | Ichthyosis, Lamellar | Darier Disease | Hailey-Hailey Disease | Hyperkeratosis, Epidermolytic | KeratodermaUnited States
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ShireCompletedHunter SyndromeUnited States, United Kingdom
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National Taiwan University HospitalUnknownRett Syndrome | Tourette Syndrome | Tic DisordersTaiwan
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Universidad de GuanajuatoCompletedDown Syndrome | Metabolic Syndrome XMexico
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The First Hospital of Jilin UniversityNot yet recruitingGastric Cancer | Magnetic Resonance Imaging | Neoadjuvant Chemotherapy | Neoadjuvant Immunotherapy | Tomography, X-Ray Computed
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Universidade do PortoMerck Serono International SA; Centro Hospitalar de Vila Nova de Gaia/EspinhoCompletedInsulin Resistance | Metabolic Syndrome X | Diastolic DysfunctionPortugal
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Pontificia Universidad Catolica de ChileCompletedOxidative Stress | Metabolic Syndrome XChile
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Kyowa Kirin Pharmaceutical Development LtdActive, not recruitingX-Linked HypophosphatemiaSpain, Italy, United Kingdom, France, Belgium, Denmark, Germany, Hungary, Portugal, Norway, Switzerland, Israel, Netherlands, Czechia, Bulgaria, Sweden, Slovenia, Ireland, Latvia, Slovakia
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ShireCompleted
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis (MPS)United States, Argentina, Mexico, Spain, United Kingdom
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National Institute of Neurological Disorders and...CompletedMotor Neuron DiseaseUnited States
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Psyadon PharmaCompletedLesch-Nyhan DiseaseUnited States
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
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Norwegian University of Life SciencesTineCompleted
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Fundación para el Fomento de la Investigación Sanitaria...AINIATechnology CenterCompletedOverweight | Dyslipidemias | Metabolic X Syndrome
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University of British ColumbiaVancouver General HospitalWithdrawn