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- US Clinical Trials Registry
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Clinical Trials on X-linked Lymphoproliferative Syndrome 2
Total 3521 results
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NeuropharmCompleted
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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Fundación Pública Andaluza para la Investigación...Delos ClinicalCompleted
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Recruiting
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Neurogene Inc.RecruitingRett SyndromeUnited States
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University of SienaRecruiting
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Vyant BioNot yet recruiting
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Rett Syndrome Research TrustVanderbilt University Medical CenterCompleted
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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ACADIA Pharmaceuticals Inc.Completed
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Rett Syndrome Research TrustCompleted
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National Human Genome Research Institute (NHGRI)CompletedRett SyndromeUnited States
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Anagnostou, Evdokia, M.D.Unity Health Toronto; Holland Bloorview Kids Rehabilitation Hospital; Ontario...Unknown
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Assistance Publique Hopitaux De MarseilleUnknown
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationCompleted
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Sheba Medical CenterUltragenyx Pharmaceutical IncUnknown
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Central Hospital, Nancy, FranceCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...Terminated
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Sheba Medical CenterUnknown
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Maastricht University Medical CenterCompleted
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Faculdades Metropolitanas UnidasUniversity of Sao PauloCompleted
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityCompletedRett Syndrome
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Eunice Kennedy Shriver National Institute of Child...UnknownRett SyndromeUnited States
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Ovid Therapeutics Inc.Completed
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IRCCS Fondazione Stella MarisRecruitingCreatine Deficiency, X-linked | Creatine Deficiency Syndrome Due to Gamt DeficiencyItaly
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingX-linked Myotubular Myopathy | Centronuclear Myopathy | Myotubular Myopathy | Myotubular Myopathy 1 | Myotubular (Centronuclear) Myopathy | Centronuclear Myopathy, X-LinkedUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSevere Combined Immunodeficiency, X-LinkedUnited Kingdom
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Wiskott-Aldrich Syndrome | X-linked Agammaglobulinemia | Primary Immune Deficiency Disorders | Hyper-IgM SyndromeUnited States, Chile, Israel
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Children's Hospital of Fudan UniversityRecruiting
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRecruiting
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... and other collaboratorsRecruiting
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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Edison Pharmaceuticals IncWithdrawn
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Anavex Life Sciences Corp.Completed
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompleted
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Neuren Pharmaceuticals Limitedrettsyndrome.orgCompleted
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUnknownRett SyndromeDenmark, Israel
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Rigshospitalet, DenmarkCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)CompletedRett SyndromeUnited States
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Edison Pharmaceuticals IncCompleted
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Boston Children's HospitalInternational Rett Syndrome FoundationCompleted
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The Cleveland ClinicTerminated
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationCompleted
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National Taiwan University HospitalUnknown
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Maastricht University Medical CenterCompleted
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineCompletedRett Syndrome
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineCompleted
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Children's Hospital of Chongqing Medical UniversityRecruiting