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- US Clinical Trials Registry
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Search clinical trials for: EPI-743 5 mg/kg
Total 2021 results
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PTC TherapeuticsAxio Research. LLCCompleted
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PTC TherapeuticsCompletedFriedreich's AtaxiaUnited States
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Yale UniversityEdison Pharmaceuticals Inc; Rembrandt FoundationCompleted
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Edison Pharmaceuticals IncCompleted
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PTC TherapeuticsCompletedMitochondrial Diseases | Drug Resistant Epilepsy | Leigh Disease | Leigh Syndrome | Mitochondrial Encephalopathy (MELAS) | Pontocerebellar Hypoplasia Type 6 (PCH6) | Alpers Disease | Alpers SyndromeUnited States, Spain, United Kingdom, Canada, France, Italy, Poland, Sweden, Japan
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Tunitas Therapeutics, Inc.Tunitas Therapeutics Australia Pty LtdTerminatedAllergy and ImmunologyAustralia
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Corvus Pharmaceuticals, Inc.TerminatedCovid-19United States, Colombia, Spain, Canada, Peru, Brazil, Italy, Argentina, Chile, Germany, Mexico, Ukraine
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University of South FloridaEdison Pharmaceuticals IncCompleted
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Eisai Co., Ltd.Completed
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National Human Genome Research Institute (NHGRI)CompletedMitochondrial Disease | Myopathy | NeurologyUnited States
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PTC TherapeuticsNo longer available
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PTC TherapeuticsActive, not recruitingFriedreich AtaxiaUnited States
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PTC TherapeuticsCompletedLeigh SyndromeUnited States
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Edison Pharmaceuticals IncWithdrawn
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Edison Pharmaceuticals IncTerminated
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Crucell Holland BVNational Institute of Allergy and Infectious Diseases (NIAID)Completed
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Crucell Holland BVNational Institute of Allergy and Infectious Diseases (NIAID)Completed
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Bill & Melinda Gates Medical Research InstituteRecruiting
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RezoluteRecruitingCongenital HyperinsulinismBulgaria, Canada, Denmark, France, Georgia, Germany, Greece, Israel, Oman, Qatar, Saudi Arabia, Spain, Turkey, United Arab Emirates, United Kingdom, Vietnam
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Bambino Gesù Hospital and Research InstituteCatholic University of the Sacred HeartCompletedGenetic Disease | Retinopathy | Methylmalonic Aciduria and Homocystinuria,Cblc TypeItaly
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Edison Pharmaceuticals IncNo longer availableLeber's Hereditary Optic NeuropathyUnited States
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aTyr Pharma, Inc.Kyorin Pharmaceutical Co.,LtdRecruitingPulmonary SarcoidosisUnited States, Japan, Netherlands, Spain, United Kingdom, France, Italy, Brazil, Germany, Puerto Rico
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PfizerCompletedAlzheimer's DiseaseUnited States
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EA Pharma Co., Ltd.Completed
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Merck Sharp & Dohme LLCTerminated
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Aegerion Pharmaceuticals, Inc.CompletedHypercholesterolemiaUnited States
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TakedaCompletedHereditary AngioedemaJapan
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Centocor, Inc.CompletedPulmonary FibrosisUnited States, Canada, Netherlands, Belgium, Germany
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Janssen Research & Development, LLCJanssen Biologics BVCompletedUlcerative ColitisUnited States, France, United Kingdom, Belgium, Switzerland, Israel, Canada, Australia, Netherlands, New Zealand, Austria, Germany, Denmark, Czechia, Argentina
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MedImmune LLCPRA Health Sciences; Cambridge Antibody TechnologyTerminatedAsthmaNetherlands, United Kingdom, Australia, Germany, Poland
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NeuroVive Pharmaceutical ABCompleted
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Naurex, Inc, an affiliate of Allergan plcCompletedMajor Depressive DisorderUnited States
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Keymed Biosciences Co.LtdNot yet recruitingSystemic Lupus Erythematosus
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GlaxoSmithKlineCompletedMuscular DystrophiesFrance, United States
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MedImmune LLCCompletedHealthy SubjectsUnited States
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Healthgen Biotechnology Corp.RecruitingEmphysema Secondary to Congenital AATDUnited States
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Corbus Pharmaceuticals Inc.Cystic Fibrosis FoundationCompletedCystic FibrosisUnited States, United Kingdom, Sweden, Canada, France, Austria, Germany, Netherlands, Italy, Belgium, Portugal, Bulgaria, Czechia, Greece, Hungary, Poland, Romania, Russian Federation, Serbia, Slovakia, Spain
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Gangnam Severance HospitalCompleted
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Aileron Therapeutics, Inc.Completed
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BioMarin PharmaceuticalCompletedPhenylketonuriaUnited States
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Providence Health & ServicesCompletedMetastatic Sarcoma | Metastatic Carcinoma | Metastatic LymphomaUnited States
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Healthgen Biotechnology Corp.Completed
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Sichuan Haisco Pharmaceutical Group Co., LtdThe First Hospital of Jilin UniversityCompletedHealthy Elderly SubjectsChina
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MedImmune LLCCompletedRelapsed/Refractory Aggressive B-cell LymphomasUnited States
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Novartis PharmaceuticalsCompletedPsoriatic ArthritisUnited States, India, Greece, Thailand, Czechia, Philippines, Bulgaria, Russian Federation, Guatemala, South Africa, Malaysia, Colombia, Brazil, Poland, Turkey
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Integro TheranosticsRecruitingBreast Cancer | DCIS | Invasive Duct Carcinoma of BreastUnited States
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Suzhou Transcenta Therapeutics Co., Ltd.Completed
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Eisai Inc.BiogenActive, not recruitingAlzheimer's DiseaseUnited States, Canada, France, Germany, Italy, Japan, Korea, Republic of, Netherlands, Spain, Sweden, United Kingdom
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel