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Search clinical trials for: Genetic: AAV5-hRKp.RPGR
Total 1584 results
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The University of Hong KongActive, not recruitingPhysical Activity | Type 2 Diabetes | Genetic Predisposition to Disease | Exercise | Fitness TrackersHong Kong
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Philipps University Marburg Medical CenterCompleted
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Opus Genetics, IncRecruiting
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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Benjamin GreenbergActive, not recruiting
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)Enrolling by invitationProstate CarcinomaUnited States
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SWOG Cancer Research NetworkNational Cancer Institute (NCI)RecruitingAdvanced Malignant Solid Neoplasm | Refractory Malignant Solid Neoplasm | Recurrent Malignant Solid Neoplasm | Metastatic Malignant Solid NeoplasmUnited States, Puerto Rico
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Assiut UniversityActive, not recruitingFamilial HypercholesterolemiaEgypt
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University Hospital, BordeauxCompleted
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Duke UniversityGenentech, Inc.TerminatedPrimary Open Angle Glaucoma | Glaucoma | Glaucoma, SuspectUnited States
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Massachusetts General HospitalNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)UnknownOverweight | Metabolic Syndrome | Pre-diabetesUnited States
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Assistance Publique - Hôpitaux de ParisCompletedIntellectual Deficiency | Cerebral AbnormalityFrance
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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Dana-Farber Cancer InstituteJohns Hopkins University; M.D. Anderson Cancer Center; Mayo Clinic; University... and other collaboratorsActive, not recruitingCandidates for Hereditary Pancreatic Cancer TestingUnited States
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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eyeDNA TherapeuticsRecruitingRetinitis PigmentosaFrance
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BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
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University of PennsylvaniaCompletedAlzheimer Disease | Genetic Predisposition to Disease
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasCompletedGene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaUnited Kingdom, United States
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Mayo ClinicNational Cancer Institute (NCI)CompletedMalignant Solid Neoplasm | Anatomic Stage III Breast Cancer AJCC v8 | Anatomic Stage IIIA Breast Cancer AJCC v8 | Anatomic Stage IIIB Breast Cancer AJCC v8 | Anatomic Stage IIIC Breast Cancer AJCC v8 | Prognostic Stage III Breast Cancer AJCC v8 | Prognostic Stage IIIA Breast Cancer AJCC v8 | Prognostic... and other conditionsUnited States
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaCompletedAchromatopsiaUnited Kingdom, United States
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Tongji HospitalRecruitingDiminished Ovarian Reserve | Premature Ovarian Insufficiency | Early MenopauseChina
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Tampere University HospitalOslo University Hospital; University of Turku; Oulu University Hospital; University... and other collaboratorsRecruitingCeliac Disease | Dermatitis HerpetiformisFinland
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University of Alabama at BirminghamNational Institute of Mental Health (NIMH)RecruitingDepression | Suicide, Attempted | Suicide | Major Depressive Disorder | Suicidal Ideas | MDD | Depression and Suicide | Depression in Adolescence | Depression, TeenUnited States
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Benjamin TerrierRecruiting
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ClinLogic LLCMDGlobalRecruitingEarly Detection of CancerUnited States
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Nova Scotia Health AuthorityRecruitingSchizophrenia | Bipolar Disorder | Major Depressive Disorder | Mental Illness | Psychosis | Cannabis UseCanada
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Nicklaus Children's Hospital f/k/a Miami Children...Rady Pediatric Genomics & Systems Medicine InstituteRecruiting
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UNICANCERInstitut National de la Santé Et de la Recherche Médicale, France; Gustave... and other collaboratorsRecruitingMutation | Hereditary Breast and Ovarian CancerFrance
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University of DundeeBritish Lung Foundation; Newcastle University; University of Leicester; University... and other collaboratorsActive, not recruitingIdiopathic Pulmonary Fibrosis | Lung Diseases, Interstitial | Idiopathic Interstitial Pneumonias | Alveolitis, Extrinsic Allergic | Lung; Disease, Interstitial, With Fibrosis | Bird Fancier's LungUnited Kingdom
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Multiple Myeloma Research FoundationActive, not recruiting
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Second Affiliated Hospital, School of Medicine,...CompletedWilson Disease | Generalized EpilepsyChina
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St Mary's University CollegeFulham Football ClubCompletedInjuries | Genetic ChangeUnited Kingdom
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University Hospital, RouenCompletedBreast Cancer | Colorectal Cancer | Ovarian Cancer | Pediatric Cancers | Multiple Primary Malignant TumoursFrance
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Data Collection Analysis Business ManagementPAS Research ServicesUnknownEndometrial Cancer | Colon CancerUnited States
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Southern Medical University, ChinaUnknown
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CHU de ReimsUnknownEndometrial Hyperplasia and Endometrial CancersFrance
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Sun Yat-sen UniversityUnknown
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University Hospital, AngersCompleted
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University Hospital, MontpellierMinistry of Health, FranceCompletedAutosomal Dominant Retinitis PigmentosaFrance
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University of British ColumbiaCompletedSchizophrenia | Schizoaffective Disorder | Bipolar DisorderCanada
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Tianjin Medical UniversityTerminatedThe Mechanism of Retinal Neovascularization of Diabetic | Retinopathy.China
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Prostate Cancer Clinical Trials ConsortiumMemorial Sloan Kettering Cancer Center; Fred Hutchinson Cancer Center; Sidney... and other collaboratorsRecruiting
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Liggins InstituteRecruiting
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University of Milano BicoccaRecruiting
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Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRecruiting
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NorthShore University HealthSystemJohns Hopkins University; Northwestern University; GoPath DiagnosticsRecruitingPerformance of Inherited Risk Assessment for Predicting Prostate Cancer From Prostate Biopsy (GenBx)Prostate CancerUnited States
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University Hospital MuensterUniversity of Pisa; Medical University of Vienna; Hacettepe University; Charite... and other collaboratorsRecruitingPrimary Ciliary Dyskinesia | Ciliary Motility DisordersGermany