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Clinical Trials on beta-Mannosidosis
Total 448 results
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HaEmek Medical Center, IsraelUnknownThalassemia | Brain Function (Measured by ERP Level)Israel
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University of Campinas, BrazilFundação de Amparo à Pesquisa do Estado de São PauloCompletedIron Overload | ThalassemiaBrazil
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Imperial College LondonCompletedAtrial Fibrillation | Cardiac Arrest | Brugada Syndrome | Athletes Heart | Ventricular Ectopic BeatUnited Kingdom
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Beni-Suef UniversityUniversity of Arizona; Maternity and Children Hospital, Makkah; Beni-Suef Health...CompletedIron Overload | Oxidative Stress | Thalassemia MajorEgypt, Saudi Arabia
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University of California, San FranciscoRecruitingAlpha-Thalassemia | Alpha Thalassemia Major | Alpha Thalassemia MinorUnited States
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Brigham and Women's HospitalBoston University; University of Pennsylvania; University of Michigan; Duke University and other collaboratorsCompletedAlzheimer Disease | Education | Neuroimaging | Risk Assessment | Neuropsychological Tests | Amyloid Beta-PeptidesUnited States
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The Hospital for Sick ChildrenSunnybrook Health Sciences Centre; University of Toronto; University of GuelphCompletedInflammation | Obesity | Insulin Resistance | PreDiabetes | Adolescent Obesity | Immunity | Gut Microbiome | Gut Hormones | Beta Cell Dysfunction | Metabolic ProblemsCanada
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King Saud UniversityCompletedChronic Periodontitis | Thalassemia Major
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Amsterdam UMC, location VUmcCompletedDiabetes Mellitus | Steroid Diabetes | Glucocorticoid-induced Diabetes | Beta-cell FunctionNetherlands
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Imara, Inc.Quintiles, Inc.CompletedSickle Cell Disease | Sickle Beta 0 Thalassemia | Sickle-Cell; Hb-SCUnited States
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Life Molecular Imaging SACompletedAlzheimer Disease | Amyloid Beta-ProteinAustralia
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Masonic Cancer Center, University of MinnesotaRecruitingSickle Cell Disease | Severe Congenital Neutropenia | Paroxysmal Nocturnal Hemoglobinuria | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Diamond Blackfan Anemia | Transfusion Dependent Alpha- or Beta- Thalassemia | Non-Malignant Hematologic DisordersUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Chelsea TherapeuticsCompletedNeurogenic Orthostatic Hypotension | Primary Autonomic Failure | Dopamine Beta Hydroxylase Deficiency | Non-Diabetic Neuropathy
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National Center for Research Resources (NCRR)Children's Hospital of PhiladelphiaCompletedOsteoporosis | Osteopenia | Thalassemia Major
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Center for Vascular Pathology, MoscowEnrolling by invitationSpinal Tumor | Spinal Hemangioma | Beta Blocker ToxicityRussian Federation
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Ersi VoskaridouCompletedOsteoporosis | Thalassemia MajorGreece
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Ain Shams UniversityUnknownDNA Damage | Endocrine Disease | Fertility Decreased MaleEgypt
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Ente Ospedaliero Ospedali GallieraUniversity of Campania "Luigi Vanvitelli"; Reggio Calabria; Ospedale Maggiore... and other collaboratorsCompletedOsteoporosis | Thalassemia Major | Thalassemia IntermediaItaly
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HaEmek Medical Center, IsraelUnknownIron Deficiency | ThalassemiaIsrael
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Fakultas Kedokteran Universitas IndonesiaCompletedThalassemia | Pneumococcal InfectionIndonesia
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload | β-thalassemiaItaly
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload in β-thalassemiaUnited States, Greece, Argentina, Germany, Belgium, Italy, United Kingdom, France, Tunisia, Canada, Turkey, Brazil
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Children's Hospital of PhiladelphiaAnn & Robert H Lurie Children's Hospital of Chicago; The Cooley's Anemia Foundation...CompletedThalassemia Major With Severe Transfusional Iron OverloadUnited States
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Chelsea TherapeuticsChiltern International Inc.CompletedPrimary Autonomic Failure | Dopamine Beta Hydroxylase Deficiency | Symptomatic Neurogenic Orthostatic Hypotension (NOH) | Non-diabetic NeuropathyUnited States, Australia, Canada, New Zealand
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Karolinska InstitutetDanderyd HospitalRecruitingAtrial Fibrillation | Atrial Flutter | Supraventricular Beat, Premature | Premature Supraventricular Beats | Premature Atrial Complex | Extrasystole, AtrialSweden
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RESnTEC, Institute of ResearchCompletedPateints of β-thalassemia Major With Iron OverloadPakistan
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National Institute of Allergy and Infectious Diseases...CompletedGroup A Beta Hemolytic Streptococcal (GAS) InfectionIndia
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Novartis PharmaceuticalsTerminatedCardiac Iron Overload | Transfusion-dependent β-thalassemia PatientsGreece
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Chelsea TherapeuticsChiltern International Inc.CompletedA Clinical Study for Patients With Neurogenic Orthostatic Hypotension (NOH) Using Droxidopa (NOH301)Primary Autonomic Failure | Dopamine Beta Hydroxylase Deficiency | Symptomatic Neurogenic Orthostatic Hypotension (NOH) | Non-diabetic NeuropathyUnited States, Canada
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Life Molecular Imaging SACompletedDown Syndrome | Amyloid Beta-proteinUnited States
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Fairview University Medical CenterCompletedNeutropenia | Sickle Cell Anemia | Red-Cell Aplasia, Pure | Thalassemia MajorUnited States
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Travere Therapeutics, Inc.Recruiting
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University Health Network, TorontoRecruitingThalassemia MajorCanada
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ApoPharmaCompletedHemosiderosis | Thalassemia MajorGreece, Italy
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University Health Network, TorontoCompletedThalassemia Major | Chronic Blood Transfusion Related Iron OverloadCanada
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Ospedale MicrocitemicoAzienda Sanitaria Locale di CagliariCompletedIron Overload | CardiomyopathyItaly
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TriVirum, Inc.CompletedAtrial Fibrillation | Arrhythmias, Cardiac | Paroxysmal Atrial Fibrillation | Afib | Irregular Heart Beat | Arrhythmia Atrial | Arrhythmias ParoxysmalUnited States
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The Methodist Hospital Research InstituteM.D. Anderson Cancer Center; National Institute of Allergy and Infectious Diseases... and other collaboratorsRecruitingAntibiotic Resistant Infection | Clostridium Difficile | Antimicrobial Drug Resistance | Carbapenem-Resistant Enterobacteriaceae Infection | Vancomycin Resistant Enterococci Infection | Vancomycin-Resistant Enterococcal Infection | Carbapenem Resistant Bacterial Infection | Extended Spectrum Beta-Lactamase...United States
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Tianjin Medical University General HospitalNot yet recruitingCardiovascular Diseases | Stroke | Cerebrovascular Disorders | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Ischemic Stroke | Molecular Mechanisms of Pharmacological Action | Physiological Effects of Drugs | Propranolol | Immunologic Factors | Beta BlockerChina
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Novartis PharmaceuticalsCompletedAnemia | HemosiderosisUnited States, Germany, Belgium, United Kingdom, Italy, Canada, France
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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UCSF Benioff Children's Hospital OaklandNovartis PharmaceuticalsCompletedTHALASSEMIA MAJORUnited States
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload | β-thalassemia Major | Pediatric Rare AnemiaItaly, France
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LMU KlinikumSeventh Framework Programme; NBIA AllianceRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA) | Pantothenate Kinase-associated Neurodegeneration (PKAN) | Aceruloplasminemia | Beta-Propeller Protein-Associated Neurodegeneration (BPAN) | Mitochondrial Membrane Protein Associated Neurodegeneration (MPAN) | Fatty Acid Hydroxylase-associated... and other conditionsCanada, Czechia, Germany, Italy, Netherlands, Poland, Serbia, Spain
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Thomas Jefferson UniversityGlaxoSmithKline; Drexel UniversityUnknownQuality of Life | Inflammation | Sickle Cell Disease | HEMOGLOBIN SS | Hemoglobin S Beta-0 ThalassemiaUnited States
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Wolfson Medical CenterUnknownPatients With Thalassemia Intermedia, | Congenital Dyserythropoietic Anemia Type I