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Clinical Trials on X-linked Adrenoleukodystrophy
Total 2355 results
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Seaside Therapeutics, Inc.SuspendedFragile X SyndromeUnited States
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NeuropharmCompleted
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ACADIA Pharmaceuticals Inc.CompletedRett SyndromeUnited States
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ACADIA Pharmaceuticals Inc.Completed
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IRCCS Eugenio MedeaAssociazione Italiana Rett (AIRett) O.n.l.u.s.Completed
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Rett Syndrome Research TrustDuke UniversityCompletedRett SyndromeUnited States
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgCompleted
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Montefiore Medical CenterRett Syndrome Research TrustCompleted
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Montefiore Medical CenterRett Syndrome Research TrustCompletedRett SyndromeUnited States
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Assistance Publique Hopitaux De MarseilleCompleted
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Edimer PharmaceuticalsCompleted
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Medical University of ViennaCompleted
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | Hyper-IgM Syndrome | X-linked AgammaglobulinaemiaUnited States, United Kingdom, Hungary
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUnknownWiskott-Aldrich Syndrome | Leukocyte Adhesion Deficiency Syndrome | X-Linked Agammaglobulinemia | X-Linked Hyper IgM SyndromeUnited States
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University of AlbertaSt. Justine's HospitalRecruitingNeurobehavioral Manifestations | Genetic Diseases, X-Linked | Mental Retardation, X-Linked | Intellectual Disability | Fragile X Syndrome | Sex Chromosome Disorders | Fragile X Mental Retardation Syndrome | Trinucleotide Repeat Expansion | Fra(X) Syndrome | FXSCanada
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruitingFragile X Syndrome
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Stanford UniversityThe John Merck FundCompletedFragile X Syndrome | Disruptive BehaviorUnited States
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Stanford UniversityCompletedDevelopmental Disabilities | Fragile X SyndromeUnited States
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Recruiting
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Neurogene Inc.RecruitingRett SyndromeUnited States
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University of SienaRecruiting
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Vyant BioNot yet recruiting
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Rett Syndrome Research TrustVanderbilt University Medical CenterCompleted
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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ACADIA Pharmaceuticals Inc.Completed
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Rett Syndrome Research TrustCompleted
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National Human Genome Research Institute (NHGRI)CompletedRett SyndromeUnited States
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Anagnostou, Evdokia, M.D.Unity Health Toronto; Holland Bloorview Kids Rehabilitation Hospital; Ontario...Unknown
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Assistance Publique Hopitaux De MarseilleUnknown
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationCompleted
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Sheba Medical CenterUltragenyx Pharmaceutical IncUnknown
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Central Hospital, Nancy, FranceCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...Terminated
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Sheba Medical CenterUnknown
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Maastricht University Medical CenterCompleted
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Faculdades Metropolitanas UnidasUniversity of Sao PauloCompleted
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityCompletedRett Syndrome
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Eunice Kennedy Shriver National Institute of Child...UnknownRett SyndromeUnited States
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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Fundación Pública Andaluza para la Investigación...Delos ClinicalCompleted
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University Hospital, Basel, SwitzerlandNovartisCompletedRett's SyndromeSwitzerland
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Hubert Serve, Prof., MDUnknown
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Stanford UniversityCompletedIntellectual Disability | Fragile X SyndromeUnited States
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Parc de Salut MarHospital Infantil Universitario Niño Jesús, Madrid, Spain; Hospital Universitario... and other collaboratorsCompletedDown Syndrome | Fragile X SyndromeSpain
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Jazz PharmaceuticalsGW PharmaceuticalsTerminatedRett Syndrome | RTTUnited States, Canada, Italy, Spain, United Kingdom, Australia
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Children's Hospital of Fudan UniversityRecruiting
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRecruiting
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... and other collaboratorsRecruiting