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Search clinical trials for: βAS3-FB vector transduced peripheral blood CD34 cells
Total 122 results
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Donald B. Kohn, M.D.California Institute for Regenerative Medicine (CIRM)Active, not recruiting
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Great Ormond Street Hospital for Children NHS Foundation...Recruiting
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSevere Combined Immunodeficiency, X-LinkedUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...WithdrawnGranulomatous Disease, Chronic, X-linked, VariantUnited Kingdom
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GenethonActive, not recruitingWiskott-Aldrich SyndromeUnited Kingdom, France
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University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... and other collaboratorsActive, not recruitingMucopolysaccharidosis Type IIIAUnited Kingdom
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GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
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GenethonHôpital Necker-Enfants MaladesCompleted
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David WilliamsActive, not recruitingGene Therapy | Severe Combined Immunodeficiency, X LinkedUnited States, United Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...UnknownX-linked Severe Combined ImmunodeficiencyUnited Kingdom
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CSL BehringTerminated
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Shanghai Zhongshan HospitalUnknownPeripheral Arterial Disease | Arteritis | Thromboangiitis ObliteransChina
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Dr. Melody Smith, MD, MSOrca Biosystems, Inc.Recruiting
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Foundation for Biomedical Research and InnovationInstitute of Biomedical Research and Innovation, Kobe, Hyogo, Japan; Kobe City... and other collaboratorsTerminatedMyocardial Infarction | Coronary Artery Disease | Chest Pain | Angina | Chronic Myocardial IschemiaJapan
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Translational Research Center for Medical Innovation...Institute of Biomedical Research and Innovation, Kobe, Hyogo, Japan; Kobe City...CompletedIschemia | Ulcer | Peripheral Vascular Diseases | Gangrene | Leg PainJapan
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David WilliamsNational Heart, Lung, and Blood Institute (NHLBI); bluebird bio; California Institute... and other collaboratorsRecruitingA Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease (GRASP, BMT CTN 2001) (GRASP)Sickle Cell DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedLymphoma | Myelodysplastic Syndromes | Leukemia | Multiple Myeloma and Plasma Cell Neoplasm | Graft Versus Host DiseaseUnited States
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David WilliamsActive, not recruiting
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Universitätsklinikum Hamburg-EppendorfTerminatedHIV Infections | AIDS-related LymphomaGermany
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OHSU Knight Cancer InstituteOregon Health and Science UniversityAvailableMalignant Neoplasm | Hematopoietic Cell Transplantation Recipient | Benign Neoplasm | Bone Marrow Transplantation RecipientUnited States
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University of California, Los AngelesRecruitingAdenosine Deaminase Severe Combined Immune DeficiencyUnited States
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Nantes University HospitalCompletedAllergic Rhinitis | Atopic Dermatitis | Allergic AsthmaFrance
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M.D. Anderson Cancer CenterRecruitingFollicular Lymphoma | Acute Myeloid Leukemia | Hodgkin Lymphoma | Acute Lymphoblastic Leukemia | Mantle Cell Lymphoma | Chronic Lymphocytic Leukemia | Non-Hodgkin Lymphoma | Myelodysplastic Syndrome | Plasma Cell Myeloma | Aplastic Anemia | Myeloproliferative Neoplasm | Bone Marrow Failure | Chronic Myelogenous...United States
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Abramson Cancer Center of the University of PennsylvaniaWithdrawnOvarian, Fallopian Tube and Peritoneal CancerUnited States
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Fundacion Clinic per a la Recerca BiomédicaNot yet recruitingRefractory Non-Hodgkin Lymphoma | Relapsed Non-Hodgkin LymphomaSpain
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bluebird bioCompletedSickle Cell DiseaseUnited States
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Barbara Ann Karmanos Cancer InstituteNational Cancer Institute (NCI)CompletedMultiple Myeloma and Plasma Cell NeoplasmUnited States
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University of NebraskaTerminatedPlasma Cell MyelomaUnited States
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Guenther KoehneSuspendedMyelodysplastic Syndromes | Graft Vs Host Disease | Graft-versus-host-diseaseUnited States
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Grupo Cooperativo de Estudio y Tratamiento de las...Completed
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)RecruitingAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Acute Leukemia | Myelodysplastic SyndromeUnited States
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Catherine BollardChildren's National Research InstituteActive, not recruitingThalassemia | Sickle Cell-thalassemia DiseaseUnited States
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AIDS Malignancy ConsortiumNational Cancer Institute (NCI); California Institute for Regenerative Medicine...Active, not recruitingHIV Infection | Plasmablastic Lymphoma | Recurrent Adult Hodgkin Lymphoma | Recurrent Adult Non-Hodgkin Lymphoma | Stage III Mantle Cell Lymphoma | Stage IV Mantle Cell Lymphoma | Recurrent Burkitt Lymphoma | Mature T-Cell and NK-Cell Non-Hodgkin Lymphoma | Recurrent Follicular Lymphoma | Stage III Follicular... and other conditionsUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Congenital Hemolytic AnemiaUnited States
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Masonic Cancer Center, University of MinnesotaNational Cancer Institute (NCI)Terminated
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Northwestern Memorial HospitalUnknownSystemic Lupus ErythematosusUnited States
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Dana-Farber Cancer InstituteRecruitingMyelodysplastic Syndromes | Graft Vs Host Disease | Stem Cell Transplant Complications | Myeloid Leukemia, Acute | Myeloid Leukemia in Relapse (Disorder)United States
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Massachusetts Eye and Ear InfirmaryBausch & Lomb IncorporatedCompletedEfficacy of Zylet vs. Lotemax for the Treatment of Ocular Surface Inflammation/MGD/Blepharitis (ZvL)Meibomian Gland Dysfunction | Posterior BlepharitisUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Institutes of Health (NIH)WithdrawnPlasma Cell MyelomaUnited States
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University Hospital Inselspital, BerneCompleted
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King's College Hospital NHS TrustUnknownMyelodysplastic Syndromes | Leukemia, Myeloid, AcuteUnited Kingdom
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Stanton Gerson MDNational Cancer Institute (NCI)Completed
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National Institutes of Health Clinical Center (CC)National Cancer Institute (NCI)TerminatedKidney Cancer | Unspecified Adult Solid Tumor, Protocol Specific | Melanoma (Skin)United States
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National Cancer Institute (NCI)TerminatedCervical Cancer | Pancreatic Cancer | Ovarian Cancer | Lung Cancer | MesotheliomaUnited States
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Paul SzabolcsRecruiting
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City of Hope Medical CenterCompletedStage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Smoldering Multiple Myeloma | Refractory Multiple MyelomaUnited States
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Masonic Cancer Center, University of MinnesotaNational Cancer Institute (NCI)Withdrawn
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedAcute Myeloid Leukemia | Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome | Chronic Myelomonocytic Leukemia | Acute Erythroid Leukemia | Acute Megakaryoblastic Leukemia | Myelodysplastic Syndrome | High Risk Myelodysplastic Syndrome | Blast Phase Chronic Myelogenous Leukemia,... and other conditionsUnited States
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Stanford UniversityTerminatedLymphoma, Non-HodgkinUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingRecurrent Grade 1 Follicular Lymphoma | Recurrent Grade 2 Follicular Lymphoma | Recurrent Grade 3 Follicular Lymphoma | Recurrent Mantle Cell Lymphoma | Recurrent Non-Hodgkin LymphomaUnited States