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Clinical Trials on X-linked Adrenal Hypoplasia Congenita
Total 2203 results
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Masonic Cancer Center, University of MinnesotaWithdrawn
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MedDay Pharmaceuticals SACompletedAdrenoleukodystrophy | Adrenomyeloneuropathy | AMNFrance, Germany, Spain
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)TerminatedAdrenoleukodystrophy | AdrenomyeloneuropathyUnited States
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Boston Children's HospitalMassachusetts General Hospital; Mayo Clinic; Karolinska University Hospital; Baylor... and other collaboratorsActive, not recruitingAplastic Anemia | Dyskeratosis Congenita | Hoyeraal Hreidarsson Syndrome | Revesz SyndromeUnited States, Norway, Sweden
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ProgenaBiomeRecruitingAutism Spectrum Disorder | Autistic Disorder | Autism | Autism, Akinetic | Autism; Atypical | Autism; Psychopathy | Autism Fragile Syndrome X | Autism With High Cognitive Abilities | Autism-Related Speech Delay | Autism, Susceptibility to, 6 | Autism Spectrum Disorder High-Functioning | Autistic Thinking | Autism... and other conditionsUnited States
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University of ZurichCompletedLeft Ventricular Noncompaction | Isolated Noncompaction of the Ventricular MyocardiumSwitzerland
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | Hyper-IgM Syndrome | X-linked AgammaglobulinaemiaUnited States, United Kingdom, Hungary
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Masonic Cancer Center, University of MinnesotaRecruiting
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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Poxel SANot yet recruiting
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Masonic Cancer Center, University of MinnesotaWithdrawnCerebral Adrenoleukodystrophy
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Completed
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Far Eastern Memorial HospitalNational Taiwan University Hospital; Fu Jen Catholic UniversityUnknownAdrenoleukodystrophyTaiwan
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University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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ACADIA Pharmaceuticals Inc.Completed
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IRCCS Eugenio MedeaAssociazione Italiana Rett (AIRett) O.n.l.u.s.Completed
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Rett Syndrome Research TrustDuke UniversityCompletedRett SyndromeUnited States
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgCompleted
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Montefiore Medical CenterRett Syndrome Research TrustCompleted
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Montefiore Medical CenterRett Syndrome Research TrustCompletedRett SyndromeUnited States
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Assistance Publique Hopitaux De MarseilleCompleted
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Medical University of ViennaCompleted
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Kyowa Kirin Co., Ltd.Active, not recruiting
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUnknownWiskott-Aldrich Syndrome | Leukocyte Adhesion Deficiency Syndrome | X-Linked Agammaglobulinemia | X-Linked Hyper IgM SyndromeUnited States
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Third Military Medical UniversityNot yet recruitingPrimary Aldosteronism Due to Aldosterone Producing Adenoma | Primary Aldosteronism Due to Adrenal Hyperplasia (Bilateral)China
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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Poxel SANot yet recruiting
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Masonic Cancer Center, University of MinnesotaRecruitingCerebral Adrenoleukodystrophy | Adrenoleukodystrophy | ALD (Adrenoleukodystrophy)United States
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Onofre, Aurora Pujol, M.D.Completed
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Hugo W. Moser Research Institute at Kennedy Krieger...TerminatedAdrenoleukodystrophyUnited States
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Onofre, Aurora Pujol, M.D.Ministerio de Sanidad, Servicios Sociales e Igualdad; Fundacion HesperiaCompleted
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Baylor College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCongenital Heart Disease | Hypoplastic Left Heart Syndrome | Transposition of the Great Arteries | Aortic Arch Hypoplasia or InterruptionUnited States
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Recruiting
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Neurogene Inc.RecruitingRett SyndromeUnited States
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University of SienaRecruiting
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Vyant BioNot yet recruiting
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Rett Syndrome Research TrustVanderbilt University Medical CenterCompleted
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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ACADIA Pharmaceuticals Inc.Completed
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Rett Syndrome Research TrustCompleted
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National Human Genome Research Institute (NHGRI)CompletedRett SyndromeUnited States
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Anagnostou, Evdokia, M.D.Unity Health Toronto; Holland Bloorview Kids Rehabilitation Hospital; Ontario...Unknown
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Assistance Publique Hopitaux De MarseilleUnknown
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationCompleted
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Sheba Medical CenterUltragenyx Pharmaceutical IncUnknown
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Central Hospital, Nancy, FranceCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...Terminated