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Clinical Trials on X-linked Lymphoproliferative Syndrome
Total 2936 results
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Baylor College of MedicineActive, not recruitingFocal Dermal Hypoplasia (FDH) | Goltz SyndromeUnited States
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Beacon TherapeuticsEnrolling by invitationX-Linked Retinitis PigmentosaUnited States
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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University of California, San FranciscoUniversity of Washington; California Institute of TechnologyRecruiting
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Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital for... and other collaboratorsRecruiting
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Colombia
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Homology Medicines, IncWithdrawnMucopolysaccharidosis IIUnited States, Canada
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIBrazil
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ShireCompletedMucopolysaccharidosis IIUnited States, United Kingdom, Brazil, Germany
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AO GENERIUMCompletedA Multi-cohort Study of the Tolerance, Safety, and Pharmacokinetics of GNR-055 in Healthy VolunteersMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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GlaxoSmithKlineCompletedMucopolysaccharidosis IIJapan
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Green Cross CorporationUnknownMucopolysaccharidosis II
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Shanghai Children's HospitalRecruitingAlport Syndrome, X-LinkedChina
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University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease-associated ColitisUnited States
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National Institute of Allergy and Infectious Diseases...Enrolling by invitationChronic Granulomatous Disease | Inflammatory Bowel DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...WithdrawnChronic Granulomatous Diseases (CGD) and Liver LesionsUnited States
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRecruitingRestless Legs Syndrome | AdrenoleukodystrophyUnited States, Netherlands
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TakedaCompletedMucopolysaccharidosis (MPS)Brazil
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The University of Hong KongQueen Mary Hospital, Hong Kong; Kowloon Hospital, Hong Kong; Castle Peak Hospital and other collaboratorsCompletedSchizophrenia | Schizophrenia Spectrum and Other Psychotic Disorders | Metabolic Syndrome xHong Kong
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Baylor College of MedicineCompletedMetabolic Syndrome X | Heart Failure, CongestiveUnited States
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Florida Atlantic UniversityBayerCompletedCardiovascular Diseases | Atherosclerosis | Metabolic Syndrome XUnited States
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Fred Hutchinson Cancer CenterCompletedMetabolism, Inborn Errors | Granulomatous Disease, ChronicUnited States
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Institute for Neurodegenerative DisordersCompletedParkinson Disease | Alzheimer Disease | Mild Cognitive Impairment | Fragile X Syndrome | Huntington Disease | Autistic Spectrum DisordersUnited States
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Beacon TherapeuticsRecruitingX-Linked Retinitis PigmentosaUnited States
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Spain, Denmark, France, Italy, Netherlands, Switzerland
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University Hospital, MontpellierAssociation Xtraordinaire sub-group DDX3X; GenidaUnknownIntellectual Developmental Disorder | X-LINKEDFrance
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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University of British ColumbiaVancouver Coastal Health Research InstituteUnknownPsychotic Disorders | Metabolic Syndrome xCanada
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University of Campinas, BrazilFundação de Amparo à Pesquisa do Estado de São PauloCompletedObesity | Insulin Resistance | Metabolic Syndrome XBrazil
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University Hospital, Clermont-FerrandInstitut National de la Recherche AgronomiqueUnknownMetabolic Syndrome X | Dysmetabolic Iron Overload SyndromeFrance
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Baylor College of MedicineNational Center for Research Resources (NCRR)CompletedObesity | Metabolic Syndrome X | Heart Failure, Congestive
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University of Colorado, DenverCompletedTurner Syndrome | Turner Syndrome Mosaicism, 45, X/46, XX or XY | Turner Syndrome Mosaicism 46,X,I(X)(Q10)/45,X | Turner Syndrome Karyotype 46,X With Abnormal Sex Chromosome , Except I(Xq)United States
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National Institute of Allergy and Infectious Diseases...Not yet recruitingHyper-Immunoglobulin E. Syndrome (HEIS) | Chronic Granulomatous Disease (CGD)United States
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University of Maryland, BaltimoreChildren's Hospital of PhiladelphiaWithdrawnOsteoporosis Pseudoglioma SyndromeUnited States
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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National Institute of Allergy and Infectious Diseases...CompletedMycosesUnited States
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National Institute of Arthritis and Musculoskeletal...CompletedIchthyosis | Ichthyosis, X-Linked | Ichthyosis, Lamellar | Darier Disease | Hailey-Hailey Disease | Hyperkeratosis, Epidermolytic | KeratodermaUnited States
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaUnited States
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Kyowa Kirin Pharmaceutical Development LtdActive, not recruitingX-Linked HypophosphatemiaSpain, Italy, United Kingdom, France, Belgium, Denmark, Germany, Hungary, Portugal, Norway, Switzerland, Israel, Netherlands, Czechia, Bulgaria, Sweden, Slovenia, Ireland, Latvia, Slovakia
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National Institute of Neurological Disorders and...CompletedMotor Neuron DiseaseUnited States
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University of IowaTerminatedObesity | Metabolic Syndrome XUnited States
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Ospedale San Giovanni BellinzonaSwiss Heart FoundationCompletedAcute Myocardial Infarction | Takotsubo Cardiomyopathy | Cardiac X SyndromeSwitzerland
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German Institute of Human NutritionUniversity Hospital Tuebingen; Ernst von Bergmann Hospital; Ministry of Food... and other collaboratorsCompletedMetabolic Diseases | Obesity | Diabetes Mellitus, Type 2 | Nutrition Disorders | Body Weight | Metabolic Syndrome xGermany
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted