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Clinical Trials on X-linked Lymphoproliferative Syndrome
Total 2936 results
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationCompleted
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National Taiwan University HospitalUnknown
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Maastricht University Medical CenterCompleted
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineCompletedRett Syndrome
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineCompleted
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.National Institutes of Health (NIH)CompletedFragile X SyndromeUnited States
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Soma JyonouchiBaylor College of MedicineCompletedX-linked Thrombocytopenia | Wiskott-Aldrich Syndrome (WAS)United States
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Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUnknownRett SyndromeUnited States
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Stanford UniversityCompletedIntellectual Disability | Fragile X SyndromeUnited States
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of Alabama... and other collaboratorsRecruiting
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National Taiwan University HospitalCompletedNeurologic Disorder | Rett Syndrome
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Jazz PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Spain, Italy, United Kingdom
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IRCCS San RaffaeleFondazione TelethonRecruitingChronic Granulomatous Disease X-linked (X-CGD)Italy
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Astellas Gene TherapiesCompletedX-linked Myotubular MyopathyUnited States, France, United Kingdom, Canada, Germany
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University of FloridaAudentes TherapeuticsCompletedX-linked Myotubular MyopathyUnited States
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Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
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Azienda Ospedaliera Universitaria SeneseEuropean Institute of Oncology; Kolfarma s.r.l. - ItalyCompletedEpilepsy | Quality of Life | Dysbiosis | Rett SyndromeItaly
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Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCDKL5 | Rett Syndrome | MECP2 Duplication | FOXG1 DisordersUnited States
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaboratorsRecruitingX Linked Myotubular MyopathyUnited Kingdom, Canada, United States
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Children's Hospital Medical Center, CincinnatiRecruitingFragile X SyndromeUnited States
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Esoterix Genetic Laboratories, LLCUnknownFragile X SyndromeUnited States
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome | MECP2 Duplication Disorder | Rett-related DisorderUnited States
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National Institute of Allergy and Infectious Diseases...RecruitingGranuloma | Granulomatous Disease, Chronic | Leukocyte Disease | Genetic Disease, X-Linked | Genetic Disease, InbornUnited States
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University Hospital, ToursCompletedHealthy Volunteers | Autism | Fragile-X Syndrome (FXS)France
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Massachusetts General HospitalNational Institutes of Health (NIH)UnknownHealthy | Fragile X SyndromeUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...CompletedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia | Hemophagocytic Lymphohistiocytosis (HLH) | Non Hodgkins Lymphoma | Familial Hemophagocytic Lymphohistiocytosis (FLH) | Viral-associated Hemophagocytic Syndrome (VAHS) | X-linked Lymphoproliferative...United States
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Children's Hospital Medical Center, CincinnatiNot yet recruitingAutism Spectrum Disorder | Fragile X Syndrome
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Murdoch Childrens Research InstituteUniversity of Sydney; Sydney Children's Hospitals Network; Women's and Children... and other collaboratorsActive, not recruitingAutosomal Recessive Disorder | X-Linked Genetic DiseasesAustralia
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Astellas Gene TherapiesCompletedMales With X-linked Myotubular Myopathy (XLMTM)United States, United Kingdom
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Ariel UniversityAssociazione Italiana Rett (AIRETT)Not yet recruitingRett SyndromeItaly
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Indiana UniversityCompletedFragile X Syndrome | Autism Spectrum DisordersUnited States
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome, Preserved Speech Variant | Mecp2 Duplication Syndrome | Rett-related DisordersUnited States
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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Ionis Pharmaceuticals, Inc.RecruitingMethyl CpG Binding Protein 2 (MECP2) Duplication SyndromeUnited States
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National Eye Institute (NEI)CompletedRetinoschisis | X-LinkedUnited States
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Ariel UniversityASST Santi Paolo e CarloCompleted
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Edimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal DysplasiaUnited States
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Nova Mentis Life Science CorpKGK Science Inc.RecruitingCognitive Dysfunction | Fragile X Syndrome | BehaviorCanada
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RespireRxFRAXA Research FoundationCompletedFragile X Syndrome | AutismUnited States
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Bambino Gesù Hospital and Research InstituteAutour Des Williams; AceaUnknownFragile X Syndrome | Williams SyndromeItaly
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Baylor College of MedicineCompleted
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Hospices Civils de LyonUnknownX-linked Mental RetardationFrance
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Chronic Granulomatous DiseaseUnited States
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Hubert Serve, Prof., MDUnknown
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Cure CMDUniversity of Michigan; Congenital Muscle Disease International RegistrCompleted