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- US Clinical Trials Registry
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Clinical Trials on X-linked Severe Combined Immunodeficiency
Total 1627 results
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Wuerzburg University HospitalKyowa Kirin, Inc.Completed
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Amicus TherapeuticsCompletedFabry DiseaseJapan, Taiwan, Turkey, United States, Brazil
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ShireNo longer available
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CENTOGENE GmbH RostockShire Human Genetic Therapies, Inc.CompletedCerebrovascular AccidentAustria, Belgium, Croatia, Finland, France, Georgia, Germany, Ireland, Italy, Malta, Poland, Portugal, Spain, United Kingdom
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseFrance, Poland, United States, Russian Federation, United Kingdom
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Lysosomal and Rare Disorders Research and Treatment...SanofiUnknown
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Amicus TherapeuticsCompletedOpen-Label Extension Study of the Long-Term Effects of Migalastat HCL in Patients With Fabry DiseaseFabry DiseaseUnited States, Austria, United Kingdom, Argentina, Australia, Belgium, Brazil, Canada, Denmark, Egypt, France, Italy, Japan, Spain, Turkey
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Genzyme, a Sanofi CompanyTerminatedFabry DiseaseAustria, Brazil, France, United States, Argentina, Belgium, Canada, Finland, Hungary, Norway, Poland, Spain, Taiwan, United Kingdom
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Boston Children's HospitalWithdrawn
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Hospices Civils de LyonCompleted
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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University Hospital, BordeauxCompleted
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Groupe Hospitalier Diaconesses Croix Saint-SimonTerminated
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Peking Union Medical College HospitalUnknownX-linked HypophosphatemiaChina
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Amicus TherapeuticsCompletedFabry DiseaseFrance, Austria, United States, Belgium, Japan, United Kingdom, Denmark, Brazil, Australia, Italy
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Italy, Spain, Turkey, Brazil, Canada, United Kingdom, France, Poland, Australia, Egypt, Argentina, Denmark
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Amicus TherapeuticsTerminatedFabry DiseaseAustralia, United States, Italy, Spain, Belgium, Turkey, Brazil, Argentina, United Kingdom, Denmark, France, Canada, Egypt
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University Hospital, CaenUnknown
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National Institute of Neurological Disorders and...National Institute of Neurological Disorders and Stroke@@@Shire Human Genetic...Completed
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Genzyme, a Sanofi CompanyCompleted
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Rigshospitalet, DenmarkCompletedFabry DiseaseDenmark
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National Institute of Neurological Disorders and...Completed
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Assistance Publique - Hôpitaux de ParisUnknown
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Children's Hospital of Fudan UniversityNot yet recruiting
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Westfälische Wilhelms-Universität MünsterChiesi GmbHRecruiting
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ISU Abxis Co., Ltd.RecruitingFabry DiseaseKorea, Republic of
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SanofiRecruiting
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SanofiRecruitingFabry's DiseaseUnited States
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Bio Sidus SARecruiting
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Bahçeşehir UniversityNot yet recruitingDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Healthy Individuals
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Hospital Clinico Universitario de SantiagoAlvaro Hermida (Co-IP); Susana Belen Bravo; Maria Teresa Cardoso; Cristobal Colon... and other collaboratorsRecruiting
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Amicus TherapeuticsRecruiting
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Amicus Therapeutics France SASCompletedFabry Disease | Anderson Fabry DiseaseFrance
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University Health Network, TorontoOzmosis Research Inc.Completed
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4D Molecular TherapeuticsActive, not recruiting
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Bio Sidus SACompleted
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TakedaCompleted
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AVROBIOTerminatedFabry DiseaseUnited States, Australia, Brazil
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National and Kapodistrian University of AthensCompletedFabry DiseaseGreece
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Genzyme, a Sanofi CompanyCompleted
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ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseUnited States, Denmark, Belgium, United Kingdom, Norway, Italy, Czechia
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ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseUnited States, Spain, United Kingdom, Paraguay
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Canada, Japan, France, Denmark
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Chiesi Farmaceutici S.p.A.Iqvia Pty Ltd; ProtalixCompletedFabry DiseaseUnited States, Belgium, Denmark, Italy, United Kingdom
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University of UtahGenzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States