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Clinical Trials on X-linked Adrenal Hypoplasia Congenita
Total 2205 results
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Sheba Medical CenterUnknown
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Maastricht University Medical CenterCompleted
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Faculdades Metropolitanas UnidasUniversity of Sao PauloCompleted
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityCompletedRett Syndrome
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Eunice Kennedy Shriver National Institute of Child...UnknownRett SyndromeUnited States
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Baylor College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCongenital Heart Disease | Hypoplastic Left Heart Syndrome | Transposition of the Great Arteries | Aortic Arch Hypoplasia or InterruptionUnited States
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Rush University Medical CenterEmory UniversityEnrolling by invitationTuberous Sclerosis | Fragile X Syndrome | Rett Syndrome | Hamartoma Syndrome, Multiple | Angelman Syndrome | Creatine Deficiency, X-linked | Telomeric 22Q13 Monosomy Syndrome | Chromosome 15Q, Partial DeletionUnited States
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University Hospital, Basel, SwitzerlandNovartisCompletedRett's SyndromeSwitzerland
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Hubert Serve, Prof., MDUnknown
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University of MichiganPatient-Centered Outcomes Research Institute; University of California, Los... and other collaboratorsCompletedCongenital Adrenal Hyperplasia | Hypospadias | Disorder of Sex Development | Intersex ConditionsUnited States
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Children's Hospital of Fudan UniversityRecruiting
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRecruiting
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... and other collaboratorsRecruiting
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Pitié-Salpêtrière HospitalRecruitingLaminopathies | EmerinopathiesFrance
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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Edison Pharmaceuticals IncWithdrawn
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Anavex Life Sciences Corp.Completed
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompleted
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Neuren Pharmaceuticals Limitedrettsyndrome.orgCompleted
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Telethon Kids InstituteRigshospitalet, Denmark; University of Haifa; Ariel UniversityUnknownRett SyndromeDenmark, Israel
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Rigshospitalet, DenmarkCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)CompletedRett SyndromeUnited States
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Edison Pharmaceuticals IncCompleted
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Boston Children's HospitalInternational Rett Syndrome FoundationCompleted
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The Cleveland ClinicTerminated
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationCompleted
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National Taiwan University HospitalUnknown
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Maastricht University Medical CenterCompleted
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineCompletedRett Syndrome
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineCompleted
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Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
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University of AlbertaWithdrawnHypoplastic Left Heart Syndrome | Congenital Heart Defect | TGA - Transposition of Great Arteries | Congential Absence of Heart Structure | Congenital Malformation of Heart, Unspecified | Hypoplastic Right Heart Syndrome | Congential Malformations of Aortic Valve | Congential Malformations of Great...Canada
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RecruitingRett Syndrome | Rett Syndrome, Atypical | RTTUnited States
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University Hospital PadovaRecruitingHypertension | Essential Hypertension | Hyperaldosteronism | Aldosteronism | Conn Adenoma | Aldosterone Disorder | Aldosterone-producing Adenoma | Bilateral Adrenal HyperplasiaItaly
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of Alabama... and other collaboratorsRecruiting
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National Taiwan University HospitalCompletedNeurologic Disorder | Rett Syndrome
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Jazz PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Spain, Italy, United Kingdom
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Universitaire Ziekenhuizen KU LeuvenKU LeuvenCompletedCommunication | Parent-Child Relations | Behavior, ChildBelgium
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Children's Hospital Los AngelesLucile Packard Children's HospitalTerminatedMetabolic Diseases | Stem Cell Transplantation | Chronic Granulomatous Disease | Bone Marrow Transplantation | Thalassemia | Wiskott-Aldrich Syndrome | Genetic Diseases | Peripheral Blood Stem Cell Transplantation | Pediatrics | Diamond-Blackfan Anemia | Allogeneic Transplantation | Combined Immune Deficiency | X-linked Lymphoproliferative Disease
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUnknownRett SyndromeUnited States
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Sunshine Care FoundationMassachusetts General Hospital; Jose R. Reyes Memorial Medical CenterCompletedX-Linked Dystonia ParkinsonismPhilippines
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University of British ColumbiaBiogenCompletedHemophilia A, Congenital | Hemophilia B, CongenitalCanada
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Masonic Cancer Center, University of MinnesotaTerminatedSickle Cell Disease | Thalassemia | Cerebral Adrenoleukodystrophy | Inherited Metabolic Disorders | High Risk Hematologic DisordersUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedSevere Combined Immunodeficiency | Adenosine Deaminase Deficiency | Immune System Disorder | Autosomal Recessive Disorder | Purine-Nucleoside Phosphorylase Deficiency | Severe Combined Immunodeficiency With Absence of T and B Cells | X-Linked Severe Combined ImmunodeficiencyUnited States
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Azienda Ospedaliera Universitaria SeneseEuropean Institute of Oncology; Kolfarma s.r.l. - ItalyCompletedEpilepsy | Quality of Life | Dysbiosis | Rett SyndromeItaly
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Newron Pharmaceuticals SPATerminatedRett SyndromeUnited States, India, United Kingdom, Australia, Italy
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedCDKL5 | Rett Syndrome | MECP2 Duplication | FOXG1 DisordersUnited States
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University Hospital OlomoucUniversity Hospital Ostrava; Tomas Bata Hospital, Czech Republic; General University... and other collaboratorsRecruitingCushing Syndrome | Pheochromocytoma | Adrenocortical Carcinoma | Adrenal Cortex Diseases | Adrenocortical Adenoma | Adrenal Tumor | Adrenalectomy; Status | Adrenal Mass | Adrenal Hyperplasia | Adrenal Disease | Adrenocortical Tumor | Conn Adenoma | Adrenal Gland MetastasisCzechia