- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on X-linked Lymphoproliferative Disease
Total 14354 results
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedDuchenne Muscular DystrophyUnited States
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Washington University School of MedicineUniversity of California, Davis; Nationwide Children's Hospital; University of... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalCompletedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Children's Hospital of Eastern OntarioCompletedDuchenne Muscular DystrophyCanada
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Cooperative International Neuromuscular Research...UnknownBecker Muscular DystrophyUnited States, Canada, Italy, United Kingdom
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | BalanceTurkey
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National Human Genome Research Institute (NHGRI)Completed
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Kevin FlaniganWithdrawnDuchenne Muscular DystrophyUnited States
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyNetherlands, Belgium, Italy, Sweden
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BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
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Assiut UniversityUnknownDuchenne Muscular Dystrophy
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited Kingdom, Italy, Belgium, Netherlands, France
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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University of Sao PauloCompletedDuchenne Muscular Dystrophy
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University of Sao PauloCompletedDuchenne Muscular DystrophyBrazil
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GenethonInstitute of MyologyUnknownDuchenne Muscular DystrophyUnited Kingdom, France
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Sarepta Therapeutics, Inc.British Medical Research CouncilCompletedDuchenne Muscular DystrophyUnited Kingdom
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Kobe UniversityNobelpharma; Japan Medical AssociationUnknownMuscular Dystrophy, DuchenneJapan
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Cooperative International Neuromuscular Research...UnknownDuchenne Muscular DystrophyUnited States, Canada
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Alan Neuromedical Technologies, LLCCompleted
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Acibadem UniversityUnknownDuchenne Muscular DystrophyTurkey
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GlaxoSmithKlineCompletedMuscular DystrophiesGermany, Belgium, Turkey, Netherlands, Spain, Israel, Australia, France, United Kingdom
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University of MessinaCompleted
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Cedars-Sinai Medical CenterCompleted
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Cooperative International Neuromuscular Research...United States Department of DefenseTerminated
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationCompleted
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Rigshospitalet, DenmarkGlostrup University Hospital, CopenhagenCompletedBecker Muscular DystrophyDenmark
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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Santhera PharmaceuticalsCompletedDuchenne Muscular DystrophyBelgium
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Assistance Publique - Hôpitaux de ParisCompletedMuscular Dystrophy, DuchenneFrance
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National Center for Research Resources (NCRR)Children's National Research InstituteCompletedMuscular Dystrophy, DuchenneUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIUnited States, Canada
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Hasan Kalyoncu UniversityNot yet recruitingHemophilia A | Hemophilia B | HemophiliaTurkey
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Assiut UniversityNot yet recruitingHemophilia A | Hemophilia B
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BUnited States, Italy, Spain, Taiwan, Australia, Belgium, United Kingdom, France, Germany, India, South Africa, Canada, Poland, Armenia, Turkey
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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Regeneron PharmaceuticalsRecruitingHemophilia BUnited States, Germany, United Kingdom, Canada
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BBulgaria, United States, United Kingdom, Russian Federation, Switzerland
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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Swedish Orphan BiovitrumIQVIA Pvt. LtdTerminatedHemophilia A | Hemophilia BBulgaria, Croatia, Czechia, France, Hungary, Ireland, Italy, Romania, Slovenia, Spain, United Kingdom
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Freeline TherapeuticsTerminatedHemophilia BUnited States, United Kingdom
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University College, LondonTerminatedHemophilia BIreland, United Kingdom, Italy, United States
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CSL BehringCompletedHemophilia BGermany, Denmark, Netherlands
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, Canada, China, France, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, Italy, Japan, South Africa, Spain, Taiwan
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BUnited States, Australia, China, Denmark, France, Israel, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Germany, India, South Africa, Spain, Taiwan, Hungary, Italy
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Sangamo TherapeuticsTerminated
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Catalyst BiosciencesCompletedHemophilia BSouth Africa
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Baxalta now part of ShireCompletedHemophilia BKorea, Republic of
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Baxalta now part of ShireCompleted
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Medexus Pharma, Inc.CompletedHemophilia BUnited States, France, United Kingdom, India, Israel, Italy, Poland