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Clinical Trials on mTOR Pathway Abberation
Total 2054 results
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Novartis PharmaceuticalsCompletedSpinal and Bulbar Muscular AtrophyUnited States, Germany, Italy, Denmark
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Sultan Abdulhamid Han Training and Research Hospital...UnknownQuality of Life | Fatigue | Chronic Obstructive Pulmonary Disease | Foot Deformities | Activity, MotorTurkey
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Stanford UniversityCompletedA Pilot Therapeutic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy PatientsMuscular Atrophy, SpinalUnited States
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Stem Cells ArabiaUnknownMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Progressive Bulbar Palsies
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University of South FloridaNational Institute of Neurological Disorders and Stroke (NINDS); University...CompletedCongenital Abnormalities | Genetic Diseases, Inborn | Nerve Compression Syndromes | Hereditary Sensory and Motor Neuropathy | Heredodegenerative Disorders, Nervous System | Tooth Diseases | Charcot Marie Tooth Disease (CMT)United States
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Ospedale San RaffaeleUniversity of Padova; Niguarda Hospital; Fondazione Salvatore MaugeriCompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis (ALS)Italy
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Temple UniversityWithdrawnAbdominal Cutaneous Nerve Entrapment Syndrome | Chronic Abdominal Wall Pain
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University of UtahLeadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular Atrophy Type IUnited States, Canada, Germany
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Centre Hospitalier Universitaire de NiceUnknown
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Parkinson's Disease and Movement Disorders CenterOrtho-McNeil Neurologics, Inc.TerminatedTourette's Syndrome | Motor Tic Disorder | Vocal Tic DisorderUnited States
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Sunnybrook Health Sciences CentreOrtho Biotech, Inc.Terminated
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National Institute of Neurological Disorders and...CompletedHealthy | Motor Neuron Disease | Lysosomal Storage Disease | Movement Disorder | Demyelinating DiseaseUnited States
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Elpida Therapeutics SPCNot yet recruitingNeuromuscular Diseases | Peripheral Neuropathy | Neuro-Degenerative Disease
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Istanbul Medipol University HospitalIstanbul UniversityRecruitingNeuromuscular Diseases | Spinal Muscular Atrophy Type 3Turkey
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University Hospital, AngersRecruitingCharcot-Marie-Tooth Disease Type 2AFrance
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Massachusetts General HospitalRecruitingSleep Disorder | Restless Legs Syndrome | Opioid-use Disorder | Opioid WithdrawalUnited States
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University Medical Centre LjubljanaRecruitingPeripheral Nervous System Diseases | Carpal Tunnel Syndrome | Nerve Compression SyndromesSlovenia
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Oregon Health and Science UniversityActive, not recruitingAnterior Cutaneous Nerve Entrapment SyndromeUnited States
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Washington University School of MedicineActive, not recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | Spinal Muscular Atrophy Type IIUnited States, Canada
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Peking University Third HospitalEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Frontotemporal DementiaChina
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Johns Hopkins UniversityTerminatedHIV Dementia | HIV-Associated Cognitive Motor ComplexUnited States
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University of MinnesotaCompletedTourette's Syndrome | Chronic Motor Tic Disorder | Chronic Vocal Tic DisorderUnited States
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St George's, University of LondonUniversity College London HospitalsUnknownPeripheral Neuropathy | CMT - Charcot-Marie-Tooth Disease | Hereditary Peripheral Neuropathy | CMT1AUnited Kingdom
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Karolinska InstitutetCompletedTourette's Disorder | Persistent (Chronic) Motor or Vocal Tic DisorderSweden
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Korea Otsuka Pharmaceutical Co., Ltd.Otsuka Pharmaceutical Co., Ltd.CompletedTourette's Disorder | Chronic Motor or Vocal Tic DisorderKorea, Republic of
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Duke UniversityUCB PharmaCompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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Nido Biosciences, Inc.RecruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseKorea, Republic of, Denmark, Italy, United Kingdom
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Aristotle University Of ThessalonikiNot yet recruitingMedullary Thyroid CancerChina, Switzerland, Spain, Greece, United States, Austria, Belgium, Brazil, Bulgaria, Colombia, Croatia, France, India, Iraq, Italy, Jordan, Morocco, Poland, Serbia, Slovakia, Thailand, Turkey, Ukraine, Vietnam
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Holland Bloorview Kids Rehabilitation HospitalCanadian Institutes of Health Research (CIHR)RecruitingStroke | Cerebral Palsy | Autism Spectrum Disorder | Spinal Cord Injuries | Acquired Brain Injury | Developmental Disability | Developmental Coordination Disorder | Motor Skills DisordersCanada
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Istituto Ortopedico RizzoliRecruitingSuperior Cluneal Nerve EntrapmentItaly
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1ST Biotherapeutics, Inc.Not yet recruitingAmyotrophic Lateral Sclerosis (ALS) | Parkinson Disease Psychosis
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...RecruitingAmyotrophic Lateral Sclerosis | Kennedy DiseaseFrance
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University Hospital TuebingenRecruitingHereditary Spastic Paraplegia | Hereditary, Spastic Paraplegia, Autosomal DominantGermany
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Scholar Rock, Inc.CompletedNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2United States, Spain, Italy, Netherlands
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University Hospital, Basel, SwitzerlandEnrolling by invitationSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IIISwitzerland
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National Institutes of Health Clinical Center (CC)CompletedDepression | HIV Infections | HIV-Associated Cognitive Motor ComplexUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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Association pour le Développement et l'Organisation...Association Française du Syndrome d'Ondine; Fonds de Recherche en Santé RespiratoireCompletedHealthy | Amyotrophic Lateral Sclerosis | Ondine SyndromeFrance
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Flex Pharma, Inc.TerminatedCharcot-Marie-Tooth DiseaseUnited States
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Ramathibodi HospitalAstraZenecaCompletedSpinobulbar Muscular Atrophy | Kennedy's DiseaseThailand
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Radboud University Medical CenterCompletedAnterior Cutaneous Nerve Entrapment Syndrome (ACNES)Netherlands
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Wayne State UniversityMuscular Dystrophy Association; Charcot-Marie-Tooth AssociationCompleted
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Holdsworth House Medical PracticeCompletedHIV-1-Associated Cognitive Motor Complex
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University of GenovaUnknownCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease Type 1AItaly
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National Institute of Neurological Disorders and...CompletedSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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WestatNational Institute of Neurological Disorders and Stroke (NINDS)TerminatedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IIIUnited States
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John ElfarNot yet recruitingCarpal Tunnel Syndrome | Compression Neuropathy
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University of ValenciaRecruitingCerebrospinal Fluid Levels of Amyloid Beta 1-42, H-tau and Phospho-tau Proteins | Cognitive Impairment and Its Evolution After Hydrocephalus Treatment | Motor Impairment and Its Evolution After Hydrocephalus Treatment | Ventricular Size and Its Evolution After Implantation of a Ventriculoperitoneal...Spain
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Centre Hospitalier Universitaire, AmiensRecruitingSpinal Muscular Atrophy | Non Invasive Ventilation | Respiratory Bacterial InfectionFrance
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Nemours Children's ClinicCompletedMuscular Dystrophy | Spinal Muscular Atrophy | Arthrogryposis