- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Exa-cel
Total 11620 results
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany
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Vertex Pharmaceuticals IncorporatedNot yet recruiting
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingSickle Cell Disease | Hemoglobinopathies | Hematological Diseases | Hydroxyurea Failure | Hydroxyurea IntoleranceUnited States, Italy, United Kingdom, Germany
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Hematological DiseasesUnited States, Belgium, Canada, France, Germany, Italy, United Kingdom
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, United Kingdom, Germany, Canada, Italy
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NHS Greater Glasgow and ClydeNot yet recruitingOsteoporosis | Osteoporosis RiskUnited Kingdom
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Sure, Inc.MaineHealthNot yet recruitingBreast Cancer
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Hospices Civils de LyonCompletedSarcopenia | SpondylarthropathyFrance
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M.D. Anderson Cancer CenterTerminatedRetinoblastomaUnited States
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Katie Larson OdeCompletedCystic Fibrosis-related DiabetesUnited States
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CARsgen Therapeutics Co., Ltd.Active, not recruitingMultiple MyelomaUnited States, Canada
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VA Office of Research and DevelopmentRecruitingLower-Limb AmputationUnited States
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Ruijin HospitalNot yet recruitingB-NHL, Extranodal, TP53 Alterations, Bulky Mass
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Centre Hospitalier Universitaire VaudoisLudwig Institute for Cancer ResearchCompleted
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Chinese University of Hong KongRecruiting
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingClinical Stage III Cutaneous Melanoma AJCC v8 | Pathologic Stage IIIB Cutaneous Melanoma AJCC v8 | Pathologic Stage IIIC Cutaneous Melanoma AJCC v8 | Pathologic Stage IIID Cutaneous Melanoma AJCC v8 | Pathologic Stage III Cutaneous Melanoma AJCC v8 | Pathologic Stage IIIA Cutaneous Melanoma... and other conditionsUnited States
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Nikkiso America, Inc.NAMSACompletedDialysis | Chronic Renal FailureUnited States
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Atara BiotherapeuticsNo longer availableLymphoproliferative Disorders | Stem Cell Transplant Complications | Epstein-Barr Virus (EBV) Infections | EBV+ Associated Lymphoma | EBV+ Associated Post-transplant Lymphoproliferative Disease (EBV+ PTLD) | Epstein-Barr Viremia | Lymphoma, AIDS-related | Epstein-Barr Virus-associated Lymphoproliferative... and other conditions
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McGill University Health Centre/Research Institute...Active, not recruitingVisceral Steatosis | Hiv | NAFLDCanada
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Fred Hutchinson Cancer CenterBreast Cancer Research FoundationCompleted
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Vanderbilt University Medical CenterUCB PharmaCompletedFistula | Abscess | Crohns DiseaseUnited States
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Mayo ClinicRecruitingIndolent Non-hodgkin Lymphoma | Chronic Lymphocytic Leukemia/Small Lymphocytic LymphomaUnited States
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H. Lee Moffitt Cancer Center and Research InstituteKite, A Gilead CompanyRecruitingLarge B-cell Lymphoma | Relapsed Non-Hodgkin LymphomaUnited States
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Services Hospital, LahoreRecruitingAndrogenetic AlopeciaPakistan
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Royan InstituteCompletedAcne Scars | Nasolabial Folds | Glabellar Crease | Deep Wrinkles of the ForeheadIran, Islamic Republic of
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The Catholic University of KoreaUnknownNon-small Cell Lung CancerKorea, Republic of
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Ohio State University Comprehensive Cancer CenterCompletedProstate CarcinomaUnited States
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Bettina MittendorferNot yet recruiting
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Smart Immune SASRecruitingHematological MalignanciesUnited States
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Second Affiliated Hospital, School of Medicine,...Zhejiang University; Hangzhou yuansheng biotechnology Co., LtdNot yet recruiting
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Chinese PLA General HospitalRecruitingLymphoma | Acute Myeloid Leukemia | Myelodysplastic Syndromes | Acute Lymphoblastic LeukemiaChina
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Michael Pulsipher, MDSeattle Children's Hospital; Nationwide Children's HospitalEnrolling by invitation
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University Hospital, BordeauxCompleted
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TC Erciyes UniversityUnknown
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)CompletedThyroid Gland Medullary Carcinoma | Differentiated Thyroid Gland Carcinoma | Malignant Adrenal Gland Pheochromocytoma | Malignant ParagangliomaUnited States
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Craig HospitalRecruitingSpinal Cord InjuriesUnited States
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United States Army Research Institute of Environmental...University of Arkansas; Eastern Michigan UniversityCompletedMuscle Protein Synthesis | Whole-body Protein BalanceUnited States
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University of CincinnatiActive, not recruiting
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Atara BiotherapeuticsRecruitingLymphoproliferative Disorders | Stem Cell Transplant Complications | Solid Organ Transplant Complications | Allogeneic Hematopoietic Cell Transplant | Epstein-Barr Virus+ Associated Post-transplant Lymphoproliferative Disease (EBV+ PTLD)United States, Austria, Australia, Belgium, Canada, France, Italy, Spain, United Kingdom
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Northeastern UniversityNational Center for Advancing Translational Sciences (NCATS)Completed
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingMelanoma | Neuroblastoma | Pancreatic Ductal Adenocarcinoma | Refractory Malignant Solid Neoplasm | Endometrial Carcinoma | Recurrent Ewing Sarcoma | Recurrent Hepatoblastoma | Recurrent Malignant Solid Neoplasm | Recurrent Non-Hodgkin Lymphoma | Recurrent Osteosarcoma | Refractory Ewing Sarcoma | Refractory... and other conditionsUnited States
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University of British ColumbiaUnknownSpinal Deformity, Paediatric Surgery, Tranexamic AcidCanada
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The University of Texas Health Science Center,...Completed
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Ruijin HospitalCellular Biomedicine Group Ltd.Completed
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University of North Carolina, Chapel HillCompleted
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Medical University of ViennaCompleted