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Clinical Trials on X-Linked Hypophosphatemia in United Kingdom
Total 1362 results
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Eli Lilly and CompanyTerminatedMuscular Dystrophy, DuchenneGermany, United States, Spain, Belgium, France, Italy, Taiwan, Netherlands, Turkey, Korea, Republic of, Argentina, Canada, Japan, Puerto Rico, Russian Federation, United Kingdom
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St. Jude Children's Research HospitalNot yet recruiting
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Medpace, Inc.CompletedBecker Muscular DystrophyUnited States
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Kevin FlaniganSarepta Therapeutics, Inc.Completed
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Kevin FlaniganActive, not recruitingDuchenne Muscular DystrophyUnited States
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Solid Biosciences Inc.CompletedDuchenne Muscular DystrophyUnited States
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Megan WaldropAudentes TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited States
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Roxanna Marie BendixenTerminatedDuchenne Muscular DystrophyUnited States
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedBecker Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Completed
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University of Colorado, DenverCompleted
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National Human Genome Research Institute (NHGRI)CompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalCompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalAsklepios Biopharmaceutical, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRecruitingRestless Legs Syndrome | AdrenoleukodystrophyUnited States, Netherlands
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BSpain, Taiwan, United Kingdom, Italy, Germany, United States, South Africa, Australia, Poland, Armenia, France, India, Canada, Brazil, Turkey, Egypt
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Novartis PharmaceuticalsRecruitingNLRC4-GOF, AIFEC (Autoinflammation With Infantile Enterocolitis), XIAP Deficiency, CDC42 MutationsSpain, France, United States, Canada, Japan, United Kingdom, Turkey, Czechia, Italy
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CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
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Kaiser PermanenteKeryx BiopharmaceuticalsCompletedHyperphosphatemiaUnited States
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumTerminatedHemophilia A | Hemophilia BUnited States
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Cedars-Sinai Medical CenterCompleted
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Washington University School of MedicineBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIUnited States, Canada
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St. Jude Children's Research HospitalRecruitingHemophilia B | Gene TherapyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedDuchenne Muscular DystrophyUnited States
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRecruitingBecker Muscular DystrophyUnited States, Italy
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Equilibra Bioscience LLCRecruitingHemophilia A | Hemophilia B | Healthy ParticipantsUnited States
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Allergy and Asthma Consultants, Wichita, KansasAidan Foundation; Neil H. Riordan PhDCompletedDuchenne's Muscular DystrophyUnited States
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National Institute of Neurological Disorders and...CompletedMuscular Dystrophy | Muscular DiseaseUnited States
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National Institute of Allergy and Infectious Diseases...Completed
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National Institute of Neurological Disorders and...CompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
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PfizerTerminatedHemophilia A | Hemophilia BUnited States
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseFrance, Poland, United States, Russian Federation, United Kingdom
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseFrance, Poland, United States, Russian Federation, United Kingdom
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ClasadoUniversity of ReadingCompletedMetabolic Syndrome XUnited Kingdom
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Solid Biosciences Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States
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ArdelyxCompletedHyperphosphatemiaUnited States, Poland, United Kingdom, Slovakia
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Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States
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Processa PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States
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The Duchenne RegistryParent Project Muscular DystrophyRecruiting
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Akashi TherapeuticsTerminatedDuchenne Muscular DystrophyUnited States