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Clinical Trials on mTOR Pathway Abberation
Total 2074 results
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Wave Life Sciences Ltd.TerminatedALS | FTDNetherlands, United Kingdom
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Transposon Therapeutics, Inc.Active, not recruitingAmyotrophic Lateral Sclerosis | Frontotemporal DementiaSpain, United States, Belgium, France, Germany
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University of Missouri-ColumbiaNational Institute on Deafness and Other Communication Disorders (NIDCD)CompletedParkinson Disease | Amyotrophic Lateral SclerosisUnited States
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Yuzuncu Yıl UniversityCompleted
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Pharnext SACompletedPhase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) (PLEO-CMT)Charcot-Marie-Tooth Disease Type 1AUnited States, United Kingdom, Belgium, Canada, France, Netherlands, Spain, Germany
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Hill-RomCompletedMotor Neuron Disease | Cystic Fibrosis | Airway Clearance ImpairmentUnited States
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Tehran University of Medical SciencesUnknownInfantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]Iran, Islamic Republic of
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Guy Hains ChiropractorCompletedCompression Neuropathy, Carpal TunnelCanada
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Assistance Publique - Hôpitaux de ParisTerminatedAmyotrophic Lateral Sclerosis | Frontotemporal DementiaFrance
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Istanbul University - Cerrahpasa (IUC)Not yet recruitingCarpal Tunnel Syndrome | Entrapment Neuropathy | Median Nerve EntrapmentTurkey
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Johns Hopkins UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingAmyotrophic Lateral Sclerosis | Tetraplegia | Locked-in Syndrome | Brainstem StrokeUnited States
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Assistance Publique Hopitaux De MarseilleRecruitingCharcot-Marie-Tooth Disease Type 1AFrance
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Anti-myostatin | Spinal Muscular Atrophy Type IIUnited States, Spain, Belgium, Germany, Netherlands, Poland, Italy, France, United Kingdom
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Alexandria UniversityCompletedHemiplegia | Spasticity, Muscle | Stroke, Ischemic | Stroke, Acute | Motor Activity | Hemiparesis | Stroke, Lacunar | Spastic | Hemiplegic GaitEgypt
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University of AberdeenNHS GrampianCompletedAbdominal Pain | Abdominal Cutaneous Nerve Entrapment SyndromeUnited Kingdom
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Afyonkarahisar Health Sciences UniversityCompletedMusculoskeletal Diseases | Carpal Tunnel Syndrome | Median Neuropathy | Entrapment NeuropathyTurkey
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Centre de Recherche de l'Institut Universitaire...Canadian Institutes of Health Research (CIHR)CompletedTourette Syndrome | Tourette Syndrome in Children | Tic Disorder, Chronic Motor or VocalCanada
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MarsiBionicsFundacion para la Investigacion Biomedica del Hospital Universitario Ramon...CompletedSpinal Muscular Atrophy Type IISpain
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Istituto Clinico HumanitasFondazione I.R.C.C.S. Istituto Neurologico Carlo Besta; Fondazione Salvatore...CompletedAmyotrophic Lateral Sclerosis | Postural Orthostatic Tachycardia Syndrome | Pure Autonomic Failure | Anti-Cholinergic Receptors AntibodiesItaly
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University of UtahMarquette UniversityCompletedTourette's Disorder | Persistent (Chronic) Motor or Vocal Tic DisorderUnited States
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Beth Israel Deaconess Medical CenterMerz PharmaceuticalsWithdrawnParkinson Disease | Amyotrophic Lateral SclerosisUnited States
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Maxima Medical CenterRecruitingChronic Pain Syndrome | Diagnosis | Nerve Entrapment Syndrome | Anterior Cutaneous Nerve Entrapment SyndromeNetherlands
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Merve KurtRecruitingDuchenne Muscular Dystrophy | Virtual Reality | Spinal Muscular Atrophy | Neuromuscular Disease | BiofeedbackTurkey
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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Beth Israel Deaconess Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)CompletedAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Radiculopathy | Trauma Injury | Orthopedic Disorder | Myopathy | Polyneuropathy and MononeuropathiesUnited States
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University of HawaiiTobira Therapeutics, Inc.CompletedAIDS Dementia Complex | Human Immunodeficiency Virus | HIV-1-Associated Cognitive Motor ComplexUnited States
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Cambridge Respiratory Innovations LimitedInnovate UKCompletedHeart Failure | Pneumonia | Motor Neuron Disease | Asthma | Vocal Cord Dysfunction | BreathlessnessUnited Kingdom
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University of South FloridaNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedCarpal Tunnel Syndrome | Charcot-Marie-Tooth Disease | Inherited Peripheral NeuropathyUnited States
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Duke UniversityCompletedProstate Cancer | Brain Cancer | ALS | Renal CancerUnited States
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Boston Children's HospitalCureAP4 FoundationRecruitingHereditary Spastic Paraplegia | SPG50 | SPG47 | SPG51 | SPG52 | AP4-related Hereditary Spastic Paraplegia | Early Onset Hereditary Spastic Paraplegia | SPG4 | SPG3A | SPG15 | SPG11United States
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University Medical Centre LjubljanaSlovenian Research AgencyRecruitingPeripheral Nervous System Diseases | Nerve Compression Syndromes | Cubital Tunnel SyndromeSlovenia
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IRCCS Eugenio MedeaCompletedCerebral Palsy | Acquired Brain Injury | Hereditary Spastic ParaplegiaItaly
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Wake Forest University Health SciencesWithdrawnMultiple Sclerosis | Parkinson Disease | Neurodegenerative Diseases | Amyotrophic Lateral SclerosisUnited States
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National Institute of Neurological Disorders and...CompletedMotor Neuron DiseaseUnited States
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University of South CarolinaCompletedMultiple Sclerosis | Amyotrophic Lateral Sclerosis | Major DepressionUnited States
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Jose Luis Urcelay SeguraUnknownAmyotrophic Lateral SclerosisSpain
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Vanderbilt University Medical CenterCompletedCognitive Impairment | Memory Impairment | HIV-1-infection | Aging, Premature | HIV-Associated Cognitive Motor ComplexUnited States
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MinYoung Kim, M.D.CompletedCerebral Palsy | Parkinson's Disease | Brain Injury | Amyotrophic Lateral SclerosisKorea, Republic of
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Hoffmann-La RocheAssociation Française contre les Myopathies (AFM), ParisCompletedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type III Non AmbulantGermany, Italy, France, Belgium, Poland, Netherlands, United Kingdom
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National Taiwan University HospitalNational Science Council, TaiwanUnknownSpinal Muscular Atrophy | Spinal Cord Injury | MyelomeningoceleTaiwan
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Maxima Medical CenterRecruitingChronic Pain Syndrome | Nerve Entrapment Syndrome | Anterior Cutaneous Nerve Entrapment SyndromeNetherlands
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Washington University School of MedicineGenentech, Inc.RecruitingB Cell Lymphoma | Diffuse Large B Cell Lymphoma | High-grade B-cell Lymphoma | Transformed Lymphoma | Aggressive Lymphoma | Follicular Lymphoma Grade 3United States
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy | Kennedys DiseaseUnited States
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Washington University School of MedicineNational Institute of Mental Health (NIMH)CompletedTourette Syndrome | Tic Disorders | Tourette's Disorder | Chronic Motor or Vocal Tic Disorder | Transient Tic Disorder | Provisional Tic DisorderUnited States
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Saglik Bilimleri UniversitesiCompletedQuality of Life | Fatigue | Muscle Weakness | Pulmonary Disease | COPD | Respiratory Disease | Dyspnea | Muscle Strength | Functional Capacity | Severe Chronic Obstructive Pulmonary Disease | Motor Imagery | Muscle; AccessoryTurkey
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth Disease | Facioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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Pharnext SACompletedCharcot-Marie-Tooth Disease | Hereditary Neuropathy With Liability to Pressure Palsies | Genetic DisordersFrance
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University of OklahomaCompletedCerebral Palsy | Spinal Muscular Atrophy | Arthrogryposis | Other Central Nervous System or Musculoskeletal DisordersUnited States
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Central Hospital, Nancy, FranceRecruiting