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Search clinical trials for: tgAAC94 gene therapy vector
Total 395 results
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Targeted Genetics CorporationCompletedRheumatoid ArthritisCanada, United States
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Targeted Genetics CorporationCompletedArthritis, Rheumatoid | Arthritis, Psoriatic | Ankylosing SpondylitisUnited States
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Children's Hospital of Chongqing Medical UniversityRecruiting
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University of California, Los AngelesNational Heart, Lung, and Blood Institute (NHLBI); Boston Children's Hospital; California Institute for Regenerative Medicine (CIRM) and other collaboratorsRecruitingGranulomatous Disease, Chronic, X-linkedUnited States
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GenethonCompletedLimb Girdle Muscular Dystrophy Type 2C | Gamma-sarcoglycanopathyFrance
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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PfizerActive, not recruitingHemophilia ASpain, Taiwan, Australia, United States, Japan, France, Turkey, Germany, Korea, Republic of, United Kingdom, Saudi Arabia, Canada, Greece, Sweden, Brazil, Italy
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Mark TuszynskiOhio State UniversityRecruitingMild Cognitive Impairment | Alzheimer's DiseaseUnited States
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic L-amino Acid Decarboxylase (AADC) DeficiencyTaiwan
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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The Methodist Hospital Research InstituteRecruitingGlioblastoma | Anaplastic AstrocytomaUnited States
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Leiden University Medical CenterZonMw: The Netherlands Organisation for Health Research and Development; Horizon...RecruitingSevere Combined Immunodeficiency Due to RAG1 DeficiencySpain, Netherlands, Italy, Poland, Australia, Turkey, United Kingdom
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World Federation of HemophiliaNot yet recruiting
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Megan WaldropAlcyone TherapeuticsEnrolling by invitation
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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David Baskin MDCenter for Cell and Gene Therapy, Baylor College of MedicineRecruitingGlioblastoma Multiforme | Astrocytoma, Grade IIIUnited States
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Tocagen Inc.CompletedGlioblastoma | Anaplastic Oligoastrocytoma | Anaplastic Astrocytoma | Anaplastic OligodendrogliomaUnited States
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Shenzhen SiBiono GeneTech Co.,LtdUnknownHCC | DiabetesChina
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University College, LondonMedical Research CouncilNot yet recruitingDrug Resistant Epilepsy
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American Gene Technologies International Inc.Enrolling by invitation
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Eunice Kennedy Shriver National Institute of Child...University of MinnesotaCompleted
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Shenzhen SiBiono GeneTech Co.,LtdUnknown
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Nanoscope Therapeutics Inc.CompletedRetinal Degeneration | Retinal Diseases | Retinitis PigmentosaIndia
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Nanoscope Therapeutics Inc.Enrolling by invitationRetinal Degeneration | Retinitis Pigmentosa | Retinal DiseaseIndia
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseUnited Kingdom
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Shenzhen Geno-Immune Medical InstituteUnknown
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Nanoscope Therapeutics Inc.Completed
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseFrance
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Hubert Serve, Prof., MDUnknown
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Eastern Cooperative Oncology GroupNational Cancer Institute (NCI)CompletedLung CancerUnited States
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Nanoscope Therapeutics Inc.Enrolling by invitationEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Neuracle Genetics, IncORA, Inc.RecruitingAge-Related Macular DegenerationCanada
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BiogenCompletedChoroideremiaUnited States, Germany, France
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Nanoscope Therapeutics Inc.Enrolling by invitationStargardt DiseaseUnited States
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REGENXBIO Inc.National Heart, Lung, and Blood Institute (NHLBI)TerminatedHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Italy, Netherlands
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University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... and other collaboratorsActive, not recruitingMucopolysaccharidosis Type IIIAUnited Kingdom
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GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
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GenethonHôpital Necker-Enfants MaladesCompleted
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Asklepios Biopharmaceutical, Inc.RecruitingCongestive Heart FailureUnited States
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Bin LiUnknownAcute LHON | Onset Within Three Months | Onset Between 3 to 6 Months | Onset Between 6 to 12 Months | Onset Between 12 to 24 Months | Onset Between 24 to 60 Months | Onset Over 60 MonthsChina
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University of PennsylvaniaCompleted
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The Christie NHS Foundation TrustUnknownSarcoma | Cervical Cancer | Breast Cancer | Ovarian Cancer | Fallopian Tube Cancer | Prostate Cancer | Vulvar Cancer | Endometrial Cancer | Vaginal Cancer | Primary Peritoneal Cavity CancerUnited Kingdom
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Giselle ShollerDell, Inc.CompletedMedulloblastoma | Neuroblastoma | Brain Tumors | Rare TumorsUnited States
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CelgeneRecruitingNeoplasmsUnited States, Belgium, Spain, Switzerland, Canada, France, Germany, Japan, Finland, United Kingdom, Austria, Italy, Netherlands, Norway, Sweden
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Orchard TherapeuticsOspedale San RaffaeleActive, not recruitingLysosomal Storage Disease | Metachromatic LeukodystrophyItaly
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STZ eyetrialActive, not recruiting
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IRCCS San RaffaeleFondazione TelethonCompletedSevere Combined Immunodeficiency Syndrome
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Shenzhen SiBiono GeneTech Co.,LtdUnknownAdvanced Oral and Maxillofacial Malignant TumorsChina
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University of PennsylvaniaTerminatedOrnithine Transcarbamylase Deficiency Disease