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Search clinical trials for: AAV2-hRPE65v2,voretigene neparvovec-rzyl
Total 13 results
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States
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Spark TherapeuticsCompleted
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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Novartis PharmaceuticalsActive, not recruitingBiallelic RPE65 Mutation-associated Retinal DystrophyJapan
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Hadassah Medical OrganizationCompletedLeber Congenital AmaurosisIsrael
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University of PennsylvaniaNational Eye Institute (NEI)Active, not recruitingRetinal Diseases | Amaurosis of LeberUnited States
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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Nantes University HospitalCompletedLeber Congenital AmaurosisFrance
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GenSight BiologicsCompletedOptic, Atrophy, Hereditary, LeberUnited Kingdom, United States, France, Germany, Italy
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GenSight BiologicsCompletedOptic, Atrophy, Hereditary, LeberUnited Kingdom, United States, Germany, Italy, France
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Mercy Health OhioTerminatedOpen Fracture | Post-Op Wound InfectionUnited States