- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on X-Linked Hypophosphatemia in United Kingdom
Total 1358 results
-
RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedFragile X Syndrome (FXS)United States
-
Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
-
SpinogenixAvance Clinical Pty Ltd.Not yet recruiting
-
Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingFragile X SyndromeUnited States
-
National Institute of Mental Health (NIMH)CompletedHealthy Volunteers | Fragile X SyndromeUnited States
-
Stanford UniversityCompletedFragile X SyndromeUnited States
-
University of California, DavisCompletedFragile X Syndrome | Genetic DiseasesUnited States
-
University of California, DavisCompleted
-
University of California, DavisThe National Fragile X FoundationCompleted
-
Stanford UniversityCompleted
-
Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRecruitingPyruvate Dehydrogenase Complex Deficiency | Pyruvate Dehydrogenase E1 Alpha Deficiency | Pyruvate Dehydrogenase E1-Beta Deficiency | Pyruvate Dehydrogenase E2 Deficiency | Pyruvate Dehydrogenase Phosphatase DeficiencyUnited Kingdom
-
Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Belgium, Australia, Israel, Switzerland, Germany, France, Canada, Denmark, Indonesia, Italy, Netherlands, Spain, Sweden, Turkey, United Kingdom
-
Jazz PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Spain, Italy, United Kingdom
-
Children's Hospital Medical Center, CincinnatiRush University Medical CenterCompleted
-
Craig EricksonHealx LimitedRecruitingFragile X SyndromeUnited States
-
Elizabeth Berry-KravisCompletedFragile X SyndromeUnited States
-
Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
-
Massachusetts General HospitalNational Institutes of Health (NIH)UnknownHealthy | Fragile X SyndromeUnited States
-
Rowan UniversityUniversity of Pennsylvania; FRAXA Research FoundationUnknown
-
BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
-
NeuroVia, Inc.UnknownX-Linked AdrenoleukodystrophyUnited States
-
Thomas S. ScanlanWithdrawnAdrenomyeloneuropathy | X-Linked AdrenoleukodystrophyUnited States
-
Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
-
Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
-
Summit TherapeuticsCompletedModified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced DietMuscular Dystrophy, DuchenneUnited Kingdom
-
Imperial College LondonSarepta Therapeutics, Inc.; Department of Health, United KingdomCompletedDuchenne Muscular DystrophyUnited Kingdom
-
National Human Genome Research Institute (NHGRI)CompletedGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets Type2United States
-
Children's Hospital Medical Center, CincinnatiCompleted
-
Randi J. Hagerman, MDCompleted
-
Indiana UniversityIndiana Clinical and Translational Sciences InstituteCompleted
-
Indiana University School of MedicineCompletedFragile X SyndromeUnited States
-
Stanford UniversityNational Institute of Mental Health (NIMH); Autism SpeaksCompleted
-
Denali Therapeutics Inc.CompletedMucopolysaccharidosis IIUnited Kingdom, United States, Italy, Netherlands
-
Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Spain
-
NeuropharmCompleted
-
Rett Syndrome Research TrustDuke UniversityCompletedRett SyndromeUnited States
-
Montefiore Medical CenterRett Syndrome Research TrustCompleted
-
Montefiore Medical CenterRett Syndrome Research TrustCompletedRett SyndromeUnited States
-
Edimer PharmaceuticalsCompleted
-
Eunice Kennedy Shriver National Institute of Child...University of WashingtonUnknownWiskott-Aldrich Syndrome | Leukocyte Adhesion Deficiency Syndrome | X-Linked Agammaglobulinemia | X-Linked Hyper IgM SyndromeUnited States
-
Sheffield Children's NHS Foundation TrustSheffield Hallam University; National Institute for Health Research, United... and other collaboratorsActive, not recruiting
-
GenethonInstitute of MyologyUnknownDuchenne Muscular DystrophyUnited Kingdom, France
-
Stanford UniversityThe John Merck FundCompletedFragile X Syndrome | Disruptive BehaviorUnited States
-
Stanford UniversityCompletedDevelopmental Disabilities | Fragile X SyndromeUnited States
-
MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasCompletedGene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaUnited Kingdom, United States
-
Novo Nordisk A/SEnrolling by invitationHaemophilia BNetherlands, United Kingdom
-
Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
-
ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
-
Rett Syndrome Research TrustCompleted
-
Hugo W. Moser Research Institute at Kennedy Krieger...Terminated