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Clinical Trials on Alpha-Mannosidosis
Total 218 results
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Krystal Biotech, Inc.RecruitingAlpha 1-Antitrypsin DeficiencyUnited States
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Hospital Universitari Vall d'Hebron Research InstituteEuropean Respiratory SocietyRecruitingAlpha 1-Antitrypsin DeficiencySpain
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University of FloridaRecruitingAlpha-1 Antitrypsin DeficiencyUnited States
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyActive, not recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, United States, Ireland, Belgium, New Zealand, Spain, Netherlands, Portugal, Canada, Australia, France, Austria, Germany, Sweden
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St. Louis UniversityBoston University; University College, London; University of Massachusetts, Worcester and other collaboratorsActive, not recruiting
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Arrowhead PharmaceuticalsCompleted
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Arrowhead PharmaceuticalsTerminatedAlpha-1 Antitrypsin DeficiencyAustralia, Netherlands, Germany, United Kingdom
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Kamada, Ltd.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Beam Therapeutics Inc.Not yet recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom
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Cyprus Institute of Neurology and GeneticsRecruitingSickle Cell Disease | Hemoglobinopathies | Thalassemia Alpha | Thalassemia, BetaUnited States, Denmark, Spain, Belgium, Portugal, Congo, The Democratic Republic of the, Greece, Argentina, Brunei Darussalam, Cyprus, Israel, Italy, Nigeria, Malaysia, Angola, Pakistan
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Vertex Pharmaceuticals IncorporatedActive, not recruitingAlpha-1 Antitrypsin DeficiencyUnited States, United Kingdom, Germany, Ireland
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Vertex Pharmaceuticals IncorporatedCompleted
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Vertex Pharmaceuticals IncorporatedCompleted
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Arrowhead PharmaceuticalsCompletedAlpha 1-Antitrypsin DeficiencyUnited States, Spain, Netherlands, Germany, Italy, Portugal
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Adverum Biotechnologies, Inc.Completed
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Vertex Pharmaceuticals IncorporatedTerminatedAlpha 1-Antitrypsin DeficiencyUnited States, Germany, Canada, Ireland
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Kamada, Ltd.CompletedAlpha-1 Antitrypsin DeficiencyUnited States
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Fondazione Salvatore MaugeriAzienda Socio Sanitaria Territoriale degli Spedali Civili di Brescia; Grifols... and other collaboratorsCompletedAlpha-1 Antitrypsin Deficiency
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OctapharmaWithdrawn
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Arrowhead PharmaceuticalsWithdrawnAlpha-1 Antitrypsin DeficiencyIreland, Canada, Italy, Sweden
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Wroclaw Medical UniversityUnknownCardiovascular Diseases | Preventive Medicine | Fatty Acids | Anti-Inflammatory Agents | Eicosapentaenoic Acid | Preventive Health Services | Alpha-Linolenic Acid | Docosahexaenoic AcidsPoland
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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Adverum Biotechnologies, Inc.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Inhibrx, Inc.CompletedAlpha-1 Antitrypsin Deficiency | AATDUnited States, New Zealand, United Kingdom
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Coram Clinical TrialsCompletedAlpha-1 Anti-trypsin DeficiencyUnited States
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Arrowhead PharmaceuticalsActive, not recruitingAlpha 1-Antitrypsin DeficiencyAustria, Germany, United Kingdom
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Dicerna Pharmaceuticals, Inc.WithdrawnAlpha 1-Antitrypsin DeficiencyNew Zealand
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Mereo BioPharmaSyneos HealthCompletedEmphysema | Alpha 1-Antitrypsin Deficiency | COPDUnited Kingdom, Belgium, United States, Denmark, Canada, Sweden, Poland, Spain
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Columbia UniversityNational Heart, Lung, and Blood Institute (NHLBI); Alpha-1 FoundationActive, not recruitingAlpha 1-Antitrypsin Deficiency | Genetic DiseaseUnited States
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University of Alabama at BirminghamNational Institutes of Health (NIH); Mereo BioPharmaCompletedEmphysema or COPD | Alpha-1 Antitrypsin Deficiency (AATD) | Pi*ZZ, Pi*SZ, Pi*Null, Another Rare Phenotype/Genotype Known to be Associated With Either Low or Functionally Impaired AAT Including F or I MutationsUnited States
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Alnylam PharmaceuticalsTerminatedAntitrypsin Deficiency Liver DiseaseUnited Kingdom
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Soroka University Medical CenterUnknownPost Cardiac Surgery Systemic Inflammatory Response
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University of Michigan Rogel Cancer CenterCSL Behring; The Leukemia and Lymphoma SocietyCompletedGraft vs Host DiseaseUnited States
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University of FloridaCompletedAlpha-1 Antitrypsin Deficiency | Liver Fibrosis | AATD | AAT DeficiencyUnited States
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Kamada, Ltd.Completed
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Huashan HospitalRecruitingPositron-Emission Tomography | Alpha Synuclein PathologyChina
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Talaris Therapeutics Inc.Duke UniversityWithdrawnAnemia, Sickle Cell | Thalassemia | Beta-Thalassemia | Bone Marrow Failure Syndromes | Diamond-Blackfan Anemia | Alpha-Thalassemia | Complex and Transfusion-dependent HemoglobinopathiesUnited States
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Indonesia UniversityDanone Institute InternationalCompletedOverweight | Nutritional Status | Complementary Feeding Recommendation | Linear Programming, | Omega-3 Fatty Acids | Malondialdehyde | Alpha-TocopherolIndonesia
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Kamada, Ltd.CompletedEmphysemaUnited Kingdom, Canada, Denmark, Germany, Ireland, Netherlands, Sweden
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Medical University of South CarolinaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedChronic PancreatitisUnited States
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Gerard TurinoCompletedEmphysema | Alpha 1-Antitrypsin DeficiencyUnited States, Canada
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Sun Yat-sen UniversityNot yet recruitingLong-term Effects of Thymosin Alpha 1 Treatment
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Grifols Therapeutics LLCCompletedAlpha 1-Antitrypsin DeficiencyDenmark, Sweden, United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)CompletedLung Diseases, Obstructive | Emphysema | Alpha 1-Antitrypsin DeficiencyUnited States
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Hospital Authority, Hong KongUnknownProstatic Hyperplasia | Adrenergic Alpha-AntagonistsChina
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Medical University of South CarolinaCSL BehringCompletedSmoking | Emphysema | Alpha-1 Antitrypsin Deficiency | COPDUnited States
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Grifols Therapeutics LLCTerminatedType 1 Diabetes MellitusUnited States
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University of NottinghamNottingham University Hospitals NHS TrustRecruitingChronic Obstructive Pulmonary Disease | Alpha 1-Antitrypsin DeficiencyUnited Kingdom