- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: AAV9 BBP-812
Total 3306 results
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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BiogenCompletedChoroideremiaUnited States, Germany, France
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Supernus Pharmaceuticals, Inc.Completed
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Supernus Pharmaceuticals, Inc.Completed
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Supernus Pharmaceuticals, Inc.Completed
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Supernus Pharmaceuticals, Inc.Completed
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MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
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Brain Neurotherapy Bio, Inc.California Institute for Regenerative Medicine (CIRM); Asklepios Biopharmaceutical...Active, not recruiting
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Chinese Academy of Medical Sciences, Fuwai HospitalActive, not recruitingPrimary HypertensionChina
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Baxalta now part of ShireTerminatedHemophilia BTurkey, Spain
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Libella Gene TherapeuticsUnknown
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Libella Gene TherapeuticsUnknownEvaluation of Safety and Tolerability of Libella Gene Therapy for Critical Limb Ischemia: AAV- hTERTCritical Limb IschemiaColombia
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Asklepios Biopharmaceutical, Inc.BayerNot yet recruiting
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VegaVect, Inc.National Eye Institute (NEI)Active, not recruiting
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Libella Gene TherapeuticsUnknownAlzheimer DiseaseColombia
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Grace Science, LLCRecruitingNGLY1 DeficiencyUnited States
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Supernus Pharmaceuticals, Inc.RecruitingAttention-Deficit/Hyperactivity DisorderUnited States
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Lantu BiopharmaNot yet recruitingSpinal Muscular Atrophy
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Chigenovo Co., LtdRecruitingBietti's Crystalline DystrophyChina
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Navire Pharma Inc., a BridgeBio companyActive, not recruitingTumor, SolidUnited States
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University of OxfordUniversity College, London; Moorfields Eye Hospital NHS Foundation TrustCompleted
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MeiraGTx, LLCActive, not recruitingParkinson DiseaseUnited States
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China National Center for Cardiovascular DiseasesCompleted
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CSL BehringRecruiting
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University College, LondonMedical Research CouncilRecruiting
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Neuracle Genetics, IncORA, Inc.RecruitingAge-Related Macular DegenerationCanada
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REGENXBIO Inc.National Heart, Lung, and Blood Institute (NHLBI)TerminatedHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Italy, Netherlands
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Hospital Israelita Albert EinsteinMinistry of Health, BrazilActive, not recruitingVascular Diseases | Ischemic Stroke | Cognitive Impairment | Blood PressureBrazil
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Brain Neurotherapy Bio, Inc.Recruiting
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic Amino Acid Decarboxylase DeficiencyTaiwan
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Neurocrine BiosciencesOregon Health and Science University; University of California, San Francisco; Veristat, Inc... and other collaboratorsCompletedParkinson's DiseaseUnited States
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GenethonCompletedLimb Girdle Muscular Dystrophy Type 2C | Gamma-sarcoglycanopathyFrance
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Sardocor Corp.RecruitingHeart Failure, Diastolic | Heart Failure With Preserved Ejection FractionUnited States
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CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
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Fondazione TelethonActive, not recruitingMucopolysaccharidosis Type VIItaly, Turkey
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MeiraGTx UK II LtdJanssen Research & Development, LLCCompleted
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LianBio LLCRecruitingAdvanced Solid Tumor | Advanced or Metastatic Non-small Cell Lung CancerChina
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Imperial College LondonBritish Heart Foundation; Leducq Foundation; Celladon CorporationTerminatedChronic Heart Failure | Patients That Have Received a Left Ventricular Assist DeviceUnited Kingdom
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The University of Texas Health Science Center at...Alzheimer's Association; The Claude D. Pepper Older Americans Independence... and other collaboratorsCompletedStress, Psychological | Stress, Physiological | Telomere ShorteningUnited States
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Vaxxinity, Inc.Syneos Health; Coalition for Epidemic Preparedness InnovationsActive, not recruitingCOVID-19 VaccinesPhilippines, United States, Panama
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Sardocor Corp.Not yet recruitingDMD-Associated Dilated Cardiomyopathy
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W. Michael HootenNational Institute on Drug Abuse (NIDA)Recruiting
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Sangamo TherapeuticsCeregeneCompletedIdiopathic Parkinson's DiseaseUnited States
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MeiraGTx, LLCEnrolling by invitationParkinson DiseaseUnited States
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University of PittsburghCompletedChest Pain | Shortness of Breath | Cardiac IschemiaUnited States
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National Institute of Allergy and Infectious Diseases...Active, not recruitingHIV-1 Infected Adults With Controlled ViremiaUnited States
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University of California, San FranciscoNational Cancer Institute (NCI); National Institutes of Health (NIH)Not yet recruitingColorectal Cancer | Colon Cancer | Cancer ColorectalUnited States
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Siemens Healthcare Diagnostics IncTerminated