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Clinical Trials on X-Linked Hypophosphatemia in United Kingdom
Total 1358 results
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National Human Genome Research Institute (NHGRI)Completed
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Kevin FlaniganWithdrawnDuchenne Muscular DystrophyUnited States
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Alan Neuromedical Technologies, LLCCompleted
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Cooperative International Neuromuscular Research...United States Department of DefenseTerminated
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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Dyne TherapeuticsRecruitingDuchenne Muscular Dystrophy (DMD)United States, Belgium, Canada, United Kingdom, Australia, Spain, Italy
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Institute for Neurodegenerative DisordersCompletedParkinson Disease | Alzheimer Disease | Mild Cognitive Impairment | Fragile X Syndrome | Huntington Disease | Autistic Spectrum DisordersUnited States
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Eli Lilly and CompanyTerminatedMuscular Dystrophy, DuchenneGermany, United States, Spain, Belgium, France, Italy, Taiwan, Netherlands, Turkey, Korea, Republic of, Argentina, Canada, Japan, Puerto Rico, Russian Federation, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterCompletedBecker Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterTerminatedMuscular DystrophyUnited States
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Cedars-Sinai Medical CenterParent Project Muscular DystrophyCompleted
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Cedars-Sinai Medical CenterCompleted
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationCompleted
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National Center for Research Resources (NCRR)Children's National Research InstituteCompletedMuscular Dystrophy, DuchenneUnited States
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Sangamo TherapeuticsTerminated
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
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University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Cure Rare Disease, IncUniversity of Massachusetts, WorcesterActive, not recruiting
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Craig McDonald, MDCardero Therapeutics, Inc.Completed
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University of FloridaEngage Health Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of FloridaCureDuchenneCompletedMuscular Dystrophy, DuchenneUnited States
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University of FloridaUnited States Department of DefenseCompletedDuchenne Muscular DystrophyUnited States
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
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Genzyme, a Sanofi CompanyTerminatedFabry Disease | Alpha Galactosidase A DeficiencyUnited States, Austria, United Kingdom
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada
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CSL BehringRecruiting
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Cedars-Sinai Medical CenterCompleted
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University of South FloridaMerck Sharp & Dohme LLCTerminatedX-linked Agammaglobulinemia | Specific Antibody Deficiency | Common Variable Immune DeficiencyUnited States
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseFrance, Poland, United States, Russian Federation, United Kingdom
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMuscular Dystrophy, DuchenneUnited States
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Cooperative International Neuromuscular Research...Completed
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BSpain, Taiwan, United Kingdom, Italy, Germany, United States, South Africa, Australia, Egypt, Poland, Armenia, France, India, Canada, Brazil, Turkey
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St. Jude Children's Research HospitalRecruitingHemophilia B | Gene TherapyUnited States
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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FibroGenActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom